JPWO2022003357A5 - - Google Patents
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- JPWO2022003357A5 JPWO2022003357A5 JP2023523681A JP2023523681A JPWO2022003357A5 JP WO2022003357 A5 JPWO2022003357 A5 JP WO2022003357A5 JP 2023523681 A JP2023523681 A JP 2023523681A JP 2023523681 A JP2023523681 A JP 2023523681A JP WO2022003357 A5 JPWO2022003357 A5 JP WO2022003357A5
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- promoter
- viral vector
- sequence identity
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- isolated cell
- Prior art date
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| GB2010009.5 | 2020-06-30 | ||
| GBGB2010009.5A GB202010009D0 (en) | 2020-06-30 | 2020-06-30 | Vector |
| PCT/GB2021/051668 WO2022003357A1 (en) | 2020-06-30 | 2021-06-30 | Vector |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023536008A JP2023536008A (ja) | 2023-08-22 |
| JP2023536008A5 JP2023536008A5 (https=) | 2024-07-08 |
| JPWO2022003357A5 true JPWO2022003357A5 (https=) | 2024-07-08 |
Family
ID=71949697
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023523681A Pending JP2023536008A (ja) | 2020-06-30 | 2021-06-30 | ベクター |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20230175016A1 (https=) |
| EP (1) | EP4172345A1 (https=) |
| JP (1) | JP2023536008A (https=) |
| KR (1) | KR20230056658A (https=) |
| CN (1) | CN115997025A (https=) |
| AU (1) | AU2021300616A1 (https=) |
| BR (1) | BR112022026521A2 (https=) |
| CA (1) | CA3183830A1 (https=) |
| GB (1) | GB202010009D0 (https=) |
| IL (1) | IL299505A (https=) |
| MX (1) | MX2022016101A (https=) |
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| GB202003618D0 (en) | 2020-03-12 | 2020-04-29 | Univ Bristol | Gene Therapy |
| AU2021293174A1 (en) | 2020-06-14 | 2023-01-19 | Vertex Pharmaceuticals Incorporated | Complement Factor I-related compositions and methods |
| GB202217332D0 (en) * | 2022-11-18 | 2023-01-04 | Univ Bristol | Methods |
| EP4410988A1 (en) * | 2023-01-31 | 2024-08-07 | Universitätsklinikum Hamburg-Eppendorf | An aav2-vector variant for targeted transfer of genes |
| WO2024178007A1 (en) * | 2023-02-21 | 2024-08-29 | University Of Pittsburgh - Of The Commonwealth System Of Higher Education | Mafb promoter for gene therapy for diabetes |
| GB202304841D0 (en) * | 2023-03-31 | 2023-05-17 | Purespring Therapeutics Ltd | Promoter |
| AU2024262827A1 (en) * | 2023-04-27 | 2025-10-16 | Oregon Health & Science University | Kidney-targeting aav capsids and methods of use thereof |
| GB202414499D0 (en) * | 2024-10-02 | 2024-11-13 | Purespring Therapeutics Ltd | Methods |
Family Cites Families (8)
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| PL332875A1 (en) | 1996-10-17 | 1999-10-25 | Oxford Biomedica Ltd | Retroviral vectors |
| WO2005012351A2 (en) * | 2003-08-01 | 2005-02-10 | The Brigham And Women's Hospital, Inc. | Novel functions for decay accelerating factor (daf) in inflammation |
| EP2357254A1 (en) * | 2005-02-14 | 2011-08-17 | University of Iowa Research Foundation | Methods and reagents for treatment and diagnosis of age-related macular degeneration |
| ES2457822T3 (es) * | 2007-11-08 | 2014-04-29 | The General Hospital Corporation | Procedimientos y composiciones de tratamiento de enfermedades proteinúricas |
| ES2857773T5 (es) * | 2011-08-24 | 2024-06-04 | Univ Leland Stanford Junior | Nuevas proteínas de la cápside de AAV para la transferencia de ácidos nucleicos |
| GB201403684D0 (en) * | 2014-03-03 | 2014-04-16 | King S College London | Vector |
| CN108291216B (zh) * | 2015-09-24 | 2022-09-16 | 宾夕法尼亚州大学信托人 | 用于治疗补体介导的疾病的组合物和方法 |
| JP7222075B2 (ja) * | 2018-09-13 | 2023-02-14 | リジェネロン・ファーマシューティカルズ・インコーポレイテッド | Ｃ３糸球体症のモデルとしての補体因子ｈ遺伝子ノックアウトラット |
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2020
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2021
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- 2021-06-30 EP EP21748644.8A patent/EP4172345A1/en active Pending
- 2021-06-30 JP JP2023523681A patent/JP2023536008A/ja active Pending
- 2021-06-30 US US18/011,592 patent/US20230175016A1/en active Pending
- 2021-06-30 AU AU2021300616A patent/AU2021300616A1/en active Pending
- 2021-06-30 CN CN202180046691.7A patent/CN115997025A/zh active Pending
- 2021-06-30 IL IL299505A patent/IL299505A/en unknown
- 2021-06-30 WO PCT/GB2021/051668 patent/WO2022003357A1/en not_active Ceased
- 2021-06-30 KR KR1020237003243A patent/KR20230056658A/ko active Pending
- 2021-06-30 BR BR112022026521A patent/BR112022026521A2/pt unknown
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