KR20220139352A - 칼리크레인(klkb1) 유전자 편집을 위한 조성물 및 방법 - Google Patents

칼리크레인(klkb1) 유전자 편집을 위한 조성물 및 방법 Download PDF

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KR20220139352A
KR20220139352A KR1020227030659A KR20227030659A KR20220139352A KR 20220139352 A KR20220139352 A KR 20220139352A KR 1020227030659 A KR1020227030659 A KR 1020227030659A KR 20227030659 A KR20227030659 A KR 20227030659A KR 20220139352 A KR20220139352 A KR 20220139352A
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guide
rna
sequence
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쇼부 오다테
제시카 린 세이처
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인텔리아 테라퓨틱스, 인크.
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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Enzymes And Modification Thereof (AREA)
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KR1020227030659A 2020-02-07 2021-02-05 칼리크레인(klkb1) 유전자 편집을 위한 조성물 및 방법 Pending KR20220139352A (ko)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202062971906P 2020-02-07 2020-02-07
US62/971,906 2020-02-07
US202062981965P 2020-02-26 2020-02-26
US62/981,965 2020-02-26
US202063019076P 2020-05-01 2020-05-01
US63/019,076 2020-05-01
PCT/US2021/016730 WO2021158858A1 (en) 2020-02-07 2021-02-05 Compositions and methods for kallikrein ( klkb1) gene editing

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Publication Number Publication Date
KR20220139352A true KR20220139352A (ko) 2022-10-14

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KR1020227030659A Pending KR20220139352A (ko) 2020-02-07 2021-02-05 칼리크레인(klkb1) 유전자 편집을 위한 조성물 및 방법

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US (4) US20230295587A1 (enExample)
EP (1) EP4100528A1 (enExample)
JP (1) JP2023512758A (enExample)
KR (1) KR20220139352A (enExample)
CN (1) CN115362256A (enExample)
AU (1) AU2021216451A1 (enExample)
BR (1) BR112022015380A2 (enExample)
CA (1) CA3169813A1 (enExample)
CL (1) CL2022002095A1 (enExample)
CO (1) CO2022012196A2 (enExample)
IL (1) IL295280A (enExample)
MX (1) MX2022009658A (enExample)
PH (1) PH12022552009A1 (enExample)
SA (1) SA522440054B1 (enExample)
WO (1) WO2021158858A1 (enExample)

Families Citing this family (9)

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US12042509B2 (en) 2021-10-01 2024-07-23 Adarx Pharmaceuticals, Inc. Prekallikrein-modulating compositions and methods of use thereof
WO2023086953A1 (en) * 2021-11-11 2023-05-19 Beam Therapeutics Inc. Compositions and methods for the treatment of hereditary angioedema (hae)
TW202346586A (zh) * 2022-01-28 2023-12-01 大陸商上海舶望製藥有限公司 用於抑制前激肽釋放酶（pkk）蛋白表達的組合物和方法
WO2024011206A1 (en) * 2022-07-08 2024-01-11 Intellia Therapeutics, Inc. Methods for in vivo editing of klkb1
WO2024012435A1 (en) * 2022-07-11 2024-01-18 CorrectSequence Therapeutics Co., Ltd Gene editing systems and methods for treating hereditary angioedema
WO2025096980A1 (en) * 2023-11-02 2025-05-08 Poseida Therapeutics, Inc. Compositions targeting klkb1 and methods of use thereof
WO2025128871A2 (en) 2023-12-13 2025-06-19 Renagade Therapeutics Management Inc. Lipid nanoparticles comprising coding rna molecules for use in gene editing and as vaccines and therapeutic agents
CN118303422B (zh) * 2024-04-17 2024-11-12 华南师范大学 Ppk基因在控制德国小蠊繁殖行为中的应用
WO2026008078A1 (en) * 2024-07-05 2026-01-08 Shanghai Vitalgen Biopharma Co., Ltd. Methods for kallikrein (klkb1) gene editing

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JPH10500310A (ja) 1994-05-19 1998-01-13 ダコ アクティーゼルスカブ 淋菌及びトラコーマ クラミジアの検出のためのｐｎａ プローブ
EP3320922A1 (en) * 2011-06-10 2018-05-16 Ionis Pharmaceuticals, Inc. Methods for modulating kallikrein (klkb1) expression
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US20260022358A1 (en) 2026-01-22
BR112022015380A2 (pt) 2022-09-27
PH12022552009A1 (en) 2024-02-05
CA3169813A1 (en) 2021-08-12
WO2021158858A1 (en) 2021-08-12
CO2022012196A2 (es) 2022-09-09
MX2022009658A (es) 2022-10-27
JP2023512758A (ja) 2023-03-29
TW202146030A (zh) 2021-12-16
SA522440054B1 (ar) 2025-04-21
CL2022002095A1 (es) 2023-03-10
IL295280A (en) 2022-10-01
US12480109B2 (en) 2025-11-25
CN115362256A (zh) 2022-11-18
US20250197828A1 (en) 2025-06-19
US20240018496A1 (en) 2024-01-18
EP4100528A1 (en) 2022-12-14
AU2021216451A1 (en) 2022-09-29
US20230295587A1 (en) 2023-09-21

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