JP2020506695A5 - - Google Patents
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- Publication number
- JP2020506695A5 JP2020506695A5 JP2019540667A JP2019540667A JP2020506695A5 JP 2020506695 A5 JP2020506695 A5 JP 2020506695A5 JP 2019540667 A JP2019540667 A JP 2019540667A JP 2019540667 A JP2019540667 A JP 2019540667A JP 2020506695 A5 JP2020506695 A5 JP 2020506695A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- vector
- raav
- recombinant
- nucleic acid
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022169032A JP2023002715A (ja) | 2017-01-30 | 2022-10-21 | 糖原病を処置するための組換えウイルスベクター |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762451963P | 2017-01-30 | 2017-01-30 | |
| US62/451,963 | 2017-01-30 | ||
| PCT/US2018/015957 WO2018140946A1 (en) | 2017-01-30 | 2018-01-30 | Recombinant virus vectors for the treatment of glycogen storage disease |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022169032A Division JP2023002715A (ja) | 2017-01-30 | 2022-10-21 | 糖原病を処置するための組換えウイルスベクター |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2020506695A JP2020506695A (ja) | 2020-03-05 |
| JP2020506695A5 true JP2020506695A5 (https=) | 2021-02-25 |
Family
ID=61274327
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019540667A Pending JP2020506695A (ja) | 2017-01-30 | 2018-01-30 | 糖原病を処置するための組換えウイルスベクター |
| JP2022169032A Pending JP2023002715A (ja) | 2017-01-30 | 2022-10-21 | 糖原病を処置するための組換えウイルスベクター |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022169032A Pending JP2023002715A (ja) | 2017-01-30 | 2022-10-21 | 糖原病を処置するための組換えウイルスベクター |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20190367944A1 (https=) |
| EP (1) | EP3574104A1 (https=) |
| JP (2) | JP2020506695A (https=) |
| AU (1) | AU2018212002A1 (https=) |
| CA (1) | CA3050917A1 (https=) |
| WO (1) | WO2018140946A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2969222T3 (es) * | 2018-12-18 | 2024-05-17 | Ultragenyx Pharmaceutical Inc | Métodos y composiciones para el tratamiento de enfermedades del almacenamiento de glucógeno |
| US20250222134A1 (en) * | 2021-10-19 | 2025-07-10 | University Of Connecticut | Compositions and methods for the treatment of glycogen storage disorders |
Family Cites Families (18)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6013516A (en) | 1995-10-06 | 2000-01-11 | The Salk Institute For Biological Studies | Vector and method of use for nucleic acid delivery to non-dividing cells |
| US6207455B1 (en) | 1997-05-01 | 2001-03-27 | Lung-Ji Chang | Lentiviral vectors |
| JP4390860B2 (ja) | 1997-05-13 | 2009-12-24 | ユニヴァーシティ・オヴ・ノース・キャロライナ・アト・チャペル・ヒル | レンチウイルスをベースにした遺伝子転移ベクター |
| US5994136A (en) | 1997-12-12 | 1999-11-30 | Cell Genesys, Inc. | Method and means for producing high titer, safe, recombinant lentivirus vectors |
| US6218181B1 (en) | 1998-03-18 | 2001-04-17 | The Salk Institute For Biological Studies | Retroviral packaging cell line |
| US6759050B1 (en) | 1998-12-03 | 2004-07-06 | Avigen, Inc. | Excipients for use in adeno-associated virus pharmaceutical formulations, and pharmaceutical formulations made therewith |
| US6218186B1 (en) | 1999-11-12 | 2001-04-17 | Trustees Of The University Of Pennsylvania | HIV-MSCV hybrid viral vector for gene transfer |
| US7575924B2 (en) | 2000-11-13 | 2009-08-18 | Research Development Foundation | Methods and compositions relating to improved lentiviral vectors and their applications |
| EP1438075A4 (en) | 2001-10-02 | 2006-04-19 | Inst Clayton De La Rech | METHOD AND COMPOSITIONS ASSOCIATED WITH LENTIVIRAL VECTORS WITH LIMITED EXPRESSION AND ITS APPLICATIONS |
| DE60333487D1 (de) | 2002-12-13 | 2010-09-02 | Genetix Pharmaceuticals Inc | Therapeutische retrovirus-vektoren für gentherapie |
| US20050261233A1 (en) * | 2004-04-21 | 2005-11-24 | Sanjay Bhanot | Modulation of glucose-6-phosphatase translocase expression |
| ES2708856T3 (es) | 2007-08-03 | 2019-04-11 | Pasteur Institut | Vectores de transferencia de gen lentivírico y sus aplicaciones medicinales |
| DK2242840T3 (da) | 2008-01-29 | 2019-10-21 | Applied Genetic Tech Corporation | Produktion af rekombinant adeno-associeret virus under anvendelse af bhk-celler i suspension |
| US8679837B2 (en) | 2009-04-02 | 2014-03-25 | University Of Florida Research Foundation, Inc. | Inducible system for highly efficient production of recombinant Adeno-associated virus (rAAV) vectors |
| US20120133514A1 (en) | 2009-06-30 | 2012-05-31 | Asp Technology Aps | Pause adviser system and use thereof |
| DK2529020T3 (en) | 2010-01-28 | 2018-08-06 | Childrens Hospital Philadelphia | SCALABLE PREPARATION PLATF FOR CLEANING VIRAL VECTORS AND CLEANED VIRAL VECTORS FOR USE IN GENTHERAPY |
| WO2015081101A1 (en) * | 2013-11-26 | 2015-06-04 | The United States Of America, As Represented By The Secretary Department Of Health And Human Services | Adeno-associated virus vectors for treatment of glycogen storage disease |
| JP6824169B2 (ja) * | 2014-12-23 | 2021-02-03 | ザ ユナイテッド ステイツ オブ アメリカ， アズ リプレゼンテッド バイ ザ セクレタリー， デパートメント オブ ヘルス アンド ヒューマン サービシーズ | 改変ｇ６ｐｃをコードするアデノ随伴ウイルスベクターおよびその使用 |
-
2018
- 2018-01-30 AU AU2018212002A patent/AU2018212002A1/en not_active Abandoned
- 2018-01-30 US US16/481,430 patent/US20190367944A1/en not_active Abandoned
- 2018-01-30 JP JP2019540667A patent/JP2020506695A/ja active Pending
- 2018-01-30 WO PCT/US2018/015957 patent/WO2018140946A1/en not_active Ceased
- 2018-01-30 EP EP18707167.5A patent/EP3574104A1/en not_active Withdrawn
- 2018-01-30 CA CA3050917A patent/CA3050917A1/en active Pending
-
2022
- 2022-10-21 JP JP2022169032A patent/JP2023002715A/ja active Pending
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