RU2452368C2 - Медленная внутрижелудочковая доставка - Google Patents
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- RU2452368C2 RU2452368C2 RU2008136196/14A RU2008136196A RU2452368C2 RU 2452368 C2 RU2452368 C2 RU 2452368C2 RU 2008136196/14 A RU2008136196/14 A RU 2008136196/14A RU 2008136196 A RU2008136196 A RU 2008136196A RU 2452368 C2 RU2452368 C2 RU 2452368C2
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| RU2692251C2 (ru) * | 2013-05-15 | 2019-06-24 | Риджентс Оф Зэ Юниверсити Оф Миннесота | Опосредованный аденоассоциированным вирусом перенос генов в центральную нервную систему |
| US10912804B2 (en) | 2007-02-23 | 2021-02-09 | University Of Florida Research Foundation, Incorporated | Compositions and methods for treating diseases |
| US11261460B2 (en) | 2007-02-23 | 2022-03-01 | University Of Florida Research Foundation, Incorporated | Compositions and methods for treating diseases |
| RU2801511C1 (ru) * | 2013-05-15 | 2023-08-09 | Риджентс Оф Зэ Юниверсити Оф Миннесота | Опосредованный аденоассоциированным вирусом перенос генов в центральную нервную систему |
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| DK1988823T3 (en) * | 2006-02-09 | 2018-12-03 | Genzyme Corp | SLOW INTRAVENTRICULAR ADMINISTRATION |
| PL3252161T3 (pl) | 2007-06-06 | 2022-03-07 | Genzyme Corporation | Terapia genowa dla lizosomalnych chorób spichrzeniowych |
| EP2167071B1 (en) * | 2007-06-13 | 2020-03-18 | Wayne State University Board Of Governors | A baclofen solution for low-volume therapeutic delivery |
| CN102549152B (zh) | 2009-07-31 | 2015-11-25 | 帕克斯瓦克斯股份有限公司 | 基于腺病毒的载体 |
| SI3998078T1 (sl) | 2009-08-28 | 2026-02-27 | Genzyme Corporation | Encimsko nadomestno zdravljenje z naraščajočim odmerkom za zdravljenje pomanjkanja kisle sfingomielinaze |
| RS62620B1 (sr) | 2010-06-25 | 2021-12-31 | Shire Human Genetic Therapies | Metode i kompozicije za isporuku cns akrilsulfataze a |
| GB201508025D0 (en) | 2015-05-11 | 2015-06-24 | Ucl Business Plc | Fabry disease gene therapy |
| TWI835747B (zh) | 2017-09-22 | 2024-03-21 | 賓州大學委員會 | 用於治療黏多醣病 ii 型之基因治療 |
| US12018087B2 (en) | 2018-08-02 | 2024-06-25 | Dyne Therapeutics, Inc. | Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject |
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| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US10912804B2 (en) | 2007-02-23 | 2021-02-09 | University Of Florida Research Foundation, Incorporated | Compositions and methods for treating diseases |
| US11261460B2 (en) | 2007-02-23 | 2022-03-01 | University Of Florida Research Foundation, Incorporated | Compositions and methods for treating diseases |
| RU2692251C2 (ru) * | 2013-05-15 | 2019-06-24 | Риджентс Оф Зэ Юниверсити Оф Миннесота | Опосредованный аденоассоциированным вирусом перенос генов в центральную нервную систему |
| RU2801511C1 (ru) * | 2013-05-15 | 2023-08-09 | Риджентс Оф Зэ Юниверсити Оф Миннесота | Опосредованный аденоассоциированным вирусом перенос генов в центральную нервную систему |
| US12121567B2 (en) | 2013-05-15 | 2024-10-22 | Regents Of The University Of Minnesota | Methods to treat mucopolysaccharidosis type II or deficiency in iduronate-2-sulfatase using a recombinant adeno-associated virus (AAV) vector encoding iduronate-2-sulfatase |
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