CA3066623A1 - Self-regulating aav vectors for safe expression of mecp2 in rett syndrome - Google Patents

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Publication number

CA3066623A1

CA3066623A1 CA3066623A CA3066623A CA3066623A1 CA 3066623 A1 CA3066623 A1 CA 3066623A1 CA 3066623 A CA3066623 A CA 3066623A CA 3066623 A CA3066623 A CA 3066623A CA 3066623 A1 CA3066623 A1 CA 3066623A1

Authority

CA

Canada

Prior art keywords

mir

hsa

mirna

nucleic acid

mecp2

Prior art date

2017-06-06

Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)

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