JPWO2023112931A5 - - Google Patents
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- Publication number
- JPWO2023112931A5 JPWO2023112931A5 JP2023567797A JP2023567797A JPWO2023112931A5 JP WO2023112931 A5 JPWO2023112931 A5 JP WO2023112931A5 JP 2023567797 A JP2023567797 A JP 2023567797A JP 2023567797 A JP2023567797 A JP 2023567797A JP WO2023112931 A5 JPWO2023112931 A5 JP WO2023112931A5
- Authority
- JP
- Japan
- Prior art keywords
- bonds
- nucleosides
- wing region
- antisense oligonucleotide
- pharma
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024214710A JP2025038021A (ja) | 2021-12-13 | 2024-12-09 | ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2021201756 | 2021-12-13 | ||
| JP2021201756 | 2021-12-13 | ||
| JP2022184853 | 2022-11-18 | ||
| JP2022184853 | 2022-11-18 | ||
| PCT/JP2022/045921 WO2023112931A1 (ja) | 2021-12-13 | 2022-12-13 | ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024214710A Division JP2025038021A (ja) | 2021-12-13 | 2024-12-09 | ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JPWO2023112931A1 JPWO2023112931A1 (https=) | 2023-06-22 |
| JPWO2023112931A5 true JPWO2023112931A5 (https=) | 2024-07-01 |
| JP7607884B2 JP7607884B2 (ja) | 2025-01-06 |
Family
ID=86774345
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023567797A Active JP7607884B2 (ja) | 2021-12-13 | 2022-12-13 | ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド |
| JP2024214710A Pending JP2025038021A (ja) | 2021-12-13 | 2024-12-09 | ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024214710A Pending JP2025038021A (ja) | 2021-12-13 | 2024-12-09 | ATN1 mRNA又はpre-mRNAを標的とするアンチセンスオリゴヌクレオチド |
Country Status (5)
| Country | Link |
|---|---|
| US (2) | US20250051769A1 (https=) |
| EP (1) | EP4450625A1 (https=) |
| JP (2) | JP7607884B2 (https=) |
| TW (1) | TW202340464A (https=) |
| WO (1) | WO2023112931A1 (https=) |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2924179B2 (ja) | 1993-02-19 | 1999-07-26 | 日本新薬株式会社 | グリセロール誘導体,デバイス及び医薬組成物 |
| WO2012018257A1 (en) * | 2010-08-05 | 2012-02-09 | Academisch Ziekenhuis Leiden H.O.D.N. Lumc | Antisense oligonucleotide directed removal of proteolytic cleavage sites from proteins |
| MX2020009765A (es) * | 2018-03-20 | 2021-01-08 | Tokyo Inst Tech | Oligonucleotido antisentido reducido en toxicidad. |
| EP4098747A4 (en) | 2020-01-31 | 2025-03-26 | Sanwa Kagaku Kenkyusho Co., Ltd. | ATN1 ANTISENSE OLIGONUCLEOTIDE |
| JPWO2022211129A1 (https=) | 2021-04-01 | 2022-10-06 | ||
| WO2023164656A2 (en) | 2022-02-25 | 2023-08-31 | Ionis Pharmaceuticals, Inc. | Compounds and methods for modulating atn1 expression |
| WO2023201281A2 (en) | 2022-04-14 | 2023-10-19 | University Of Massachusetts | Oligonucleotides for atn1 modulation |
-
2022
- 2022-12-13 JP JP2023567797A patent/JP7607884B2/ja active Active
- 2022-12-13 TW TW111147856A patent/TW202340464A/zh unknown
- 2022-12-13 WO PCT/JP2022/045921 patent/WO2023112931A1/ja not_active Ceased
- 2022-12-13 EP EP22907455.4A patent/EP4450625A1/en active Pending
- 2022-12-13 US US18/719,037 patent/US20250051769A1/en active Pending
-
2024
- 2024-06-12 US US18/741,110 patent/US12291710B2/en active Active
- 2024-12-09 JP JP2024214710A patent/JP2025038021A/ja active Pending
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