CN107532162A - 用于利用寡核苷酸编辑细胞中核酸的组合物和方法 - Google Patents

用于利用寡核苷酸编辑细胞中核酸的组合物和方法 Download PDF

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CN107532162A
CN107532162A CN201580075918.5A CN201580075918A CN107532162A CN 107532162 A CN107532162 A CN 107532162A CN 201580075918 A CN201580075918 A CN 201580075918A CN 107532162 A CN107532162 A CN 107532162A
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oligonucleotides
editing
modification
nucleic acid
nucleotides
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托德·M·伍尔夫
亚历山大·列别杰夫
理查德·I·浩吉费
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CN201580075918.5A 2014-12-12 2015-12-11 用于利用寡核苷酸编辑细胞中核酸的组合物和方法 Pending CN107532162A (zh)

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
US201462091027P 2014-12-12 2014-12-12
US62/091,027 2014-12-12
US201562141077P 2015-03-31 2015-03-31
US62/141,077 2015-03-31
US201562180175P 2015-06-16 2015-06-16
US62/180,175 2015-06-16
US201562252693P 2015-11-09 2015-11-09
US62/252,693 2015-11-09
PCT/US2015/065348 WO2016094845A2 (en) 2014-12-12 2015-12-11 Compositions and methods for editing nucleic acids in cells utilizing oligonucleotides

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CN107532162A true CN107532162A (zh) 2018-01-02

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US (1) US12359197B2 (https=)
EP (2) EP4372091A3 (https=)
JP (2) JP6997623B2 (https=)
CN (1) CN107532162A (https=)
CA (1) CA2969464A1 (https=)
WO (1) WO2016094845A2 (https=)

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CN113453696A (zh) * 2018-09-26 2021-09-28 牛津大学创新有限公司 血红蛋白基因的编辑
WO2021209010A1 (zh) * 2020-04-15 2021-10-21 博雅辑因（北京）生物科技有限公司 一种治疗赫勒氏综合征的方法和药物
CN113666847A (zh) * 2021-08-31 2021-11-19 派普医药(江苏)有限公司 一种odmt,n-fmoc-氨基丁基-1,3-丙二醇的合成方法
CN115552034A (zh) * 2020-01-31 2022-12-30 瑞泽恩制药公司 液相色谱法和质谱法用于表征寡核苷酸的用途
CN115997124A (zh) * 2020-04-30 2023-04-21 维兰尼迪科技有限责任公司 用于检测生物或化学实体或事件的分子导线

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