TW202108760A - 有用於治療異染性白質失養症之組成物 - Google Patents

有用於治療異染性白質失養症之組成物 Download PDF

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TW202108760A
TW202108760A TW109114778A TW109114778A TW202108760A TW 202108760 A TW202108760 A TW 202108760A TW 109114778 A TW109114778 A TW 109114778A TW 109114778 A TW109114778 A TW 109114778A TW 202108760 A TW202108760 A TW 202108760A
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sequence
seq
vector
raav
harsa
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TW109114778A
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茱麗葉 豪杜司
詹姆士Ｍ 威爾森
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賓州大學委員會
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TW109114778A 2019-05-03 2020-05-04 有用於治療異染性白質失養症之組成物 TW202108760A (zh)

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US201962843091P 2019-05-03 2019-05-03
US62/843,091 2019-05-03

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US (2) US12338451B2 (https=)
EP (1) EP3962454A4 (https=)
JP (1) JP7715640B2 (https=)
KR (1) KR20220020261A (https=)
CN (1) CN114072129A (https=)
AR (1) AR118850A1 (https=)
AU (1) AU2020270421A1 (https=)
BR (1) BR112021021908A2 (https=)
CA (1) CA3135539A1 (https=)
CL (1) CL2021002881A1 (https=)
CO (1) CO2021016323A2 (https=)
IL (1) IL287715A (https=)
MX (1) MX2021013420A (https=)
PE (1) PE20220930A1 (https=)
SG (1) SG11202111867XA (https=)
TW (1) TW202108760A (https=)
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JP2025521111A (ja) * 2022-05-16 2025-07-08 ジェンザイム・コーポレーション 異染性白質ジストロフィーを治療する方法
WO2024036250A2 (en) * 2022-08-10 2024-02-15 Homology Medicines, Inc. Adeno-associated virus compositions for arsa gene transfer and methods of use thereof
WO2024079361A1 (en) * 2022-10-14 2024-04-18 Neuway Pharma Gmbh A PROTEIN- OR PEPTIDE-BASED CAPSULE (PPC), PREFERABLY A VLP, LOADED WITH A MESSENGER RNA (mRNA) AND A METHOD OF PRODUCTION AND PURIFICATION THEREOF
CN118389675B (zh) * 2024-05-27 2025-06-27 南方医科大学珠江医院 芳香族氨基酸脱羧酶作为标志物在肝性脑病的检测产品中的应用

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