JPWO2020251954A5 - - Google Patents
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- Publication number
- JPWO2020251954A5 JPWO2020251954A5 JP2021573242A JP2021573242A JPWO2020251954A5 JP WO2020251954 A5 JPWO2020251954 A5 JP WO2020251954A5 JP 2021573242 A JP2021573242 A JP 2021573242A JP 2021573242 A JP2021573242 A JP 2021573242A JP WO2020251954 A5 JPWO2020251954 A5 JP WO2020251954A5
- Authority
- JP
- Japan
- Prior art keywords
- amino acid
- seq
- capsid protein
- protein corresponding
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (13)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962859539P | 2019-06-10 | 2019-06-10 | |
| US62/859,539 | 2019-06-10 | ||
| US201962866374P | 2019-06-25 | 2019-06-25 | |
| US62/866,374 | 2019-06-25 | ||
| US201962915523P | 2019-10-15 | 2019-10-15 | |
| US62/915,523 | 2019-10-15 | ||
| US202062960487P | 2020-01-13 | 2020-01-13 | |
| US62/960,487 | 2020-01-13 | ||
| US202062987858P | 2020-03-10 | 2020-03-10 | |
| US62/987,858 | 2020-03-10 | ||
| US202063010970P | 2020-04-16 | 2020-04-16 | |
| US63/010,970 | 2020-04-16 | ||
| PCT/US2020/036846 WO2020251954A1 (en) | 2019-06-10 | 2020-06-09 | Adeno-associated virus compositions for arsa gene transfer and methods of use thereof |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022536338A JP2022536338A (ja) | 2022-08-15 |
| JPWO2020251954A5 true JPWO2020251954A5 (https=) | 2023-06-05 |
| JP2022536338A5 JP2022536338A5 (https=) | 2023-06-05 |
Family
ID=73782242
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021573242A Pending JP2022536338A (ja) | 2019-06-10 | 2020-06-09 | Ａｒｓａ遺伝子移入のためのアデノ随伴ウイルス組成物およびその使用方法 |
Country Status (15)
| Country | Link |
|---|---|
| US (1) | US20220204991A1 (https=) |
| EP (1) | EP3980447A4 (https=) |
| JP (1) | JP2022536338A (https=) |
| KR (1) | KR20220035107A (https=) |
| CN (1) | CN114502575A (https=) |
| AU (1) | AU2020292256B2 (https=) |
| BR (1) | BR112021024855A2 (https=) |
| CA (1) | CA3142932A1 (https=) |
| CL (1) | CL2021003295A1 (https=) |
| CO (1) | CO2021016797A2 (https=) |
| IL (1) | IL288863A (https=) |
| MX (1) | MX2021015076A (https=) |
| PE (1) | PE20220233A1 (https=) |
| TW (1) | TW202112807A (https=) |
| WO (1) | WO2020251954A1 (https=) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| RU2769577C1 (ru) * | 2021-06-01 | 2022-04-04 | федеральное государственное автономное образовательное учреждение высшего образования "Казанский (Приволжский) федеральный университет" (ФГАОУ ВО КФУ) | Препарат для лечения метахроматической лейкодистрофии и способ ее лечения |
| AU2023273809A1 (en) * | 2022-05-16 | 2025-01-02 | Genzyme Corporation | Methods of treating metachromatic leukodystrophy |
| JP2025525792A (ja) | 2022-07-29 | 2025-08-07 | リジェネロン・ファーマシューティカルズ・インコーポレイテッド | トランスフェリン受容体１に対して再標的化されるウイルス粒子 |
| WO2024036250A2 (en) * | 2022-08-10 | 2024-02-15 | Homology Medicines, Inc. | Adeno-associated virus compositions for arsa gene transfer and methods of use thereof |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US9839696B2 (en) * | 2010-04-30 | 2017-12-12 | City Of Hope | Recombinant adeno-associated vectors for targeted treatment |
| EP2634253B1 (en) * | 2010-10-27 | 2016-05-11 | Jichi Medical University | Adeno-associated virus virions for transferring genes into neural cells |
| IL248102B (en) * | 2014-05-02 | 2022-07-01 | Genzyme Corp | aav vectors for gene therapy of the central nervous system and retina |
| EP3245221A4 (en) * | 2015-01-16 | 2018-06-13 | Voyager Therapeutics, Inc. | Central nervous system targeting polynucleotides |
| JP6836999B2 (ja) * | 2015-03-24 | 2021-03-03 | ザ リージェンツ オブ ザ ユニバーシティ オブ カリフォルニアＴｈｅ Ｒｅｇｅｎｔｓ Ｏｆ Ｔｈｅ Ｕｎｉｖｅｒｓｉｔｙ Ｏｆ Ｃａｌｉｆｏｒｎｉａ | アデノ随伴ウイルス変異体及びその使用方法 |
| HK1256341A1 (zh) * | 2015-05-15 | 2019-09-20 | 明尼苏达大学董事会 | 用於治疗性递送到中枢神经系统的腺相关物 |
| TWI813532B (zh) * | 2015-06-18 | 2023-09-01 | 美商博得學院股份有限公司 | 降低脱靶效應的ｃｒｉｓｐｒ酶突變 |
| KR102528641B1 (ko) * | 2018-02-01 | 2023-05-03 | 호몰로지 메디슨, 인크. | Pah 유전자 전달을 위한 아데노-연관 바이러스 조성물 및 이의 사용 방법 |
| US20220127625A1 (en) * | 2019-02-15 | 2022-04-28 | Generation Bio Co. | Modulation of rep protein activity in closed-ended dna (cedna) production |
| BR112021021908A2 (pt) * | 2019-05-03 | 2022-02-01 | Univ Pennsylvania | Composições úteis no tratamento da leucodistrofia metacromática |
-
2020
- 2020-06-09 EP EP20821636.6A patent/EP3980447A4/en not_active Withdrawn
- 2020-06-09 WO PCT/US2020/036846 patent/WO2020251954A1/en not_active Ceased
- 2020-06-09 JP JP2021573242A patent/JP2022536338A/ja active Pending
- 2020-06-09 CA CA3142932A patent/CA3142932A1/en active Pending
- 2020-06-09 MX MX2021015076A patent/MX2021015076A/es unknown
- 2020-06-09 BR BR112021024855A patent/BR112021024855A2/pt not_active IP Right Cessation
- 2020-06-09 KR KR1020227000707A patent/KR20220035107A/ko active Pending
- 2020-06-09 CN CN202080054069.6A patent/CN114502575A/zh active Pending
- 2020-06-09 TW TW109119333A patent/TW202112807A/zh unknown
- 2020-06-09 AU AU2020292256A patent/AU2020292256B2/en not_active Ceased
- 2020-06-09 PE PE2021002049A patent/PE20220233A1/es unknown
-
2021
- 2021-12-09 IL IL288863A patent/IL288863A/en unknown
- 2021-12-10 CL CL2021003295A patent/CL2021003295A1/es unknown
- 2021-12-10 US US17/643,631 patent/US20220204991A1/en not_active Abandoned
- 2021-12-10 CO CONC2021/0016797A patent/CO2021016797A2/es unknown
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