AR122013A1 - Composiciones de virus adenoasociados compatibles entre especies y métodos para su uso - Google Patents

Composiciones de virus adenoasociados compatibles entre especies y métodos para su uso

Info

Publication number
AR122013A1
AR122013A1 ARP210101222A ARP210101222A AR122013A1 AR 122013 A1 AR122013 A1 AR 122013A1 AR P210101222 A ARP210101222 A AR P210101222A AR P210101222 A ARP210101222 A AR P210101222A AR 122013 A1 AR122013 A1 AR 122013A1
Authority
AR
Argentina
Prior art keywords
methods
adeno
associated virus
species
compatible
Prior art date
Application number
ARP210101222A
Other languages
English (en)
Inventor
Aravind Asokan
Trevor Gonzalez
Lawrence Patrick Havlik
Original Assignee
Univ Duke
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Univ Duke filed Critical Univ Duke
Publication of AR122013A1 publication Critical patent/AR122013A1/es

Links

Classifications

    • CCHEMISTRY; METALLURGY
    • C07ORGANIC CHEMISTRY
    • C07KPEPTIDES
    • C07K14/00Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • C07K14/005Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from viruses
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09Recombinant DNA-technology
    • C12N15/63Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79Vectors or expression systems specially adapted for eukaryotic hosts
    • C12N15/85Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
    • C12N15/86Viral vectors
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14122New viral proteins or individual genes, new structural or functional aspects of known viral proteins or genes
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12NMICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector

Abstract

Vectores de virus adenoasociados (AAV) que comprenden variantes de proteínas de la cápside, composiciones farmacéuticas, métodos para su elaboración y métodos para su administración a un sujeto.
ARP210101222A 2020-05-05 2021-05-05 Composiciones de virus adenoasociados compatibles entre especies y métodos para su uso AR122013A1 (es)

Applications Claiming Priority (1)

Application Number Priority Date Filing Date Title
US202063020062P 2020-05-05 2020-05-05

Publications (1)

Publication Number Publication Date
AR122013A1 true AR122013A1 (es) 2022-08-03

Family

ID=78468375

Family Applications (1)

Application Number Title Priority Date Filing Date
ARP210101222A AR122013A1 (es) 2020-05-05 2021-05-05 Composiciones de virus adenoasociados compatibles entre especies y métodos para su uso

Country Status (13)

Country Link
US (3) US20230151389A1 (es)
EP (1) EP4125977A2 (es)
JP (1) JP2023524291A (es)
KR (1) KR20230029616A (es)
CN (1) CN116096377A (es)
AR (1) AR122013A1 (es)
AU (1) AU2021268946A1 (es)
BR (1) BR112022022644A2 (es)
CA (1) CA3177869A1 (es)
IL (1) IL297577A (es)
MX (1) MX2022013963A (es)
TW (1) TW202208631A (es)
WO (1) WO2021226267A2 (es)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2024044725A2 (en) * 2022-08-24 2024-02-29 Regenxbio Inc. Recombinant adeno-associated viruses and uses thereof

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2648241T3 (es) * 2003-09-30 2017-12-29 The Trustees Of The University Of Pennsylvania Clados de virus adenoasociados (AAV), secuencias, vectores que contienen el mismo, y usos de los mismos
US10746742B2 (en) * 2014-04-25 2020-08-18 Oregon Health & Science University Methods of viral neutralizing antibody epitope mapping

Also Published As

Publication number Publication date
CA3177869A1 (en) 2021-11-11
JP2023524291A (ja) 2023-06-09
CN116096377A (zh) 2023-05-09
AU2021268946A1 (en) 2022-12-01
US20230151389A1 (en) 2023-05-18
TW202208631A (zh) 2022-03-01
KR20230029616A (ko) 2023-03-03
BR112022022644A2 (pt) 2023-01-17
WO2021226267A2 (en) 2021-11-11
EP4125977A2 (en) 2023-02-08
US20240067988A1 (en) 2024-02-29
WO2021226267A3 (en) 2021-12-16
US20240076695A1 (en) 2024-03-07
MX2022013963A (es) 2023-02-22
IL297577A (en) 2022-12-01

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