CN112912399A - 肌肉靶向复合物及其用于治疗蓬佩病的用途 - Google Patents

肌肉靶向复合物及其用于治疗蓬佩病的用途 Download PDF

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CN112912399A
CN112912399A CN201980064590.5A CN201980064590A CN112912399A CN 112912399 A CN112912399 A CN 112912399A CN 201980064590 A CN201980064590 A CN 201980064590A CN 112912399 A CN112912399 A CN 112912399A
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complex
antibody
muscle
oligonucleotide
transferrin receptor
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Chinese (zh)
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罗梅什·R·苏布拉马尼亚
穆罕默德·T·卡塔纳尼
蒂莫西·威登
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Dyne Therapeutics Inc
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Dyne Therapeutics Inc
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Priority to CN202410663435.8A priority Critical patent/CN118662653A/zh
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CN201980064590.5A 2018-08-02 2019-08-02 肌肉靶向复合物及其用于治疗蓬佩病的用途 Pending CN112912399A (zh)

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PCT/US2019/044960 WO2020028841A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating pompe disease

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