TW202237845A - 用於涉及去胺作用之基因體編輯之多核苷酸、組合物及方法 - Google Patents
用於涉及去胺作用之基因體編輯之多核苷酸、組合物及方法 Download PDFInfo
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| MX2021001070A (es) | 2018-07-31 | 2021-05-27 | Intellia Therapeutics Inc | Composiciones y métodos para editar el gen hidroxiácido oxidasa 1 (hao1) para tratar la hiperoxaluria primaria tipo 1 (ph1). |
| AU2019326408A1 (en) * | 2018-08-23 | 2021-03-11 | Sangamo Therapeutics, Inc. | Engineered target specific base editors |
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| IL282267B2 (en) | 2018-10-15 | 2026-03-01 | Univ Massachusetts | Programmed DNA editing by chimeric deaminase-nme2cas9 proteins |
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| EP3911735A4 (en) * | 2019-01-16 | 2023-07-12 | Beam Therapeutics, Inc. | MODIFIED IMMUNE CELLS WITH INCREASED ANTINEOPLASTIC ACTIVITY AND RESISTANCE TO IMMUNOSUPPRESSION |
| AU2020248337A1 (en) * | 2019-03-28 | 2021-11-04 | Intellia Therapeutics, Inc. | Compositions and methods for ttr gene editing and treating ATTR amyloidosis comprising a corticosteroid or use thereof |
| CN114127044A (zh) | 2019-04-25 | 2022-03-01 | 英特利亚治疗股份有限公司 | 可电离的胺类脂质和脂质纳米颗粒 |
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- 2023-07-07 CO CONC2023/0009114A patent/CO2023009114A2/es unknown
Also Published As
| Publication number | Publication date |
|---|---|
| CO2023009114A2 (es) | 2023-08-18 |
| CL2023001684A1 (es) | 2024-01-05 |
| WO2022125968A1 (en) | 2022-06-16 |
| MX2023006876A (es) | 2023-07-31 |
| CA3205000A1 (en) | 2022-06-16 |
| IL303506A (en) | 2023-08-01 |
| EP4259792A1 (en) | 2023-10-18 |
| CR20230305A (es) | 2023-11-10 |
| AU2021394998A9 (en) | 2024-05-02 |
| JP2023553935A (ja) | 2023-12-26 |
| KR20230129996A (ko) | 2023-09-11 |
| AU2021394998A1 (en) | 2023-06-29 |
| US20240002820A1 (en) | 2024-01-04 |
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