TW201814044A - 多核苷酸、載體、藥物組成物及其等之用途、以及載體獲得方法 - Google Patents
多核苷酸、載體、藥物組成物及其等之用途、以及載體獲得方法 Download PDFInfo
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Cited By (1)
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| TWI841566B (zh) * | 2018-05-30 | 2024-05-11 | 西班牙商艾斯提夫製藥股份有限公司 | 用於治療黏多醣症 iv a 型之腺相關病毒載體 |
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| US9309534B2 (en) | 2010-07-12 | 2016-04-12 | Universidad Autonoma De Barcelona | Gene therapy composition for use in diabetes treatment |
| EP2692868A1 (en) | 2012-08-02 | 2014-02-05 | Universitat Autònoma De Barcelona | Adeno-associated viral (AAV) vectors useful for transducing adipose tissue |
| JP2016523835A (ja) * | 2013-05-15 | 2016-08-12 | リージェンツ オブ ザ ユニバーシティ オブ ミネソタ | 中枢神経系へのアデノ随伴ウイルスを介した遺伝子導入 |
| US10973931B2 (en) | 2014-09-16 | 2021-04-13 | Universitat Autònoma De Barcelona | Adeno-associated viral vectors for the gene therapy of metabolic diseases |
| US11085055B2 (en) | 2014-12-05 | 2021-08-10 | Universitat Autonoma De Barcelona | Viral vectors for the treatment of diabetes |
| EP3242945B1 (en) | 2015-01-07 | 2021-09-01 | Universitat Autònoma de Barcelona | Single-vector gene construct comprising insulin and glucokinase genes |
| KR102765034B1 (ko) | 2017-05-24 | 2025-02-11 | 유니버시타트 아우토노마 데 바르셀로나 | 섬유아세포 성장 인자 21 (ｆｇｆ21) 코딩 서열을 포함하는 바이러스 발현 컨스트럭트 |
| IL278213B2 (en) | 2018-04-27 | 2026-04-01 | Rocket Pharmaceuticals Ltd | A gene therapy vector encoding an e3 ubiquitin protein ligase (park2) and use thereof in treating or inhibiting the onset of parkinson’s disease (pd) |
| EP3820537A4 (en) * | 2018-07-12 | 2022-04-13 | Spacecraft Seven, LLC | GENE THERAPY VECTORS FOR TREATMENT OF DANON DISEASE |
| IL283452B2 (en) | 2018-11-26 | 2026-04-01 | Univ Barcelona Autonoma | FIBROBLAST GROWTH FACTOR 21 (FGF21)-BASED GENE THERAPY |
| ES2948620T3 (es) | 2019-07-10 | 2023-09-14 | Masonic Medical Res Laboratory | Vgll4 con elemento regulador CIS de UCP-1 y método de uso del mismo |
| CN111718947B (zh) * | 2020-06-18 | 2022-08-23 | 舒泰神（北京）生物制药股份有限公司 | 用于治疗ⅲa或ⅲb型粘多糖贮积症的腺相关病毒载体及用途 |
| WO2022032226A1 (en) | 2020-08-07 | 2022-02-10 | Spacecraft Seven, Llc | Plakophilin-2 (pkp2) gene therapy using aav vector |
| CN114480454B (zh) * | 2020-10-27 | 2024-03-29 | 华东理工大学 | 用于治疗粘多糖贮积症ⅱ型的腺相关病毒载体、药物及其应用 |
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| US7232670B2 (en) * | 2001-09-28 | 2007-06-19 | St. Jude Children's Research Hospital | Targeting proteins to cells expressing mannose receptors via expression in insect cells |
| CN110496230A (zh) * | 2003-02-11 | 2019-11-26 | 夏尔人类遗传性治疗公司 | 使用甲酰-甘氨酸生成酶(fge)对多种硫酸酯酶缺乏症和其它病症进行诊断和治疗 |
| EP2394667A1 (en) * | 2010-06-10 | 2011-12-14 | Laboratorios Del Dr. Esteve, S.A. | Vectors and sequences for the treatment of diseases |
| SG10201604810UA (en) * | 2012-02-07 | 2016-08-30 | Global Bio Therapeutics Inc | Compartmentalized method of nucleic acid delivery and compositions and uses thereof |
| CN105916990B (zh) * | 2013-08-02 | 2020-02-04 | 巴塞罗那自治大学 | 用于转导脂肪组织的腺相关病毒载体 |
| WO2015060722A1 (en) * | 2013-10-24 | 2015-04-30 | Uniqure Ip B.V. | Aav-5 pseudotyped vector for gene therapy for neurological diseases |
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| SG11201609314XA (en) | 2014-05-14 | 2016-12-29 | Esteve Labor Dr | Adenoassociated virus vectors for the treatment of lysosomal storage disorders |
| EA201791803A1 (ru) * | 2015-02-10 | 2017-11-30 | Джензим Корпорейшн | Улучшенная доставка вирусных частиц в полосатое тело и кору больших полушарий |
| US9981021B1 (en) * | 2015-04-09 | 2018-05-29 | Kinetiq, Inc. | Subcutaneous therapeutic enzyme formulations, uses, and methods for generating thereof |
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Cited By (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| TWI841566B (zh) * | 2018-05-30 | 2024-05-11 | 西班牙商艾斯提夫製藥股份有限公司 | 用於治療黏多醣症 iv a 型之腺相關病毒載體 |
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| WO2018060097A1 (en) | 2018-04-05 |
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| EP3519569B1 (en) | 2020-12-02 |
| US11338046B2 (en) | 2022-05-24 |
| JP2019528793A (ja) | 2019-10-17 |
| AU2017333336B2 (en) | 2023-11-09 |
| CN109863243A (zh) | 2019-06-07 |
| JP7059285B2 (ja) | 2022-04-25 |
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