TW202117017A - 人類心肌病的ａａｖ心臟基因療法 - Google Patents
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| US201962876540P | 2019-07-19 | 2019-07-19 | |
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| WO2023147304A1 (en) | 2022-01-25 | 2023-08-03 | The Trustees Of The University Of Pennsylvania | Aav capsids for improved heart transduction and detargeting of liver |
| WO2024130070A2 (en) | 2022-12-17 | 2024-06-20 | The Trustees Of The University Of Pennsylvania | Recombinant aav capsids with cardiac- and skeletal muscle- specific targeting motifs and uses thereof |
| WO2024130067A2 (en) | 2022-12-17 | 2024-06-20 | The Trustees Of The University Of Pennsylvania | Recombinant aav mutant vectors with cardiac and skeletal muscle-specific targeting motifs and compositions containing same |
| AR133098A1 (es) | 2023-06-29 | 2025-08-27 | Univ Pennsylvania | Aav mutante con motivos dirigidos al sistema nervioso central y composiciones que lo contienen |
| WO2025106661A1 (en) | 2023-11-14 | 2025-05-22 | The Trustees Of The University Of Pennsylvania | Compositions with cardiac and skeletal musclespecific targeting motifs and uses thereof |
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| CA2412847A1 (en) * | 2000-06-30 | 2002-01-10 | Collateral Therapeutics, Inc. | Dual recombinant gene therapy compositions and methods of use |
| US8383601B2 (en) * | 2006-10-30 | 2013-02-26 | Thomas Jefferson University | Tissue specific gene therapy treatment |
| EP2295072A1 (en) * | 2009-09-15 | 2011-03-16 | Max-Delbrück-Centrum für Molekulare Medizin (MDC) | Use of ARC for inhibiting cell death during liver failure |
| WO2015049277A1 (en) * | 2013-10-01 | 2015-04-09 | Ruprecht-Karls-Universität Heidelberg | S100 based treatment of cardiac power failure |
| WO2017191274A2 (en) * | 2016-05-04 | 2017-11-09 | Curevac Ag | Rna encoding a therapeutic protein |
| WO2019073058A1 (en) * | 2017-10-12 | 2019-04-18 | Universität Heidelberg | GENE THERAPY OF CARDIAC ARRHYTHMIA BASED ON KCNK3 |
| SG11202011061SA (en) * | 2018-06-08 | 2020-12-30 | University Of Florida Research Foundation Incorporated | Aav cardiac gene therapy for cardiomyopathy |
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| EP3999074A1 (en) | 2022-05-25 |
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| CL2022000115A1 (es) | 2022-10-07 |
| BR112022000898A2 (pt) | 2022-06-07 |
| AR122289A1 (es) | 2022-08-31 |
| JP2022541793A (ja) | 2022-09-27 |
| MX2022000767A (es) | 2022-04-25 |
| IL289667A (en) | 2022-03-01 |
| KR20220034801A (ko) | 2022-03-18 |
| CN114206351A (zh) | 2022-03-18 |
| WO2021016126A1 (en) | 2021-01-28 |
| CO2022001686A2 (es) | 2022-03-29 |
| AU2020316339A1 (en) | 2021-11-18 |
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