CN116064534A - 编码Cas9核酸酶的核酸的饮食控制的表达及其用途 - Google Patents

编码Cas9核酸酶的核酸的饮食控制的表达及其用途 Download PDF

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CN116064534A
CN116064534A CN202211117939.7A CN202211117939A CN116064534A CN 116064534 A CN116064534 A CN 116064534A CN 202211117939 A CN202211117939 A CN 202211117939A CN 116064534 A CN116064534 A CN 116064534A
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nucleic acid
cells
expression
cas9
pharmaceutical composition
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CN202211117939.7A
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Chinese (zh)
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P·拉瓦萨德
J·马莱特
C·瑟格拉
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Centre National de la Recherche Scientifique CNRS
Assistance Publique Hopitaux de Paris APHP
Institut National de la Sante et de la Recherche Medicale INSERM
Sorbonne Universite
Commissariat a lEnergie Atomique et aux Energies Alternatives CEA
Institut du Cerveau et de La Moelle Epiniere ICM
Original Assignee
Centre National de la Recherche Scientifique CNRS
Assistance Publique Hopitaux de Paris APHP
Institut National de la Sante et de la Recherche Medicale INSERM
Sorbonne Universite
Commissariat a lEnergie Atomique et aux Energies Alternatives CEA
Institut du Cerveau et de La Moelle Epiniere ICM
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Publication of CN116064534A publication Critical patent/CN116064534A/zh
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CN202211117939.7A 2016-06-03 2017-06-02 编码Cas9核酸酶的核酸的饮食控制的表达及其用途 Pending CN116064534A (zh)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
EPEP16172964 2016-06-03
EP16172964 2016-06-03
CN201780045274.4A CN109906271A (zh) 2016-06-03 2017-06-02 编码Cas9核酸酶的核酸的饮食控制的表达及其用途
PCT/EP2017/063549 WO2017207797A1 (en) 2016-06-03 2017-06-02 Diet controlled expression of a nucleic acid encoding cas9 nuclease and uses thereof

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CN201780045274.4A Division CN109906271A (zh) 2016-06-03 2017-06-02 编码Cas9核酸酶的核酸的饮食控制的表达及其用途

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CN201780045274.4A Pending CN109906271A (zh) 2016-06-03 2017-06-02 编码Cas9核酸酶的核酸的饮食控制的表达及其用途

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AU (1) AU2017275769B2 (enExample)
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Cited By (1)

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Publication number Priority date Publication date Assignee Title
CN116732043A (zh) * 2023-08-10 2023-09-12 四川省医学科学院·四川省人民医院 一种突变基因及其白内障筛查的用途与白内障筛查试剂盒

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Publication number Priority date Publication date Assignee Title
AU2019314475A1 (en) * 2018-08-01 2021-02-18 The Regents Of The University Of Colorado A Body Corporate Programmable designer therapeutic fusogenic secreted gectosome vesicles for macromolecule delivery and genome modification
CN115820654A (zh) * 2019-08-30 2023-03-21 深圳华大基因股份有限公司 Loxhd1基因突变体及其应用
CN114058689B (zh) * 2020-07-30 2024-08-20 南京市妇幼保健院 一种基因突变检测试剂盒及其应用
AU2023304674A1 (en) * 2022-07-05 2025-01-16 Centre Hospitalier Universitaire De Clermont-Fd Controlled expression of a transgene in human t or nk cells for use in cellular immunotherapy
WO2024100176A1 (en) * 2022-11-10 2024-05-16 Nutritheragene Controlled gene therapy of ocular diseases

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FR2982277B1 (fr) * 2011-11-08 2015-08-21 Agronomique Inst Nat Rech Cassette d'expression inductible et ses utilisations
PT3363902T (pt) * 2012-12-06 2019-12-19 Sigma Aldrich Co Llc Modificação e regulação de genoma baseadas em crispr
US20150098954A1 (en) * 2013-10-08 2015-04-09 Elwha Llc Compositions and Methods Related to CRISPR Targeting
BR112016013201B1 (pt) * 2013-12-12 2023-01-31 The Broad Institute, Inc. Uso de uma composição compreendendo um sistema crispr-cas no tratamento de uma doença genética ocular
EP3540051B1 (en) * 2013-12-12 2022-08-17 The Broad Institute, Inc. Delivery, use and therapeutic applications of the crispr-cas systems and compositions for hsv and viral diseases and disorders.

Cited By (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN116732043A (zh) * 2023-08-10 2023-09-12 四川省医学科学院·四川省人民医院 一种突变基因及其白内障筛查的用途与白内障筛查试剂盒
CN116732043B (zh) * 2023-08-10 2023-10-17 四川省医学科学院·四川省人民医院 一种突变基因及其白内障筛查的用途与白内障筛查试剂盒

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AU2017275769A1 (en) 2018-12-20
IL263291A (en) 2018-12-31
RU2018142174A3 (enExample) 2020-09-30
JP2022133441A (ja) 2022-09-13
CA3025591A1 (en) 2017-12-07
US20190185832A1 (en) 2019-06-20
AU2017275769B2 (en) 2023-04-13
JP2019517262A (ja) 2019-06-24
BR112018074930A2 (pt) 2019-03-12
KR20190031230A (ko) 2019-03-25
IL263291B1 (en) 2023-03-01
WO2017207797A1 (en) 2017-12-07
RU2018142174A (ru) 2020-07-10
KR102317622B1 (ko) 2021-10-26
US20230313161A1 (en) 2023-10-05
CN109906271A (zh) 2019-06-18
RU2771383C2 (ru) 2022-05-04
IL263291B2 (en) 2023-07-01
SG11201810772XA (en) 2018-12-28
JP7436145B2 (ja) 2024-02-21

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