JPWO2022076848A5 - - Google Patents
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- Publication number
- JPWO2022076848A5 JPWO2022076848A5 JP2023521661A JP2023521661A JPWO2022076848A5 JP WO2022076848 A5 JPWO2022076848 A5 JP WO2022076848A5 JP 2023521661 A JP2023521661 A JP 2023521661A JP 2023521661 A JP2023521661 A JP 2023521661A JP WO2022076848 A5 JPWO2022076848 A5 JP WO2022076848A5
- Authority
- JP
- Japan
- Prior art keywords
- viral vector
- polypeptide
- enpp1
- enpp3
- nucleic acid
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063089515P | 2020-10-08 | 2020-10-08 | |
| US63/089,515 | 2020-10-08 | ||
| US202163165650P | 2021-03-24 | 2021-03-24 | |
| US63/165,650 | 2021-03-24 | ||
| US202163248339P | 2021-09-24 | 2021-09-24 | |
| US63/248,339 | 2021-09-24 | ||
| PCT/US2021/054216 WO2022076848A1 (en) | 2020-10-08 | 2021-10-08 | Liver specific production of enpp1 or enpp3 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023548758A JP2023548758A (ja) | 2023-11-21 |
| JPWO2022076848A5 true JPWO2022076848A5 (https=) | 2024-10-16 |
| JP2023548758A5 JP2023548758A5 (https=) | 2024-10-16 |
Family
ID=81126156
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023521661A Pending JP2023548758A (ja) | 2020-10-08 | 2021-10-08 | Ｅｎｐｐ１またはｅｎｐｐ３の肝臓特異的生成 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20240148907A1 (https=) |
| EP (1) | EP4225927A4 (https=) |
| JP (1) | JP2023548758A (https=) |
| AU (1) | AU2021356692A1 (https=) |
| CA (1) | CA3195071A1 (https=) |
| TW (1) | TW202229557A (https=) |
| WO (1) | WO2022076848A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2023049864A1 (en) * | 2021-09-24 | 2023-03-30 | Inozyme Pharma, Inc. | Lyophilized enpp1 polypeptide formulations and uses thereof |
| CN119242712A (zh) * | 2024-09-27 | 2025-01-03 | 南京师范大学 | 特异性靶向骨骼肌细胞的携带miRNA-486基因的腺相关病毒载体、药物组合物 |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP1736553A1 (en) * | 2005-06-17 | 2006-12-27 | Centre National De La Recherche Scientifique | ENPP1 (PC-1) gene haplotype associated with the risk of obesity and type 2 diabetes and their applications |
| CA2788682C (en) * | 2010-02-05 | 2019-03-05 | The University Of North Carolina At Chapel Hill | Compositions and methods for enhanced parvovirus transduction |
| WO2014126965A2 (en) * | 2013-02-13 | 2014-08-21 | Yale University | Compositions and methods for treating pathological calcification and ossification |
| KR20250078598A (ko) * | 2015-05-19 | 2025-06-02 | 예일 유니버시티 | 병리학적 석회화 병태를 치료하기 위한 조성물, 및 이의 사용 방법 |
| WO2017087936A1 (en) * | 2015-11-20 | 2017-05-26 | Yale University | Compositions for treating ectopic calcification disorders, and methods using same |
| KR20210142599A (ko) * | 2019-01-18 | 2021-11-25 | 이노자임 파마, 인코포레이티드 | Enpp1 또는 enpp3 결핍을 수반하는 질환의 치료 |
-
2021
- 2021-10-08 WO PCT/US2021/054216 patent/WO2022076848A1/en not_active Ceased
- 2021-10-08 CA CA3195071A patent/CA3195071A1/en active Pending
- 2021-10-08 JP JP2023521661A patent/JP2023548758A/ja active Pending
- 2021-10-08 EP EP21878635.8A patent/EP4225927A4/en not_active Withdrawn
- 2021-10-08 AU AU2021356692A patent/AU2021356692A1/en active Pending
- 2021-10-08 TW TW110137622A patent/TW202229557A/zh unknown
-
2023
- 2023-04-07 US US18/297,228 patent/US20240148907A1/en active Pending
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