NL300843I2 - - Google Patents

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Publication number
NL300843I2
NL300843I2 NL300843C NL300843C NL300843I2 NL 300843 I2 NL300843 I2 NL 300843I2 NL 300843 C NL300843 C NL 300843C NL 300843 C NL300843 C NL 300843C NL 300843 I2 NL300843 I2 NL 300843I2
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NL
Netherlands
Application number
NL300843C
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Amicus Therapeutics Inc
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Publication date
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First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=38723987&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=NL300843(I2) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Amicus Therapeutics Inc filed Critical Amicus Therapeutics Inc
Publication of NL300843I2 publication Critical patent/NL300843I2/nl

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Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445Non condensed piperidines, e.g. piperocaine
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445Non condensed piperidines, e.g. piperocaine
    • A61K31/45Non condensed piperidines, e.g. piperocaine having oxo groups directly attached to the heterocyclic ring, e.g. cycloheximide
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K45/00Medicinal preparations containing active ingredients not provided for in groups A61K31/00 - A61K41/00
    • A61K45/06Mixtures of active ingredients without chemical characterisation, e.g. antiphlogistics and cardiaca
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/0012Galenical forms characterised by the site of application
    • A61K9/0053Mouth and digestive tract, i.e. intraoral and peroral administration
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K9/00Medicinal preparations characterised by special physical form
    • A61K9/48Preparations in capsules, e.g. of gelatin, of chocolate
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P13/00Drugs for disorders of the urinary system
    • A61P13/12Drugs for disorders of the urinary system of the kidneys
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00Drugs for disorders of the metabolism
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00Drugs for disorders of the cardiovascular system
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00Drugs for disorders of the cardiovascular system
    • A61P9/10Drugs for disorders of the cardiovascular system for treating ischaemic or atherosclerotic diseases, e.g. antianginal drugs, coronary vasodilators, drugs for myocardial infarction, retinopathy, cerebrovascula insufficiency, renal arteriosclerosis
    • CCHEMISTRY; METALLURGY
    • C07ORGANIC CHEMISTRY
    • C07DHETEROCYCLIC COMPOUNDS
    • C07D211/00Heterocyclic compounds containing hydrogenated pyridine rings, not condensed with other rings
    • C07D211/04Heterocyclic compounds containing hydrogenated pyridine rings, not condensed with other rings with only hydrogen or carbon atoms directly attached to the ring nitrogen atom
    • C07D211/06Heterocyclic compounds containing hydrogenated pyridine rings, not condensed with other rings with only hydrogen or carbon atoms directly attached to the ring nitrogen atom having no double bonds between ring members or between ring members and non-ring members
    • C07D211/36Heterocyclic compounds containing hydrogenated pyridine rings, not condensed with other rings with only hydrogen or carbon atoms directly attached to the ring nitrogen atom having no double bonds between ring members or between ring members and non-ring members with hetero atoms or with carbon atoms having three bonds to hetero atoms with at the most one bond to halogen, e.g. ester or nitrile radicals, directly attached to ring carbon atoms
    • C07D211/40Oxygen atoms
    • C07D211/44Oxygen atoms attached in position 4
    • C07D211/46Oxygen atoms attached in position 4 having a hydrogen atom as the second substituent in position 4
    • GPHYSICS
    • G01MEASURING; TESTING
    • G01NINVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N33/00Investigating or analysing materials by specific methods not covered by groups G01N1/00 - G01N31/00
    • G01N33/48Biological material, e.g. blood, urine; Haemocytometers
    • G01N33/50Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing
    • G01N33/5005Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing involving human or animal cells
    • G01N33/5094Chemical analysis of biological material, e.g. blood, urine; Testing involving biospecific ligand binding methods; Immunological testing involving human or animal cells for blood cell populations
    • GPHYSICS
    • G01MEASURING; TESTING
    • G01NINVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2333/00Assays involving biological materials from specific organisms or of a specific nature
    • G01N2333/90Enzymes; Proenzymes
    • G01N2333/914Hydrolases (3)
    • G01N2333/924Hydrolases (3) acting on glycosyl compounds (3.2)
    • GPHYSICS
    • G01MEASURING; TESTING
    • G01NINVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2333/00Assays involving biological materials from specific organisms or of a specific nature
    • G01N2333/90Enzymes; Proenzymes
    • G01N2333/914Hydrolases (3)
    • G01N2333/924Hydrolases (3) acting on glycosyl compounds (3.2)
    • G01N2333/94Hydrolases (3) acting on glycosyl compounds (3.2) acting on alpha-galactose-glycoside bonds, e.g. alpha-galactosidase
    • GPHYSICS
    • G01MEASURING; TESTING
    • G01NINVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2800/00Detection or diagnosis of diseases
    • G01N2800/04Endocrine or metabolic disorders
    • GPHYSICS
    • G01MEASURING; TESTING
    • G01NINVESTIGATING OR ANALYSING MATERIALS BY DETERMINING THEIR CHEMICAL OR PHYSICAL PROPERTIES
    • G01N2800/00Detection or diagnosis of diseases
    • G01N2800/52Predicting or monitoring the response to treatment, e.g. for selection of therapy based on assay results in personalised medicine; Prognosis

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • General Health & Medical Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Animal Behavior & Ethology (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Engineering & Computer Science (AREA)
  • Organic Chemistry (AREA)
  • Epidemiology (AREA)
  • Immunology (AREA)
  • Urology & Nephrology (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Hematology (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Molecular Biology (AREA)
  • Biomedical Technology (AREA)
  • Cell Biology (AREA)
  • Tropical Medicine & Parasitology (AREA)
  • Pathology (AREA)
  • General Physics & Mathematics (AREA)
  • Biochemistry (AREA)
  • Ecology (AREA)
  • Analytical Chemistry (AREA)
  • Physics & Mathematics (AREA)
  • Food Science & Technology (AREA)
  • Biotechnology (AREA)
  • Microbiology (AREA)
  • Cardiology (AREA)
  • Heart & Thoracic Surgery (AREA)
  • Physiology (AREA)
  • Nutrition Science (AREA)
  • Diabetes (AREA)
  • Obesity (AREA)
  • Vascular Medicine (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
NL300843C 2006-05-16 2016-11-11 NL300843I2 (nl)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US80108906P 2006-05-16 2006-05-16
US85363106P 2006-10-23 2006-10-23

Publications (1)

Publication Number Publication Date
NL300843I2 true NL300843I2 (nl) 2016-12-21

Family

ID=38723987

Family Applications (1)

Application Number Title Priority Date Filing Date
NL300843C NL300843I2 (nl) 2006-05-16 2016-11-11

Country Status (18)

Country Link
US (9) US7851143B2 (nl)
EP (5) EP2024745B1 (nl)
JP (6) JP2009537149A (nl)
AU (1) AU2007253900A1 (nl)
CA (1) CA2652553C (nl)
CY (3) CY1115180T1 (nl)
DK (2) DK2533050T6 (nl)
ES (3) ES2573498T3 (nl)
HK (3) HK1178975A1 (nl)
HU (2) HUE027569T2 (nl)
LT (1) LTC2787345I2 (nl)
LU (1) LU93312I2 (nl)
MX (2) MX351004B (nl)
NL (1) NL300843I2 (nl)
PL (2) PL2533050T6 (nl)
PT (1) PT2533050E (nl)
SI (2) SI2533050T1 (nl)
WO (1) WO2007137072A2 (nl)

Families Citing this family (30)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PL2533050T6 (pl) 2006-05-16 2016-05-31 Amicus Therapeutics Inc Możliwości leczenia choroby Fabry'ego
CA2685332A1 (en) * 2007-04-26 2008-11-06 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
US9999618B2 (en) 2007-04-26 2018-06-19 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
US20110152319A1 (en) * 2008-02-12 2011-06-23 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
DK2946785T3 (en) * 2008-02-12 2019-02-18 Amicus Therapeutics Inc PROCEDURE FOR PREVENTING RESPONSE TO DISEASES OF PHARMACOLOGICAL CHAPERONE TREATMENT
MX2010009875A (es) * 2008-03-12 2010-11-26 Amicus Therapeutics Inc Ensayos para diagnosticar y evaluar opciones de tratamiento para enfermedad de pompe.
JP5739898B2 (ja) * 2009-11-17 2015-06-24 ベイラー リサーチ インスティテュートBaylor Research Institute 心疾患マーカーとしての尿中トリアオシルセラミド(gb3)
WO2011109448A1 (en) * 2010-03-05 2011-09-09 Baylor Research Institute Involvement of androgen/androgen receptor pathway in fabry disease
EP3698792A1 (en) * 2011-03-11 2020-08-26 Amicus Therapeutics, Inc. Dosing regimens for the treatment of fabry disease
EP2707101B1 (en) 2011-05-12 2019-02-13 Proteostasis Therapeutics, Inc. Proteostasis regulators
KR102076585B1 (ko) * 2011-12-22 2020-02-12 센토제너 아이피 게엠베하 리소좀 효소를 재배열하는 능력을 갖는 화합물 및 암브록솔 및/또는 암브록솔의 유도체의 조합물
JP2015504919A (ja) 2012-01-25 2015-02-16 プロテオステイシス セラピューティクス,インコーポレイテッド プロテアソーム活性を調節する化合物
WO2014127038A1 (en) * 2013-02-12 2014-08-21 Baylor Research Institute Methods and compositions related to calcium homeostasis and fabry disease
RU2685269C2 (ru) * 2013-12-23 2019-04-17 БКН Пептидес, С.А. Аналоги бикалутамида или (s)-бикалутамид в качестве активирующих экзоцитоз соединений для применения в лечении расстройства лизосомного накопления или гликогеноза
US9675627B2 (en) * 2014-04-14 2017-06-13 Amicus Therapeutics, Inc. Dosing regimens for treating and/or preventing cerebral amyloidoses
CA2955297A1 (en) 2014-07-25 2016-01-28 Shire Human Genetic Therapies, Inc. Crystal structure of human four-phosphate adaptor protein 2 glycolipid transfer protein like domain
GB201508025D0 (en) 2015-05-11 2015-06-24 Ucl Business Plc Fabry disease gene therapy
US20190183869A1 (en) * 2016-07-19 2019-06-20 Amicus Therapeutics, Inc. Treatment of fabry disease in ert-naïve and ert-experienced patients
US11335461B1 (en) 2017-03-06 2022-05-17 Cerner Innovation, Inc. Predicting glycogen storage diseases (Pompe disease) and decision support
CA3224537A1 (en) 2017-05-30 2018-12-06 Amicus Therapeutics, Inc. Methods of treating fabry patients having renal impairment
CN117357524A (zh) * 2017-05-30 2024-01-09 阿米库斯治疗学公司 治疗具有肾损害的法布里患者的方法
US11923048B1 (en) 2017-10-03 2024-03-05 Cerner Innovation, Inc. Determining mucopolysaccharidoses and decision support tool
AU2019217868A1 (en) 2018-02-06 2020-10-01 Amicus Therapeutics, Inc. Use of migalastat for treating fabry disease in pregnant patients
DK3749308T3 (da) * 2018-02-06 2024-01-22 Amicus Therapeutics Inc Behandling af patienter med klassisk fabrys sygdom med migalastat
EP3814336A1 (en) 2018-06-27 2021-05-05 Proteostasis Therapeutics, Inc. Proteasome activity enhancing compounds
KR20210024588A (ko) 2018-06-27 2021-03-05 프로테오스타시스 테라퓨틱스, 인크. 프로테아좀 활성 증진 화합물
WO2020023390A1 (en) 2018-07-25 2020-01-30 Modernatx, Inc. Mrna based enzyme replacement therapy combined with a pharmacological chaperone for the treatment of lysosomal storage disorders
EP3895708A3 (en) 2019-08-07 2022-01-19 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene
US11191827B1 (en) * 2020-12-09 2021-12-07 Tevogen Bio Inc. COVID-19 peptide specific T-cells and methods of treating and preventing COVID-19
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same

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DK2946785T3 (en) 2008-02-12 2019-02-18 Amicus Therapeutics Inc PROCEDURE FOR PREVENTING RESPONSE TO DISEASES OF PHARMACOLOGICAL CHAPERONE TREATMENT
US20110152319A1 (en) 2008-02-12 2011-06-23 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
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JP5739898B2 (ja) 2009-11-17 2015-06-24 ベイラー リサーチ インスティテュートBaylor Research Institute 心疾患マーカーとしての尿中トリアオシルセラミド(gb3)
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US10155027B2 (en) 2012-07-17 2018-12-18 Amicus Therapeutics, Inc. Alpha-galactosidase A and 1-deoxygalactonojirimycin co-formulation for the treatment of fabry disease
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US20190183869A1 (en) 2016-07-19 2019-06-20 Amicus Therapeutics, Inc. Treatment of fabry disease in ert-naïve and ert-experienced patients
US11357834B2 (en) 2017-01-10 2022-06-14 Amicus Therapeutics, Inc. Recombinant α-galactosidase A for treatment of Fabry disease
CA3224537A1 (en) 2017-05-30 2018-12-06 Amicus Therapeutics, Inc. Methods of treating fabry patients having renal impairment
WO2019017938A1 (en) 2017-07-19 2019-01-24 Amicus Therapeutics, Inc. TREATMENT OF FABRY'S DISEASE IN PATIENTS WITHOUT SUBSTITUTED ENZYMATIC THERAPY (TES) AND PATIENTS SUBJECT TO TES
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AU2019217868A1 (en) 2018-02-06 2020-10-01 Amicus Therapeutics, Inc. Use of migalastat for treating fabry disease in pregnant patients
DK3749308T3 (da) 2018-02-06 2024-01-22 Amicus Therapeutics Inc Behandling af patienter med klassisk fabrys sygdom med migalastat
KR20210046729A (ko) 2018-08-20 2021-04-28 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 돌연변이를 갖는 환자에서 파브리 질병을 치료하는 방법
US20220313670A1 (en) 2019-06-11 2022-10-06 Amicus Therapeutics, Inc. Methods Of Treating Fabry Disease In Patients Having Renal Impairment
EP3895708A3 (en) 2019-08-07 2022-01-19 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene

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Publication number Publication date
US10406143B2 (en) 2019-09-10
CA2652553A1 (en) 2007-11-29
JP2009537149A (ja) 2009-10-29
SI2533050T1 (sl) 2014-07-31
US10383864B2 (en) 2019-08-20
EP2024745A4 (en) 2010-03-17
MX2008014679A (es) 2009-04-14
EP2787345A1 (en) 2014-10-08
EP2533050A1 (en) 2012-12-12
US20180325881A1 (en) 2018-11-15
JP2013100307A (ja) 2013-05-23
JP6800176B2 (ja) 2020-12-16
JP2016006088A (ja) 2016-01-14
US20180250279A1 (en) 2018-09-06
LU93312I2 (fr) 2017-01-26
DK2533050T3 (da) 2014-06-02
EP3457135A1 (en) 2019-03-20
US7851143B2 (en) 2010-12-14
JP6026268B2 (ja) 2016-11-16
US20190388409A1 (en) 2019-12-26
US20150238474A1 (en) 2015-08-27
US20220160690A1 (en) 2022-05-26
ES2464527T7 (es) 2015-09-14
CY1117656T1 (el) 2017-05-17
US9987263B2 (en) 2018-06-05
PL2787345T3 (pl) 2016-08-31
EP2955520A1 (en) 2015-12-16
WO2007137072A3 (en) 2008-10-16
EP2955520B1 (en) 2018-10-31
LTC2787345I2 (lt) 2017-10-10
CY2016040I2 (el) 2017-06-28
EP2024745B1 (en) 2015-07-08
PL2533050T3 (pl) 2014-08-29
US20120220632A1 (en) 2012-08-30
HUS1600048I1 (hu) 2017-01-30
US20080056994A1 (en) 2008-03-06
LTPA2016033I1 (lt) 2016-12-12
HK1178975A1 (en) 2013-09-19
CY1115180T1 (el) 2016-12-14
ES2573498T3 (es) 2016-06-08
HUE027569T2 (en) 2016-10-28
ES2464527T3 (es) 2014-06-03
US9000011B2 (en) 2015-04-07
PT2533050E (pt) 2014-05-26
EP2533050B3 (en) 2015-06-24
JP2020196717A (ja) 2020-12-10
JP2023027053A (ja) 2023-03-01
CY2016040I1 (el) 2017-06-28
US20110104727A1 (en) 2011-05-05
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ES2464527T9 (es) 2015-07-24
MX351004B (es) 2017-09-26
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SI2787345T1 (sl) 2016-08-31
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HK1129458A1 (en) 2009-11-27
US20170042868A1 (en) 2017-02-16
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