TW202117017A - 人類心肌病的ａａｖ心臟基因療法 - Google Patents
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| US201962876540P | 2019-07-19 | 2019-07-19 | |
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| TW109124287A TW202117017A (zh) | 2019-07-19 | 2020-07-17 | 人類心肌病的ａａｖ心臟基因療法 |
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| MX2023007602A (es) * | 2020-12-23 | 2023-09-21 | Univ Florida | Mayor eficiencia del empaquetamiento de vectores para terapia genica cardiaca. |
| US20250144243A1 (en) | 2022-01-25 | 2025-05-08 | The Trustees Of The University Of Pennsylvania | Aav capsids for improved heart transduction and detargeting of liver |
| WO2024130070A2 (en) | 2022-12-17 | 2024-06-20 | The Trustees Of The University Of Pennsylvania | Recombinant aav capsids with cardiac- and skeletal muscle- specific targeting motifs and uses thereof |
| KR20250135916A (ko) | 2022-12-17 | 2025-09-15 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | 심장 및 골격근 특이적 표적화 모티프를 갖는 재조합 aav 돌연변이체 벡터 및 이를 포함하는 조성물 |
| AR133098A1 (es) | 2023-06-29 | 2025-08-27 | Univ Pennsylvania | Aav mutante con motivos dirigidos al sistema nervioso central y composiciones que lo contienen |
| WO2025106661A1 (en) | 2023-11-14 | 2025-05-22 | The Trustees Of The University Of Pennsylvania | Compositions with cardiac and skeletal musclespecific targeting motifs and uses thereof |
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| DE19915485A1 (de) * | 1999-04-07 | 2000-10-19 | Hugo A Katus | Therapie der Herzinsuffizienz |
| CA2412847A1 (en) * | 2000-06-30 | 2002-01-10 | Collateral Therapeutics, Inc. | Dual recombinant gene therapy compositions and methods of use |
| WO2008054713A2 (en) * | 2006-10-30 | 2008-05-08 | Thomas Jefferson University | Tissue specific gene therapy treatment |
| EP2295072A1 (en) * | 2009-09-15 | 2011-03-16 | Max-Delbrück-Centrum für Molekulare Medizin (MDC) | Use of ARC for inhibiting cell death during liver failure |
| CA2925691A1 (en) * | 2013-10-01 | 2015-04-09 | Ruprecht-Karls-Univeristat Heidelberg | S100 based treatment of cardiac power failure |
| EP3452101A2 (en) * | 2016-05-04 | 2019-03-13 | CureVac AG | Rna encoding a therapeutic protein |
| EP3694996A1 (en) * | 2017-10-12 | 2020-08-19 | Universität Heidelberg | Kcnk3-based gene therapy of cardiac arrhythmia |
| US20210260215A1 (en) * | 2018-06-08 | 2021-08-26 | University Of Florida Research Foundation, Incorporated | Aav cardiac gene therapy for cardiomyopathy |
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| KR20220034801A (ko) | 2022-03-18 |
| CA3142534A1 (en) | 2021-01-28 |
| JP2022541793A (ja) | 2022-09-27 |
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| EP3999074A1 (en) | 2022-05-25 |
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| CN114206351A (zh) | 2022-03-18 |
| IL289667A (en) | 2022-03-01 |
| MX2022000767A (es) | 2022-04-25 |
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