JPWO2020160458A5 - - Google Patents
Download PDFInfo
- Publication number
- JPWO2020160458A5 JPWO2020160458A5 JP2021544547A JP2021544547A JPWO2020160458A5 JP WO2020160458 A5 JPWO2020160458 A5 JP WO2020160458A5 JP 2021544547 A JP2021544547 A JP 2021544547A JP 2021544547 A JP2021544547 A JP 2021544547A JP WO2020160458 A5 JPWO2020160458 A5 JP WO2020160458A5
- Authority
- JP
- Japan
- Prior art keywords
- acid sequence
- amino acid
- grn
- optionally
- seq
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024231791A JP2025060943A (ja) | 2019-02-01 | 2024-12-27 | 神経認知障害を処置するための組成物及び方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962800096P | 2019-02-01 | 2019-02-01 | |
| US62/800,096 | 2019-02-01 | ||
| PCT/US2020/016192 WO2020160458A1 (en) | 2019-02-01 | 2020-01-31 | Compositions and methods for treating neurocognitive disorders |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024231791A Division JP2025060943A (ja) | 2019-02-01 | 2024-12-27 | 神経認知障害を処置するための組成物及び方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022523913A JP2022523913A (ja) | 2022-04-27 |
| JPWO2020160458A5 true JPWO2020160458A5 (https=) | 2023-04-25 |
| JP2022523913A5 JP2022523913A5 (https=) | 2023-04-25 |
Family
ID=71841663
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021544547A Pending JP2022523913A (ja) | 2019-02-01 | 2020-01-31 | 神経認知障害を処置するための組成物及び方法 |
| JP2024231791A Pending JP2025060943A (ja) | 2019-02-01 | 2024-12-27 | 神経認知障害を処置するための組成物及び方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024231791A Pending JP2025060943A (ja) | 2019-02-01 | 2024-12-27 | 神経認知障害を処置するための組成物及び方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20220111005A1 (https=) |
| EP (1) | EP3917539A4 (https=) |
| JP (2) | JP2022523913A (https=) |
| CA (1) | CA3128003A1 (https=) |
| IL (1) | IL285269A (https=) |
| MA (1) | MA54874A (https=) |
| WO (1) | WO2020160458A1 (https=) |
Families Citing this family (20)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP7013753B2 (ja) * | 2017-09-15 | 2022-02-01 | 株式会社三洋物産 | 遊技機 |
| JP7013754B2 (ja) * | 2017-09-15 | 2022-02-01 | 株式会社三洋物産 | 遊技機 |
| BR112021015817A2 (pt) | 2019-02-22 | 2021-10-13 | The Trustees Of The University Of Pennsylvania | Vírus adeno-associado recombinante para tratamento de neurodegeneração com início na idade adulta associado a grn |
| IL292382A (en) * | 2019-10-22 | 2022-06-01 | Applied Genetic Tech Corporation | Adeno-associated virus (aav) systems for treatment of progranulin associated neurodegenerative diseases or disorders |
| EP4146797A1 (en) * | 2020-05-06 | 2023-03-15 | Orchard Therapeutics (Europe) Limited | Treatment for neurodegenerative diseases |
| WO2021239308A1 (en) * | 2020-05-27 | 2021-12-02 | Universität Zürich | Viral vectors expressing therapeutic proteins specifically in myeloid cells and microglia |
| JP6879413B2 (ja) * | 2020-06-24 | 2021-06-02 | 株式会社三洋物産 | 遊技機 |
| US20240033332A1 (en) * | 2020-12-17 | 2024-02-01 | Kyoto University | Agent for activating a neuron |
| JP2021079226A (ja) * | 2021-03-01 | 2021-05-27 | 株式会社三洋物産 | 遊技機 |
| JP2021087833A (ja) * | 2021-03-01 | 2021-06-10 | 株式会社三洋物産 | 遊技機 |
| JP2021079225A (ja) * | 2021-03-01 | 2021-05-27 | 株式会社三洋物産 | 遊技機 |
| JP2021087836A (ja) * | 2021-03-01 | 2021-06-10 | 株式会社三洋物産 | 遊技機 |
| US20240342207A1 (en) * | 2021-08-02 | 2024-10-17 | Board Of Regents, The University Of Texas System | Modified nucleic acid compositions and associated methods for treatment of phenylketonuria |
| EP4504762A1 (en) * | 2022-04-08 | 2025-02-12 | Shape Therapeutics Inc. | Promoter switches for tissue-specific expression |
| JP7556433B2 (ja) * | 2022-08-22 | 2024-09-26 | 株式会社三洋物産 | 遊技機 |
| JP7556434B2 (ja) * | 2022-08-22 | 2024-09-26 | 株式会社三洋物産 | 遊技機 |
| JP7556432B2 (ja) * | 2022-08-22 | 2024-09-26 | 株式会社三洋物産 | 遊技機 |
| EP4680752A1 (en) * | 2023-03-14 | 2026-01-21 | UCB Biopharma SRL | Gene therapy |
| WO2024205404A1 (en) * | 2023-03-27 | 2024-10-03 | Sanquin IP B.V. | Novel capsid engineered aav vectors for liver-directed gene therapy |
| CN121313796A (zh) * | 2025-11-24 | 2026-01-13 | 北京大学 | 多肽grn-e及其在制备围绝经期情绪障碍的药物或制剂中的应用 |
Family Cites Families (14)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP0495831B1 (en) * | 1989-10-16 | 1997-01-15 | Hem Pharmaceuticals Corp. | Diagnosis and treatment of neuro-cognitive disorders associated with systemic immunological malfunction |
| MD1367C2 (ro) | 1992-11-13 | 2000-11-30 | Idec Pharmaceuticals Corporation | Metode de tratament al limfomului celulelor B, anticorpi anti-CD20, hibridom. |
| US20050163760A1 (en) * | 2001-12-06 | 2005-07-28 | Nathalie Cartier-Lacave | Use of cd34+ hematopoietic progenitor cells for the treatment of cns disorders |
| CA2653974A1 (en) * | 2006-05-30 | 2008-02-14 | Mayo Foundation For Medical Education And Research | Detecting and treating dementia |
| WO2007146046A2 (en) * | 2006-06-07 | 2007-12-21 | Genzyme Corporation | Gene therapy for amyotrophic lateral sclerosis and other spinal cord disorders |
| WO2009089635A1 (en) * | 2008-01-16 | 2009-07-23 | Neurodyn, Inc. | Treating neurodegenerative diseases with progranulin (pgrn) |
| WO2010022175A1 (en) * | 2008-08-19 | 2010-02-25 | Yale University | Identification of sortilin as a neuronal receptor for the frontotemporal dementia protein, progranulin |
| JP5879256B2 (ja) * | 2009-05-02 | 2016-03-08 | ジェンザイム・コーポレーション | 神経変性障害のための遺伝子治療 |
| US20110203007A1 (en) * | 2010-02-16 | 2011-08-18 | Board Of Supervisors Of Louisiana State University And Agricultural And Mechanical College | Assays of neurodegenerative disorders, including frontotemporal dementia and amyotrophic lateral sclerosis |
| US20150352185A1 (en) * | 2010-11-16 | 2015-12-10 | Denis G. Kay | Method for increasing neprilysin expression and activity |
| WO2017151884A1 (en) * | 2016-03-02 | 2017-09-08 | The Children's Hospital Of Philadelphia | Therapy for frontotemporal dementia |
| US20210284701A1 (en) * | 2016-07-14 | 2021-09-16 | Emory University | Granulin Compositions and Uses Related Thereto |
| AU2018236353B2 (en) | 2017-03-15 | 2023-12-21 | The Regents Of The University Of California | Methods of treating lysosomal disorders |
| BR112021015817A2 (pt) * | 2019-02-22 | 2021-10-13 | The Trustees Of The University Of Pennsylvania | Vírus adeno-associado recombinante para tratamento de neurodegeneração com início na idade adulta associado a grn |
-
2020
- 2020-01-31 US US17/427,298 patent/US20220111005A1/en active Pending
- 2020-01-31 JP JP2021544547A patent/JP2022523913A/ja active Pending
- 2020-01-31 WO PCT/US2020/016192 patent/WO2020160458A1/en not_active Ceased
- 2020-01-31 EP EP20748326.4A patent/EP3917539A4/en active Pending
- 2020-01-31 CA CA3128003A patent/CA3128003A1/en active Pending
- 2020-01-31 MA MA054874A patent/MA54874A/fr unknown
-
2021
- 2021-08-01 IL IL285269A patent/IL285269A/en unknown
-
2024
- 2024-12-27 JP JP2024231791A patent/JP2025060943A/ja active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JPWO2020160458A5 (https=) | ||
| AU2015364636B9 (en) | Gene therapy for Juvenile Batten Disease | |
| Kaufmann et al. | Gene therapy on the move | |
| JP2025015673A (ja) | 脊髄軟膜下遺伝子送達システム | |
| ES2615180T3 (es) | Métodos y composiciones para el tratamiento de enfermedades cerebrales | |
| JP2022508182A (ja) | 組換えウイルスベクター及びそれの産生のための核酸 | |
| EP3546584B1 (en) | Compositions for treating lysosmal storage disease (lsd) | |
| EP2500434A1 (en) | Capsid-free AAV vectors, compositions, and methods for vector production and gene delivery | |
| JP2017529854A (ja) | 高効率ゲノム編集のためのアデノ随伴ウイルスベクターバリアント及びその方法 | |
| JP2021517168A5 (https=) | ||
| Ruiz de Garibay et al. | Gene therapy for fabry disease: a review of the literature | |
| US20100111911A1 (en) | Mitochondrial nucleic acid delivery systems | |
| JPWO2020160468A5 (https=) | ||
| CN115461066B (zh) | 用于基因疗法的编码天冬氨酸酰化酶(aspa)的经修饰的核酸和载体 | |
| CN114072514A (zh) | 用于治疗atp酶介导的疾病的组合物和方法 | |
| JP7616668B2 (ja) | Ｕｂｅ３ａ遺伝子および発現カセットならびにそれらの使用 | |
| US20230190893A1 (en) | Compositions and methods for treating an inherited retinal disease | |
| Von Jonquieres et al. | Emerging concepts in vector development for glial gene therapy: implications for leukodystrophies | |
| JPWO2019173756A5 (https=) | ||
| JPWO2020160441A5 (https=) | ||
| US20240067942A1 (en) | Lysosomal acid lipase variants and uses thereof | |
| Silver et al. | Towards a rAAV-based gene therapy for ADA-SCID: from ADA deficiency to current and future treatment strategies | |
| US20240156873A1 (en) | Methods to genetically engineer hematopoietic stem and progenitor cells for red cell specific expression of therapeutic proteins | |
| Nandi et al. | Revolutionizing Gene Therapy: An Explicative Review on Engineering Adeno-associated Virus Vectors | |
| Segurado | Introduction to AAV‐based in vivo Gene Therapy |