JPWO2023112931A5 - - Google Patents

Download PDF

Info

Publication number
JPWO2023112931A5
JPWO2023112931A5 JP2023567797A JP2023567797A JPWO2023112931A5 JP WO2023112931 A5 JPWO2023112931 A5 JP WO2023112931A5 JP 2023567797 A JP2023567797 A JP 2023567797A JP 2023567797 A JP2023567797 A JP 2023567797A JP WO2023112931 A5 JPWO2023112931 A5 JP WO2023112931A5
Authority
JP
Japan
Prior art keywords
bonds
nucleosides
wing region
antisense oligonucleotide
pharma
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2023567797A
Other languages
English (en)
Japanese (ja)
Other versions
JP7607884B2 (ja
JPWO2023112931A1 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/JP2022/045921 external-priority patent/WO2023112931A1/ja
Publication of JPWO2023112931A1 publication Critical patent/JPWO2023112931A1/ja
Publication of JPWO2023112931A5 publication Critical patent/JPWO2023112931A5/ja
Priority to JP2024214710A priority Critical patent/JP2025038021A/ja
Application granted granted Critical
Publication of JP7607884B2 publication Critical patent/JP7607884B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2023567797A 2021-12-13 2022-12-13 ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド Active JP7607884B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024214710A JP2025038021A (ja) 2021-12-13 2024-12-09 ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
JP2021201756 2021-12-13
JP2021201756 2021-12-13
JP2022184853 2022-11-18
JP2022184853 2022-11-18
PCT/JP2022/045921 WO2023112931A1 (ja) 2021-12-13 2022-12-13 ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024214710A Division JP2025038021A (ja) 2021-12-13 2024-12-09 ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド

Publications (3)

Publication Number Publication Date
JPWO2023112931A1 JPWO2023112931A1 (https=) 2023-06-22
JPWO2023112931A5 true JPWO2023112931A5 (https=) 2024-07-01
JP7607884B2 JP7607884B2 (ja) 2025-01-06

Family

ID=86774345

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2023567797A Active JP7607884B2 (ja) 2021-12-13 2022-12-13 ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド
JP2024214710A Pending JP2025038021A (ja) 2021-12-13 2024-12-09 ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024214710A Pending JP2025038021A (ja) 2021-12-13 2024-12-09 ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド

Country Status (5)

Country Link
US (2) US20250051769A1 (https=)
EP (1) EP4450625A1 (https=)
JP (2) JP7607884B2 (https=)
TW (1) TW202340464A (https=)
WO (1) WO2023112931A1 (https=)

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2924179B2 (ja) 1993-02-19 1999-07-26 日本新薬株式会社 グリセロール誘導体,デバイス及び医薬組成物
WO2012018257A1 (en) * 2010-08-05 2012-02-09 Academisch Ziekenhuis Leiden H.O.D.N. Lumc Antisense oligonucleotide directed removal of proteolytic cleavage sites from proteins
MX2020009765A (es) * 2018-03-20 2021-01-08 Tokyo Inst Tech Oligonucleotido antisentido reducido en toxicidad.
EP4098747A4 (en) 2020-01-31 2025-03-26 Sanwa Kagaku Kenkyusho Co., Ltd. ATN1 ANTISENSE OLIGONUCLEOTIDE
JPWO2022211129A1 (https=) 2021-04-01 2022-10-06
WO2023164656A2 (en) 2022-02-25 2023-08-31 Ionis Pharmaceuticals, Inc. Compounds and methods for modulating atn1 expression
WO2023201281A2 (en) 2022-04-14 2023-10-19 University Of Massachusetts Oligonucleotides for atn1 modulation

Similar Documents

Publication Publication Date Title
CN110079524B (zh) 用于调节hbv和ttr表达的组合物和方法
JP7748500B2 (ja) トリループを含む二本鎖核酸インヒビター分子
KR100991975B1 (ko) 핵산을 기본으로 하는 화합물 및 이의 사용방법
KR20180134364A (ko) 트리틸-모노-GalNAc 화합물 및 이의 용도
CN110832077B (zh) 用于抑制α-ENaC表达的RNAi剂及使用方法
US20240368593A1 (en) Gapmer oligonucleotides comprising a phosphorodithioate internucleoside linkage
JP2019534009A5 (https=)
TW201923080A (zh) 用於降低PAPD5及PAPD7 mRNA以治療B型肝炎感染之核酸分子
CN111448316B (zh) 新的硫代亚磷酰胺
CN121079412A (zh) 经修饰的指导rna
CN104321334A (zh) 三环核苷及由其制备的低聚化合物
CA3210172A1 (en) Compounds and methods for reducing pln expression
CN113795581A (zh) 具有缩短的有义链的双链核酸抑制剂分子
JP7476102B2 (ja) ホスホロジチオアートヌクレオシド間結合を含むオリゴヌクレオチド
JPWO2023112931A5 (https=)
US20240336920A1 (en) Threose nucleic acid antisense oligonucleotides and methods thereof
TW202345861A (zh) 經修飾之間隔體寡聚物及其使用方法
EP4332221A1 (en) Threose nucleic acid antisense oligonucleotides and methods thereof
WO2022266486A2 (en) Products and compositions
CN115279904A (zh) 抑制asah1基因表达的组合物和方法
TW202102516A (zh) 膦醯基乙酸酯間隙子寡核苷酸
JP2021510295A (ja) Gsk3b発現を調節するためのオリゴヌクレオチド
JPWO2021252799A5 (https=)
HK40083632A (en) Compositions and methods for inhibiting asah1 gene expression
HK40129500A (en) Translation enhancing nucleic acid compounds: aso coupled translation - upregulation 1 (act-up1) and uses thereof