CN111433361B - 天使综合征反义治疗 - Google Patents

天使综合征反义治疗 Download PDF

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CN111433361B
CN111433361B CN201880077892.1A CN201880077892A CN111433361B CN 111433361 B CN111433361 B CN 111433361B CN 201880077892 A CN201880077892 A CN 201880077892A CN 111433361 B CN111433361 B CN 111433361B
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artificial sequence
synthetic construct
rna
dna
aso
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CN111433361A (zh
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S·V·迪多
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Texas A&M University System
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CN201880077892.1A 2017-12-01 2018-11-30 天使综合征反义治疗 Active CN111433361B (zh)

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US201762593431P 2017-12-01 2017-12-01
US62/593,431 2017-12-01
US201862676034P 2018-05-24 2018-05-24
US62/676,034 2018-05-24
PCT/US2018/063416 WO2019109001A1 (en) 2017-12-01 2018-11-30 Angelman syndrome antisense treatment

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CA3079755A1 (en) 2019-06-06
US20230112629A1 (en) 2023-04-13
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