JPWO2020112802A5 - - Google Patents
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- Publication number
- JPWO2020112802A5 JPWO2020112802A5 JP2021530800A JP2021530800A JPWO2020112802A5 JP WO2020112802 A5 JPWO2020112802 A5 JP WO2020112802A5 JP 2021530800 A JP2021530800 A JP 2021530800A JP 2021530800 A JP2021530800 A JP 2021530800A JP WO2020112802 A5 JPWO2020112802 A5 JP WO2020112802A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleic acid
- isolated nucleic
- injection
- vector
- subject
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2024128634A JP2024177670A (ja) | 2018-11-28 | 2024-08-05 | 神経変性疾患のための遺伝子治療 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862772230P | 2018-11-28 | 2018-11-28 | |
| US62/772,230 | 2018-11-28 | ||
| PCT/US2019/063289 WO2020112802A1 (en) | 2018-11-28 | 2019-11-26 | Gene therapies for neurodegenerative disease |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024128634A Division JP2024177670A (ja) | 2018-11-28 | 2024-08-05 | 神経変性疾患のための遺伝子治療 |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2022511453A JP2022511453A (ja) | 2022-01-31 |
| JP2022511453A5 JP2022511453A5 (https=) | 2022-11-21 |
| JPWO2020112802A5 true JPWO2020112802A5 (https=) | 2022-11-21 |
| JP7616995B2 JP7616995B2 (ja) | 2025-01-17 |
Family
ID=70852200
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021530800A Active JP7616995B2 (ja) | 2018-11-28 | 2019-11-26 | 神経変性疾患のための遺伝子治療 |
| JP2024128634A Withdrawn JP2024177670A (ja) | 2018-11-28 | 2024-08-05 | 神経変性疾患のための遺伝子治療 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024128634A Withdrawn JP2024177670A (ja) | 2018-11-28 | 2024-08-05 | 神経変性疾患のための遺伝子治療 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20220010001A1 (https=) |
| EP (1) | EP3887396A4 (https=) |
| JP (2) | JP7616995B2 (https=) |
| KR (1) | KR20210096168A (https=) |
| CN (1) | CN113557243A (https=) |
| AU (1) | AU2019388975A1 (https=) |
| BR (1) | BR112021010234A2 (https=) |
| CA (1) | CA3121211A1 (https=) |
| IL (1) | IL283496B2 (https=) |
| MX (1) | MX2021006253A (https=) |
| WO (1) | WO2020112802A1 (https=) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| BR112020006671A2 (pt) | 2017-10-03 | 2020-12-01 | Prevail Therapeutics, Inc. | terapias genéticas para distúrbios lisossômicos |
| KR102709597B1 (ko) | 2017-10-03 | 2024-09-26 | 프리베일 테라퓨틱스, 인크. | 리소좀 장애를 위한 유전자 요법 |
| EP4045653A1 (en) * | 2019-10-16 | 2022-08-24 | Cornell University | Gene therapy for alzheimer's disease |
| EP4232572A4 (en) * | 2020-10-22 | 2024-09-25 | Duke University | COMPOSITIONS AND PROCEDURES RELATED TO ALZHEIMER’S DISEASE |
| KR20230112672A (ko) * | 2020-11-25 | 2023-07-27 | 프리베일 테라퓨틱스, 인크. | 신경변성 질환을 위한 유전자 요법 |
| EP4426833A1 (en) * | 2021-11-03 | 2024-09-11 | F. Hoffmann-La Roche AG | Oligonucleotides for modulating apolipoprotein e4 expression |
| EP4615981A1 (en) | 2022-11-11 | 2025-09-17 | Eli Lilly and Company | Synthetic nucleic acids including astrocyte-directed promoter constructs and methods of using the same |
| CN119220609B (zh) * | 2024-09-27 | 2025-09-12 | 科辉智药(深圳)新药研究中心有限公司 | 一种共表达TRIM11和ApoE2的核酸序列构建体及其应用 |
Family Cites Families (14)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP3265577B2 (ja) * | 1992-10-13 | 2002-03-11 | デューク・ユニバーシティ | アポリポ蛋白ｅの４型イソ型の測定法 |
| AU2001253233B2 (en) * | 2000-04-06 | 2006-12-07 | Kos Pharmaceuticals, Inc. | Compounds and methods for lowering cholesterol levels without inducing hypertriglyceridemia |
| US20050019927A1 (en) * | 2003-07-13 | 2005-01-27 | Markus Hildinger | DECREASING GENE EXPRESSION IN A MAMMALIAN SUBJECT IN VIVO VIA AAV-MEDIATED RNAi EXPRESSION CASSETTE TRANSFER |
| US8435539B2 (en) * | 2004-02-13 | 2013-05-07 | Immunomedics, Inc. | Delivery system for cytotoxic drugs by bispecific antibody pretargeting |
| CA2643048A1 (en) * | 2006-02-21 | 2007-08-30 | Oklahoma Medical Research Foundation | Treatment of alzheimer's disease with inhibitors of apoe binding to apoe receptor |
| JP6469000B2 (ja) * | 2012-05-18 | 2019-02-13 | ユニバーシティー オブ アイオワ リサーチ ファウンデーション | アミロイドの沈着を処置するための方法および組成物 |
| WO2013181618A2 (en) * | 2012-05-31 | 2013-12-05 | The Trustees Of Columbia University In The City Of New York | Methods to treat alzheimer's disease using apoe inhibitors |
| EP3626309B1 (en) * | 2012-08-13 | 2023-03-08 | The Rockefeller University | Lxrbeta agonist for the treatment of cancer |
| MX2016006584A (es) * | 2013-11-20 | 2016-09-06 | Univ Iowa Res Found | Métodos y composiciones para tratar los depósitos de amiloide. |
| WO2015153760A2 (en) * | 2014-04-01 | 2015-10-08 | Sangamo Biosciences, Inc. | Methods and compositions for prevention or treatment of a nervous system disorder |
| EP3842514A1 (en) * | 2014-09-12 | 2021-06-30 | Whitehead Institute for Biomedical Research | Cells expressing apolipoprotein e and uses thereof |
| WO2018045347A1 (en) * | 2016-09-02 | 2018-03-08 | Spark Therapeutics, Inc. | Methods and vectors for treating cns disorders |
| KR102719222B1 (ko) * | 2017-05-11 | 2024-10-21 | 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 | 신경 세로이드 지질갈색소증에 대한 유전자 요법 |
| EP4045653A1 (en) * | 2019-10-16 | 2022-08-24 | Cornell University | Gene therapy for alzheimer's disease |
-
2019
- 2019-11-26 JP JP2021530800A patent/JP7616995B2/ja active Active
- 2019-11-26 MX MX2021006253A patent/MX2021006253A/es unknown
- 2019-11-26 CA CA3121211A patent/CA3121211A1/en active Pending
- 2019-11-26 US US17/297,492 patent/US20220010001A1/en not_active Abandoned
- 2019-11-26 AU AU2019388975A patent/AU2019388975A1/en active Pending
- 2019-11-26 EP EP19889757.1A patent/EP3887396A4/en active Pending
- 2019-11-26 CN CN201980086952.0A patent/CN113557243A/zh active Pending
- 2019-11-26 BR BR112021010234-5A patent/BR112021010234A2/pt unknown
- 2019-11-26 IL IL283496A patent/IL283496B2/en unknown
- 2019-11-26 KR KR1020217019516A patent/KR20210096168A/ko not_active Ceased
- 2019-11-26 WO PCT/US2019/063289 patent/WO2020112802A1/en not_active Ceased
-
2024
- 2024-08-05 JP JP2024128634A patent/JP2024177670A/ja not_active Withdrawn
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