RU2730677C2 - Соединение для модуляции экспрессии гена c9orf72 и его применение - Google Patents

Соединение для модуляции экспрессии гена c9orf72 и его применение Download PDF

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RU2730677C2
RU2730677C2 RU2015117680A RU2015117680A RU2730677C2 RU 2730677 C2 RU2730677 C2 RU 2730677C2 RU 2015117680 A RU2015117680 A RU 2015117680A RU 2015117680 A RU2015117680 A RU 2015117680A RU 2730677 C2 RU2730677 C2 RU 2730677C2
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modified
modified oligonucleotide
c9orf72
sugar
compound
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RU2015117680A (ru
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Франк С. БЕННЕТТ
Сьюзан М. Фрайер
Эрик Е. СВЭЙЗИ
Франк РИГО
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Ионис Фармасьютикалз, Инк.
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    • C12N2310/34Spatial arrangement of the modifications
    • C12N2310/346Spatial arrangement of the modifications having a combination of backbone and sugar modifications

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RU2015117680A 2012-10-15 2013-10-15 Соединение для модуляции экспрессии гена c9orf72 и его применение RU2730677C2 (ru)

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US201261714132P 2012-10-15 2012-10-15
US61/714,132 2012-10-15
PCT/US2013/065073 WO2014062691A2 (en) 2012-10-15 2013-10-15 Compositions for modulating c9orf72 expression

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EP (1) EP2906258A4 (https=)
JP (3) JP6570447B2 (https=)
KR (1) KR20150070278A (https=)
CN (2) CN110951731A (https=)
AU (2) AU2013331434B2 (https=)
BR (1) BR112015008399A8 (https=)
CA (1) CA2888486A1 (https=)
HK (1) HK1212597A1 (https=)
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