AU2014223243B2 - Talen-based gene correction - Google Patents
Talen-based gene correction Download PDFInfo
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- AU2014223243B2 AU2014223243B2 AU2014223243A AU2014223243A AU2014223243B2 AU 2014223243 B2 AU2014223243 B2 AU 2014223243B2 AU 2014223243 A AU2014223243 A AU 2014223243A AU 2014223243 A AU2014223243 A AU 2014223243A AU 2014223243 B2 AU2014223243 B2 AU 2014223243B2
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| US9850497B2 (en) * | 2013-11-04 | 2017-12-26 | Regents Of The University Of Minnesota | Gene targeting methods and tools |
| RU2714404C2 (ru) | 2014-01-31 | 2020-02-14 | Фэктор Байосайенс Инк. | Способы и продукты для получения и доставки нуклеиновых кислот |
| AU2015350103A1 (en) | 2014-11-17 | 2017-06-29 | Adicet Bio, Inc. | Engineered gamma delta T-cells |
| EP3543339A1 (en) | 2015-02-13 | 2019-09-25 | Factor Bioscience Inc. | Nucleic acid products and methods of administration thereof |
| CN104726495B (zh) * | 2015-03-25 | 2018-06-19 | 西北农林科技大学 | 一种基于talen介导的基因打靶敲除山羊blg的载体及重组细胞 |
| CN108124453B (zh) | 2015-03-31 | 2022-04-05 | 爱克莱根科技公司 | 用于将DNA序列靶向并入细胞或生物体的基因组中的Cas9逆转录病毒整合酶和Cas9重组酶系统 |
| WO2016178207A1 (en) | 2015-05-04 | 2016-11-10 | Ramot At Tel-Aviv University Ltd. | Methods and kits for fragmenting dna |
| IL255697B2 (en) | 2015-05-18 | 2023-11-01 | Tcr2 Therapeutics Inc | Compositions and methods for TCR programming using fusion proteins |
| US10166255B2 (en) | 2015-07-31 | 2019-01-01 | Regents Of The University Of Minnesota | Intracellular genomic transplant and methods of therapy |
| US20180296600A1 (en) * | 2015-10-27 | 2018-10-18 | The Board Of Trustees Of The Leland Stanford Junior University | Treatment of epidermolysis bullosa by injection of autologous collagen vii overexpressing leukocytes |
| PT3377637T (pt) | 2016-04-08 | 2020-06-17 | Krystal Biotech Inc | Composições para uso em métodos para o tratamento de ferimentos, transtornos e doenças da pele |
| EP3454870A4 (en) | 2016-05-12 | 2020-03-04 | Adicet Bio Inc. | METHOD FOR SELECTIVE EXPANSION OF GAMMA DELTA T CELL POPULATIONS AND COMPOSITIONS THEREOF |
| CN109715668A (zh) | 2016-08-02 | 2019-05-03 | T细胞受体治疗公司 | 用于使用融合蛋白进行tcr重编程的组合物和方法 |
| CN116115629A (zh) | 2016-08-17 | 2023-05-16 | 菲克特生物科学股份有限公司 | 核酸产品及其施用方法 |
| IL292551B2 (en) | 2016-10-07 | 2023-10-01 | Tcr2 Therapeutics Inc | Preparations and methods for reprogramming T-cell receptors using fusion proteins |
| GB2604416B (en) | 2016-10-18 | 2023-03-15 | Univ Minnesota | Tumor infiltating lymphocytes and methods of therapy |
| AU2017363311A1 (en) | 2016-11-22 | 2019-06-13 | TCR2 Therapeutics Inc. | Compositions and methods for TCR reprogramming using fusion proteins |
| CA3047999A1 (en) | 2016-12-21 | 2018-06-28 | TCR2 Therapeutics Inc. | Engineered t cells for the treatment of cancer |
| US12344826B2 (en) | 2017-01-25 | 2025-07-01 | The George Washington University, A Congressionally Chartered Not-For-Profit Corporation | Apparatus and methods for in vitro preclinical human trials |
| TW201839136A (zh) | 2017-02-06 | 2018-11-01 | 瑞士商諾華公司 | 治療血色素異常症之組合物及方法 |
| WO2018154413A1 (en) * | 2017-02-22 | 2018-08-30 | Crispr Therapeutics Ag | Materials and methods for treatment of dystrophic epidermolysis bullosa (deb) and other collagen type vii alpha 1 chain (col7a1) gene related conditions or disorders |
| WO2018229226A1 (en) | 2017-06-14 | 2018-12-20 | Technische Universität Dresden | Methods and means for genetic alteration of genomes utilizing designer dna recombining enzymes |
| US20200206272A1 (en) | 2017-06-19 | 2020-07-02 | National University Corporation Hokkaido University | Treatment agent for epidermolysis bullosa |
| JP2020530307A (ja) | 2017-06-30 | 2020-10-22 | インティマ・バイオサイエンス，インコーポレーテッド | 遺伝子治療のためのアデノ随伴ウイルスベクター |
| AU2018370120C1 (en) | 2017-11-15 | 2024-05-30 | Adicet Therapeutics, Inc. | Methods for selective expansion of d3 yd T-cell populations and compositions thereof |
| CA3094345A1 (en) | 2018-04-12 | 2019-10-17 | Krystal Biotech, Inc. | Compositions and methods for the treatment of autosomal recessive congenital ichthyosis |
| WO2019204226A1 (en) | 2018-04-16 | 2019-10-24 | University Of Massachusetts | Compositions and methods for improved gene editing |
| AU2019260757B2 (en) | 2018-04-27 | 2023-09-28 | Krystal Biotech, Inc. | Recombinant nucleic acids encoding cosmetic protein(s) for aesthetic applications |
| EP4252759B1 (en) | 2018-05-11 | 2025-08-06 | Memorial Sloan Kettering Cancer Center | T cell receptors targeting pik3ca mutations and uses thereof |
| US11827892B2 (en) | 2018-06-07 | 2023-11-28 | The State Of Israel, Ministry Of Agriculture & Rural Development, Agricultural Research Organization (Aro) (Volcani Center) | Nucleic acid constructs and methods of using same |
| EP3800998A1 (en) | 2018-06-07 | 2021-04-14 | The State of Israel, Ministry of Agriculture & Rural Development, Agricultural Research Organization (ARO) (Volcani Center) | Methods of regenerating and transforming cannabis |
| JP2021535747A (ja) * | 2018-09-07 | 2021-12-23 | ウィスコンシン アラムニ リサーチ ファンデーション | ヒト多能性幹細胞からの造血前駆細胞の生成 |
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| JP2023519346A (ja) | 2020-03-27 | 2023-05-10 | メンドゥス・ベスローテン・フェンノートシャップ | 養子細胞療法の有効性を増強するための白血病由来の改変細胞のエクスビボ（ｅｘ ｖｉｖｏ）使用 |
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| JP2024504613A (ja) | 2021-01-14 | 2024-02-01 | センティ バイオサイエンシズ インコーポレイテッド | 分泌性ペイロード調節 |
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| WO2012065143A1 (en) * | 2010-11-12 | 2012-05-18 | The General Hospital Corporation | Polycomb-associated non-coding rnas |
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| HUE041436T2 (hu) * | 2009-12-10 | 2019-05-28 | Univ Minnesota | Tal-effektor-közvetített DNS-módosítás |
| CN103210087B (zh) * | 2010-09-06 | 2015-04-29 | 淡马锡生命科学研究院有限公司 | Xa10与AvrXa10之间的分子相互作用 |
| EP2758529B1 (en) | 2011-09-21 | 2019-03-20 | Sangamo Therapeutics, Inc. | Methods and compositions for regulation of transgene expression |
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2018
- 2018-10-31 US US16/176,073 patent/US10973844B2/en not_active Expired - Fee Related
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2019
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2020
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2021
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| WO2012065143A1 (en) * | 2010-11-12 | 2012-05-18 | The General Hospital Corporation | Polycomb-associated non-coding rnas |
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| US20190054111A1 (en) | 2019-02-21 |
| WO2014134412A1 (en) | 2014-09-04 |
| JP2016512960A (ja) | 2016-05-12 |
| CA2902954A1 (en) | 2014-09-04 |
| EP2961262A4 (en) | 2016-10-12 |
| JP2019089821A (ja) | 2019-06-13 |
| EP2961262B1 (en) | 2019-07-24 |
| ES2750550T3 (es) | 2020-03-26 |
| US9393257B2 (en) | 2016-07-19 |
| HK1219021A1 (en) | 2017-03-24 |
| JP6480874B2 (ja) | 2019-03-13 |
| US10973844B2 (en) | 2021-04-13 |
| US10172880B2 (en) | 2019-01-08 |
| US20210187006A1 (en) | 2021-06-24 |
| US20160367588A1 (en) | 2016-12-22 |
| EP2961262A1 (en) | 2016-01-06 |
| JP6893945B2 (ja) | 2021-06-23 |
| US20140256798A1 (en) | 2014-09-11 |
| AU2020200307A1 (en) | 2020-02-06 |
| AU2014223243A1 (en) | 2015-09-10 |
| JP2021088565A (ja) | 2021-06-10 |
| EP3567104A1 (en) | 2019-11-13 |
| NZ711254A (en) | 2021-02-26 |
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