JPWO2020247814A5 - - Google Patents

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Publication number
JPWO2020247814A5
JPWO2020247814A5 JP2021572301A JP2021572301A JPWO2020247814A5 JP WO2020247814 A5 JPWO2020247814 A5 JP WO2020247814A5 JP 2021572301 A JP2021572301 A JP 2021572301A JP 2021572301 A JP2021572301 A JP 2021572301A JP WO2020247814 A5 JPWO2020247814 A5 JP WO2020247814A5
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JP
Japan
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optionally substituted
cells
mol
optionally
virus
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Pending
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JP2021572301A
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English (en)
Japanese (ja)
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JP2022534798A (ja
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Priority claimed from PCT/US2020/036415 external-priority patent/WO2020247814A1/en
Publication of JP2022534798A publication Critical patent/JP2022534798A/ja
Publication of JPWO2020247814A5 publication Critical patent/JPWO2020247814A5/ja
Pending legal-status Critical Current

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JP2021572301A 2019-06-05 2020-06-05 真核細胞を修飾するための組成物及び方法 Pending JP2022534798A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962857587P 2019-06-05 2019-06-05
US62/857,587 2019-06-05
PCT/US2020/036415 WO2020247814A1 (en) 2019-06-05 2020-06-05 Compositions and methods for modifying eukaryotic cells

Publications (2)

Publication Number Publication Date
JP2022534798A JP2022534798A (ja) 2022-08-03
JPWO2020247814A5 true JPWO2020247814A5 (de) 2023-06-13

Family

ID=73652293

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021572301A Pending JP2022534798A (ja) 2019-06-05 2020-06-05 真核細胞を修飾するための組成物及び方法

Country Status (5)

Country Link
US (1) US20230002784A1 (de)
EP (1) EP3980549A4 (de)
JP (1) JP2022534798A (de)
CN (1) CN114450412A (de)
WO (1) WO2020247814A1 (de)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2021202658A1 (en) 2021-04-28 2022-11-17 Fondazione Telethon Gene therapy

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2000041732A1 (en) * 1999-01-19 2000-07-20 The Children's Hospital Of Philadelphia Hydrogel compositions for controlled delivery of virus vectors and methods of use thereof
CA2401239A1 (en) * 2000-03-03 2001-09-13 Valentis, Inc. Improved poloxamer and poloxamine compositions for nucleic acid delivery
DK2820138T3 (da) * 2012-02-29 2020-12-07 Helmholtz Zentrum Muenchen Deutsches Forschungszentrum Gesundheit & Umwelt Gmbh Retroviral transduktion under anvendelse af poloxamerer
IL257939B2 (en) * 2015-09-24 2023-03-01 Biomarin Pharm Inc Adeno-associated virus factor 8 vectors, associated virus particles, and medicinal formulations comprising the same
CA3014078A1 (en) * 2016-02-12 2017-08-17 Bluebird Bio, Inc. Vcn enhancer compositions and methods of using the same
JP7228523B2 (ja) * 2017-03-29 2023-02-24 ブルーバード バイオ, インコーポレイテッド ヘモグロビン異常症を治療するためのベクターおよび組成物

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