AU2018253959B2 - Gene therapy - Google Patents

Gene therapy Download PDF

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Publication number
AU2018253959B2
AU2018253959B2 AU2018253959A AU2018253959A AU2018253959B2 AU 2018253959 B2 AU2018253959 B2 AU 2018253959B2 AU 2018253959 A AU2018253959 A AU 2018253959A AU 2018253959 A AU2018253959 A AU 2018253959A AU 2018253959 B2 AU2018253959 B2 AU 2018253959B2
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Prior art keywords
ifn
ctrl
cells
cell
injection
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AU2018253959A
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AU2018253959A1 (en
Inventor
Giulia ESCOBAR
Bernhard Rudolf Gentner
Adele MUCCI
Luigi Naldini
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Fondazione Telethon
Ospedale San Raffaele SRL
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Fondazione Telethon
Ospedale San Raffaele SRL
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Priority claimed from GBGB1706410.6A external-priority patent/GB201706410D0/en
Priority claimed from GBGB1801511.5A external-priority patent/GB201801511D0/en
Application filed by Fondazione Telethon, Ospedale San Raffaele SRL filed Critical Fondazione Telethon
Publication of AU2018253959A1 publication Critical patent/AU2018253959A1/en
Assigned to OSPEDALE SAN RAFFAELE S.R.L., FONDAZIONE TELETHON ETS reassignment OSPEDALE SAN RAFFAELE S.R.L. Amend patent request/document other than specification (104) Assignors: FONDAZIONE TELETHON, OSPEDALE SAN RAFFAELE S.R.L.
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    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • A61K35/00—Medicinal preparations containing materials or reaction products thereof with undetermined constitution
    • A61K35/12—Materials from mammals; Compositions comprising non-specified tissues or cells; Compositions comprising non-embryonic stem cells; Genetically modified cells
    • A61K35/28—Bone marrow; Haematopoietic stem cells; Mesenchymal stem cells of any origin, e.g. adipose-derived stem cells
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    • A01K—ANIMAL HUSBANDRY; AVICULTURE; APICULTURE; PISCICULTURE; FISHING; REARING OR BREEDING ANIMALS, NOT OTHERWISE PROVIDED FOR; NEW BREEDS OF ANIMALS
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    • A01K67/027—New or modified breeds of vertebrates
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    • A61K31/33—Heterocyclic compounds
    • A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/40—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having five-membered rings with one nitrogen as the only ring hetero atom, e.g. sulpiride, succinimide, tolmetin, buflomedil
    • A61K31/403—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having five-membered rings with one nitrogen as the only ring hetero atom, e.g. sulpiride, succinimide, tolmetin, buflomedil condensed with carbocyclic rings, e.g. carbazole
    • A61K31/404—Indoles, e.g. pindolol
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    • C07K16/18—Immunoglobulins [IGs], e.g. monoclonal or polyclonal antibodies against material from animals or humans
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AU2018253959A 2017-04-21 2018-04-20 Gene therapy Active AU2018253959B2 (en)

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