CN112399849A - 含有反义寡核苷酸的组合物及其在迪谢内肌营养不良症的治疗中的用途 - Google Patents
含有反义寡核苷酸的组合物及其在迪谢内肌营养不良症的治疗中的用途 Download PDFInfo
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| PCT/JP2019/026393 WO2020004675A1 (ja) | 2018-06-26 | 2019-06-26 | アンチセンスオリゴヌクレオチドを含有する組成物およびデュシェンヌ型筋ジストロフィーの治療へのその使用 |
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| BR112022022889A2 (pt) | 2020-05-11 | 2023-04-04 | Stoke Therapeutics Inc | Oligômeros antissentido de opa1 para tratamento de condições e doenças |
| MX2023012559A (es) | 2021-04-30 | 2023-12-15 | Sarepta Therapeutics Inc | Métodos de tratamiento para la distrofia muscular. |
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| EP3815696A1 (en) | 2021-05-05 |
| AU2019293687B2 (en) | 2025-10-02 |
| JPWO2020004675A1 (ja) | 2021-07-15 |
| CL2020003367A1 (es) | 2021-05-24 |
| CA3101321A1 (en) | 2020-01-02 |
| MX2020013880A (es) | 2021-03-09 |
| AU2019293687A1 (en) | 2021-01-07 |
| US20210261963A1 (en) | 2021-08-26 |
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| PH12020552078A1 (en) | 2021-05-31 |
| TW202035692A (zh) | 2020-10-01 |
| BR112020026542A2 (pt) | 2021-04-06 |
| NZ770540A (en) | 2025-12-19 |
| KR20210023988A (ko) | 2021-03-04 |
| US20240158792A1 (en) | 2024-05-16 |
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