JPWO2023141302A5 - - Google Patents

Info

Publication number
JPWO2023141302A5
JPWO2023141302A5 JP2024543383A JP2024543383A JPWO2023141302A5 JP WO2023141302 A5 JPWO2023141302 A5 JP WO2023141302A5 JP 2024543383 A JP2024543383 A JP 2024543383A JP 2024543383 A JP2024543383 A JP 2024543383A JP WO2023141302 A5 JPWO2023141302 A5 JP WO2023141302A5
Authority
JP
Japan
Prior art keywords
oligonucleotide
musk
composition according
composition
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024543383A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025503098A5 (https=
JP2025503098A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/011286 external-priority patent/WO2023141302A1/en
Publication of JP2025503098A publication Critical patent/JP2025503098A/ja
Publication of JP2025503098A5 publication Critical patent/JP2025503098A5/ja
Publication of JPWO2023141302A5 publication Critical patent/JPWO2023141302A5/ja
Pending legal-status Critical Current

Links

JP2024543383A 2022-01-20 2023-01-20 ＭｕＳＫ標的化オリゴヌクレオチド Pending JP2025503098A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263301416P 2022-01-20 2022-01-20
US63/301,416 2022-01-20
PCT/US2023/011286 WO2023141302A1 (en) 2022-01-20 2023-01-20 Musk-targeting oligonucleotides

Publications (3)

Publication Number Publication Date
JP2025503098A JP2025503098A (ja) 2025-01-30
JP2025503098A5 JP2025503098A5 (https=) 2026-04-22
JPWO2023141302A5 true JPWO2023141302A5 (https=) 2026-04-22

Family

ID=87349235

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024543383A Pending JP2025503098A (ja) 2022-01-20 2023-01-20 ＭｕＳＫ標的化オリゴヌクレオチド

Country Status (6)

Country Link
US (1) US20250257359A1 (https=)
EP (1) EP4466360A4 (https=)
JP (1) JP2025503098A (https=)
AU (1) AU2023210230A1 (https=)
CA (1) CA3248917A1 (https=)
WO (1) WO2023141302A1 (https=)

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2013074636A1 (en) * 2011-11-14 2013-05-23 New York University Muscle specific receptor kinase and modulation thereof
US20200282074A1 (en) * 2017-09-22 2020-09-10 Avidity Biosciences, Inc. Nucleic acid-polypeptide compositions and methods of inducing exon skipping
CA3136949A1 (en) * 2019-04-18 2020-10-22 Brown University Neurogenesis
JP2022551970A (ja) * 2019-10-16 2022-12-14 ブラウン ユニバーシティ 筋再生および筋成長

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