JPWO2021081217A5 - - Google Patents
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- Publication number
- JPWO2021081217A5 JPWO2021081217A5 JP2022524118A JP2022524118A JPWO2021081217A5 JP WO2021081217 A5 JPWO2021081217 A5 JP WO2021081217A5 JP 2022524118 A JP2022524118 A JP 2022524118A JP 2022524118 A JP2022524118 A JP 2022524118A JP WO2021081217 A5 JPWO2021081217 A5 JP WO2021081217A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- seq
- nucleotides
- expression cassette
- raav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (17)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962924970P | 2019-10-23 | 2019-10-23 | |
| US62/924,970 | 2019-10-23 | ||
| US201962934915P | 2019-11-13 | 2019-11-13 | |
| US62/934,915 | 2019-11-13 | ||
| PCT/US2019/067872 WO2020132455A1 (fr) | 2018-12-21 | 2019-12-20 | Compositions pour la réduction spécifique de drg de l'expression de transgène |
| USPCT/US2019/067872 | 2019-12-20 | ||
| US202062972404P | 2020-02-10 | 2020-02-10 | |
| US62/972,404 | 2020-02-10 | ||
| US202063005894P | 2020-04-06 | 2020-04-06 | |
| US63/005,894 | 2020-04-06 | ||
| US202063023602P | 2020-05-12 | 2020-05-12 | |
| US63/023,602 | 2020-05-12 | ||
| US202063038514P | 2020-06-12 | 2020-06-12 | |
| US63/038,514 | 2020-06-12 | ||
| US202063043600P | 2020-06-24 | 2020-06-24 | |
| US63/043,600 | 2020-06-24 | ||
| PCT/US2020/056881 WO2021081217A1 (fr) | 2019-10-23 | 2020-10-22 | Compositions pour la réduction spécifique de drg de l'expression de transgène |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022553406A JP2022553406A (ja) | 2022-12-22 |
| JPWO2021081217A5 true JPWO2021081217A5 (fr) | 2023-10-18 |
Family
ID=75620360
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022524118A Pending JP2022553406A (ja) | 2019-10-23 | 2020-10-22 | 導入遺伝子発現のｄｒｇ特異的低減のための組成物 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20220389457A1 (fr) |
| EP (1) | EP4048785A4 (fr) |
| JP (1) | JP2022553406A (fr) |
| KR (1) | KR20220105158A (fr) |
| AU (1) | AU2020369570A1 (fr) |
| CA (1) | CA3155154A1 (fr) |
| IL (1) | IL292372A (fr) |
| WO (1) | WO2021081217A1 (fr) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2021270447A1 (en) * | 2020-05-12 | 2023-01-05 | The Trustees Of The University Of Pennsylvania | Compositions for DRG-specific reduction of transgene expression |
| WO2024008950A1 (fr) * | 2022-07-08 | 2024-01-11 | Ospedale San Raffaele S.R.L. | Cassettes transgéniques |
| CN116064593B (zh) * | 2023-02-09 | 2024-05-14 | 四川大学 | 一种毛白杨pgag基因及其应用 |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2833923A4 (fr) * | 2012-04-02 | 2016-02-24 | Moderna Therapeutics Inc | Polynucléotides modifiés pour la production de protéines |
| EP3913061A1 (fr) * | 2014-05-02 | 2021-11-24 | Genzyme Corporation | Vecteurs aav pour thérapie génique de la rétine et du snc |
| EP3411488A1 (fr) * | 2016-02-03 | 2018-12-12 | The Trustees Of The University Of Pennsylvania | Thérapie génique pour traiter la mucopolysaccharidose de type i |
| CN108697774A (zh) * | 2016-02-22 | 2018-10-23 | 北卡罗来纳大学教堂山分校 | 治疗mps i-相关失明的aav-idua载体 |
| BR112020000063A2 (pt) * | 2017-07-06 | 2020-07-14 | The Trustees Of The University Of Pennsylvania | terapia gênica mediada por aav9 para tratamento de mucopolissacaridose tipo i |
| WO2019060454A2 (fr) * | 2017-09-20 | 2019-03-28 | 4D Molecular Therapeutics Inc. | Virus adéno-associé à variant de capsides et leurs procédés d'utilisation |
-
2020
- 2020-10-22 KR KR1020227016895A patent/KR20220105158A/ko unknown
- 2020-10-22 EP EP20880317.1A patent/EP4048785A4/fr active Pending
- 2020-10-22 US US17/770,137 patent/US20220389457A1/en active Pending
- 2020-10-22 CA CA3155154A patent/CA3155154A1/fr active Pending
- 2020-10-22 AU AU2020369570A patent/AU2020369570A1/en active Pending
- 2020-10-22 JP JP2022524118A patent/JP2022553406A/ja active Pending
- 2020-10-22 WO PCT/US2020/056881 patent/WO2021081217A1/fr active Application Filing
- 2020-10-22 IL IL292372A patent/IL292372A/en unknown
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