AU2017313917B2 - CRISPR-Cas genome engineering via a modular AAV delivery system - Google Patents

CRISPR-Cas genome engineering via a modular AAV delivery system Download PDF

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Publication number
AU2017313917B2
AU2017313917B2 AU2017313917A AU2017313917A AU2017313917B2 AU 2017313917 B2 AU2017313917 B2 AU 2017313917B2 AU 2017313917 A AU2017313917 A AU 2017313917A AU 2017313917 A AU2017313917 A AU 2017313917A AU 2017313917 B2 AU2017313917 B2 AU 2017313917B2
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cas9
polynucleotide
aav
expression
capsid
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AU2017313917A1 (en
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Ana Moreno COLLADO
Dhruva KATREKAR
Prashant MALI
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University of California San Diego UCSD
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University of California Berkeley
University of California San Diego UCSD
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AU2017313917A 2016-08-18 2017-08-18 CRISPR-Cas genome engineering via a modular AAV delivery system Active AU2017313917B2 (en)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201662376855P 2016-08-18 2016-08-18
US62/376,855 2016-08-18
US201662415858P 2016-11-01 2016-11-01
US62/415,858 2016-11-01
US201762481589P 2017-04-04 2017-04-04
US62/481,589 2017-04-04
PCT/US2017/047687 WO2018035503A1 (en) 2016-08-18 2017-08-18 Crispr-cas genome engineering via a modular aav delivery system

Publications (2)

Publication Number Publication Date
AU2017313917A1 AU2017313917A1 (en) 2019-03-07
AU2017313917B2 true AU2017313917B2 (en) 2023-12-21

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US (1) US20200340012A1 (https=)
EP (1) EP3500667A4 (https=)
JP (3) JP2019524162A (https=)
KR (1) KR20190065251A (https=)
CN (1) CN109996880A (https=)
AU (1) AU2017313917B2 (https=)
CA (1) CA3034089A1 (https=)
IL (2) IL315358A (https=)
WO (1) WO2018035503A1 (https=)

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US9526784B2 (en) 2013-09-06 2016-12-27 President And Fellows Of Harvard College Delivery system for functional nucleases
US9388430B2 (en) 2013-09-06 2016-07-12 President And Fellows Of Harvard College Cas9-recombinase fusion proteins and uses thereof
US9340799B2 (en) 2013-09-06 2016-05-17 President And Fellows Of Harvard College MRNA-sensing switchable gRNAs
US20150165054A1 (en) 2013-12-12 2015-06-18 President And Fellows Of Harvard College Methods for correcting caspase-9 point mutations
WO2016022363A2 (en) 2014-07-30 2016-02-11 President And Fellows Of Harvard College Cas9 proteins including ligand-dependent inteins
JP7109784B2 (ja) 2015-10-23 2022-08-01 プレジデント アンド フェローズ オブ ハーバード カレッジ 遺伝子編集のための進化したＣａｓ９蛋白質
JP7305534B2 (ja) * 2016-07-06 2023-07-10 バーテックス ファーマシューティカルズ インコーポレイテッド 疼痛関連障害を処置するための物質及び方法
AU2017292173B2 (en) 2016-07-06 2022-01-13 Vertex Pharmaceuticals Incorporated Materials and methods for treatment of pain related disorders
KR102547316B1 (ko) 2016-08-03 2023-06-23 프레지던트 앤드 펠로우즈 오브 하바드 칼리지 아데노신 핵염기 편집제 및 그의 용도
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EP3526320A1 (en) 2016-10-14 2019-08-21 President and Fellows of Harvard College Aav delivery of nucleobase editors
WO2018119359A1 (en) 2016-12-23 2018-06-28 President And Fellows Of Harvard College Editing of ccr5 receptor gene to protect against hiv infection
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CA3057192A1 (en) 2017-03-23 2018-09-27 President And Fellows Of Harvard College Nucleobase editors comprising nucleic acid programmable dna binding proteins
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