JP2021533197A - ポンペ病を処置するための筋標的化複合体およびそれらの使用 - Google Patents

ポンペ病を処置するための筋標的化複合体およびそれらの使用 Download PDF

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JP2021533197A
JP2021533197A JP2021529257A JP2021529257A JP2021533197A JP 2021533197 A JP2021533197 A JP 2021533197A JP 2021529257 A JP2021529257 A JP 2021529257A JP 2021529257 A JP2021529257 A JP 2021529257A JP 2021533197 A JP2021533197 A JP 2021533197A
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antibody
muscle
oligonucleotide
complex
transferrin receptor
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JPWO2020028841A5 (enExample
Inventor
スブラマニアン，ロメシ，アール．
カタナニ，モハメド，ティー．
ウィーデン，ティモシー
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Dyne Therapeutics Inc
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Dyne Therapeutics Inc
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Publication of JP2021533197A publication Critical patent/JP2021533197A/ja
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Priority to JP2025006544A priority Critical patent/JP2025071093A/ja
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JP2021529257A 2018-08-02 2019-08-02 ポンペ病を処置するための筋標的化複合体およびそれらの使用 Pending JP2021533197A (ja)

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JP2025006544A JP2025071093A (ja) 2018-08-02 2025-01-17 ポンペ病を処置するための筋標的化複合体およびそれらの使用

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US201862713959P 2018-08-02 2018-08-02
US62/713,959 2018-08-02
PCT/US2019/044960 WO2020028841A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating pompe disease

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