TWI848486B - 組織選擇性轉基因表現 - Google Patents

組織選擇性轉基因表現 Download PDF

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TWI848486B
TWI848486B TW111150116A TW111150116A TWI848486B TW I848486 B TWI848486 B TW I848486B TW 111150116 A TW111150116 A TW 111150116A TW 111150116 A TW111150116 A TW 111150116A TW I848486 B TWI848486 B TW I848486B
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cases
transgene
expression
selective
sequence
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TW111150116A
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Chinese (zh)
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TW202315945A (zh
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史蒂芬妮 德萊特拉
安卓 楊
思穎 陳
卡提克 瑞瑪穆斯
大衛 歐博克夫勒
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美商編碼製藥公司
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TW111150116A 2017-04-03 2018-04-03 組織選擇性轉基因表現 TWI848486B (zh)

Applications Claiming Priority (2)

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US201762480998P 2017-04-03 2017-04-03
US62/480,998 2017-04-03

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TW202315945A TW202315945A (zh) 2023-04-16
TWI848486B true TWI848486B (zh) 2024-07-11

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TW111150116A TWI848486B (zh) 2017-04-03 2018-04-03 組織選擇性轉基因表現
TW107111969A TWI808079B (zh) 2017-04-03 2018-04-03 組織選擇性轉基因表現
TW111150117A TW202315946A (zh) 2017-04-03 2018-04-03 組織選擇性轉基因表現

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US (6) US10519465B2 (https=)
EP (2) EP3607073B1 (https=)
JP (2) JP7246359B2 (https=)
KR (1) KR102604159B1 (https=)
CN (2) CN117821509A (https=)
AU (1) AU2018250161B2 (https=)
BR (1) BR112019020777A2 (https=)
CA (1) CA3058189A1 (https=)
CL (2) CL2019002805A1 (https=)
CO (1) CO2019011450A2 (https=)
EA (1) EA201992358A1 (https=)
ES (1) ES2981970T3 (https=)
IL (1) IL269767A (https=)
MA (1) MA71412A (https=)
MX (4) MX2019011772A (https=)
PL (1) PL3607073T3 (https=)
SA (1) SA519410244B1 (https=)
SG (1) SG11201909203WA (https=)
TW (3) TWI848486B (https=)
WO (1) WO2018187363A1 (https=)

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CN113966399A (zh) 2018-09-26 2022-01-21 加州理工学院 用于靶向基因疗法的腺相关病毒组合物
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WO2020097121A1 (en) * 2018-11-05 2020-05-14 Allen Institute Artificial expression constructs for selectively modulating gene expression in excitatory cortical neurons
KR20210133227A (ko) * 2019-02-05 2021-11-05 더 브로드 인스티튜트, 인코퍼레이티드 뉴런 세포 흥분성을 정상화하고 드라베 증후군을 치료하기 위한 개재뉴런-특이적 치료제
JP7624728B2 (ja) * 2019-02-25 2025-01-31 ユニバーシティ オブ マサチューセッツ Ｄｎａ結合ドメイントランスアクチベーター及びその使用
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CN115867657A (zh) 2020-05-11 2023-03-28 斯托克制药公司 用于治疗疾患和疾病的opa1反义寡聚物
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WO2022020706A1 (en) * 2020-07-24 2022-01-27 University Of Massachusetts Dna-binding domain transactivators and uses thereof
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