AU2017324462B2 - Modulation of liver genes - Google Patents

Modulation of liver genes Download PDF

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Publication number
AU2017324462B2
AU2017324462B2 AU2017324462A AU2017324462A AU2017324462B2 AU 2017324462 B2 AU2017324462 B2 AU 2017324462B2 AU 2017324462 A AU2017324462 A AU 2017324462A AU 2017324462 A AU2017324462 A AU 2017324462A AU 2017324462 B2 AU2017324462 B2 AU 2017324462B2
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seq
gene
exon
sequence
sbs
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AU2017324462A
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AU2017324462A1 (en
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Anthony Conway
Gary K. Lee
David Paschon
Lei Zhang
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Sangamo Therapeutics Inc
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Sangamo Therapeutics Inc
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    • A61K48/00—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy
    • A61K48/005—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
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    • A61P13/00—Drugs for disorders of the urinary system
    • A61P13/02—Drugs for disorders of the urinary system of urine or of the urinary tract, e.g. urine acidifiers
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    • C07K14/811—Serine protease (E.C. 3.4.21) inhibitors
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    • C12N9/14—Hydrolases (3)
    • C12N9/48—Hydrolases (3) acting on peptide bonds (3.4)
    • C12N9/50—Proteinases, e.g. Endopeptidases (3.4.21-3.4.25)
    • C12N9/64—Proteinases, e.g. Endopeptidases (3.4.21-3.4.25) derived from animal tissue
    • C12N9/6421—Proteinases, e.g. Endopeptidases (3.4.21-3.4.25) derived from animal tissue from mammals
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    • C12N9/14—Hydrolases (3)
    • C12N9/48—Hydrolases (3) acting on peptide bonds (3.4)
    • C12N9/50—Proteinases, e.g. Endopeptidases (3.4.21-3.4.25)
    • C12N9/64—Proteinases, e.g. Endopeptidases (3.4.21-3.4.25) derived from animal tissue
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    • C12N9/6424—Serine endopeptidases (3.4.21)
    • C12N9/6445—Kallikreins (3.4.21.34; 3.4.21.35)
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    • C12N2750/14011—Parvoviridae
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AU2017324462A 2016-09-07 2017-09-07 Modulation of liver genes Expired - Fee Related AU2017324462B2 (en)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201662384428P 2016-09-07 2016-09-07
US62/384,428 2016-09-07
PCT/US2017/050446 WO2018049009A2 (en) 2016-09-07 2017-09-07 Modulation of liver genes

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AU2017324462A1 AU2017324462A1 (en) 2019-03-14
AU2017324462B2 true AU2017324462B2 (en) 2024-03-21

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US (2) US10960085B2 (enExample)
EP (1) EP3509645A4 (enExample)
JP (2) JP7256739B2 (enExample)
AU (1) AU2017324462B2 (enExample)
CA (1) CA3035534A1 (enExample)
WO (1) WO2018049009A2 (enExample)

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