JPWO2019204593A5 - - Google Patents
Download PDFInfo
- Publication number
- JPWO2019204593A5 JPWO2019204593A5 JP2020557222A JP2020557222A JPWO2019204593A5 JP WO2019204593 A5 JPWO2019204593 A5 JP WO2019204593A5 JP 2020557222 A JP2020557222 A JP 2020557222A JP 2020557222 A JP2020557222 A JP 2020557222A JP WO2019204593 A5 JPWO2019204593 A5 JP WO2019204593A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- composition
- composition according
- subject
- virus
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201862659281P | 2018-04-18 | 2018-04-18 | |
| US62/659,281 | 2018-04-18 | ||
| PCT/US2019/028108 WO2019204593A1 (en) | 2018-04-18 | 2019-04-18 | Gene therapy for diseases caused by unbalanced nucleotide pools including mitochondrial dna depletion syndromes |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2021522173A JP2021522173A (ja) | 2021-08-30 |
| JPWO2019204593A5 true JPWO2019204593A5 (ru) | 2022-04-18 |
Family
ID=68239912
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020557222A Pending JP2021522173A (ja) | 2018-04-18 | 2019-04-18 | ミトコンドリアｄｎａ枯渇症候群を含む不均衡ヌクレオチドプールに起因する疾患の遺伝子治療 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20210100917A1 (ru) |
| EP (1) | EP3781671A4 (ru) |
| JP (1) | JP2021522173A (ru) |
| KR (1) | KR20210009317A (ru) |
| CN (1) | CN112312929A (ru) |
| AU (1) | AU2019255745A1 (ru) |
| BR (1) | BR112020021324A2 (ru) |
| CA (1) | CA3097392A1 (ru) |
| CL (1) | CL2020002704A1 (ru) |
| CO (1) | CO2020014193A2 (ru) |
| MX (1) | MX2020010994A (ru) |
| WO (1) | WO2019204593A1 (ru) |
Families Citing this family (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20170174614A1 (en) | 2015-12-22 | 2017-06-22 | Zogenix International Limited | Metabolism resistant fenfluramine analogs and methods of using the same |
| KR102688278B1 (ko) | 2015-12-22 | 2024-07-26 | 조게닉스 인터내셔널 리미티드 | 펜플루라민 조성물 및 그 제조 방법 |
| RU2746000C2 (ru) | 2016-08-24 | 2021-04-05 | Зодженикс Интернэшнл Лимитед | Состав для ингибирования образования агонистов 5-ht2b и способы его применения |
| US10682317B2 (en) | 2017-09-26 | 2020-06-16 | Zogenix International Limited | Ketogenic diet compatible fenfluramine formulation |
| WO2019216919A1 (en) | 2018-05-11 | 2019-11-14 | Zogenix International Limited | Compositions and methods for treating seizure-induced sudden death |
| WO2021102104A1 (en) * | 2019-11-20 | 2021-05-27 | University Of Massachusetts | Aav-based delivery of thymine kinase 2 |
| US11612574B2 (en) | 2020-07-17 | 2023-03-28 | Zogenix International Limited | Method of treating patients infected with severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) |
| US20220096514A1 (en) * | 2020-09-29 | 2022-03-31 | Zogenix International Limited | Methods of treating thymidine kinase 2 deficiency by administering deoxycytidine and deoxythymidine |
| EP4313068A1 (en) * | 2021-03-26 | 2024-02-07 | Zogenix Mds, Inc. | Aqueous solutions containing purines and pyrimidines and uses thereof |
Family Cites Families (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN101460055A (zh) * | 2006-04-07 | 2009-06-17 | 得克萨斯大学体系董事会 | 和腺伴随病毒-噬菌体颗粒相关的方法和组合物 |
| US10292996B2 (en) * | 2015-03-26 | 2019-05-21 | The Trustees Of Columbia University In The City Of New York | Deoxyribonucleoside monophospate bypass therapy for mitochondrial DNA depletion syndrome |
-
2019
- 2019-04-18 MX MX2020010994A patent/MX2020010994A/es unknown
- 2019-04-18 AU AU2019255745A patent/AU2019255745A1/en active Pending
- 2019-04-18 BR BR112020021324-1A patent/BR112020021324A2/pt unknown
- 2019-04-18 WO PCT/US2019/028108 patent/WO2019204593A1/en unknown
- 2019-04-18 US US17/048,236 patent/US20210100917A1/en active Pending
- 2019-04-18 JP JP2020557222A patent/JP2021522173A/ja active Pending
- 2019-04-18 EP EP19787753.3A patent/EP3781671A4/en active Pending
- 2019-04-18 CA CA3097392A patent/CA3097392A1/en active Pending
- 2019-04-18 KR KR1020207032655A patent/KR20210009317A/ko unknown
- 2019-04-18 CN CN201980039834.4A patent/CN112312929A/zh active Pending
-
2020
- 2020-10-19 CL CL2020002704A patent/CL2020002704A1/es unknown
- 2020-11-17 CO CONC2020/0014193A patent/CO2020014193A2/es unknown
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2022068181A5 (ru) | ||
| RU2021102893A (ru) | Модифицированные гены атаксии фридрейха и векторы для генной терапии | |
| JP2021106619A5 (ru) | ||
| FI3684423T3 (fi) | Adenoassesioidun viruksen kapsidivariantteja ja niiden käyttömenetelmiä | |
| RU2017115477A (ru) | Полинуклеотиды aadc для лечения болезни паркинсона | |
| JP2018148927A5 (ru) | ||
| JP2019511570A5 (ru) | ||
| JP2020522269A5 (ru) | ||
| JP2022060228A5 (ru) | ||
| JPWO2020206189A5 (ru) | ||
| JP2019513399A5 (ru) | ||
| JPWO2019204593A5 (ru) | ||
| JPWO2020106916A5 (ru) | ||
| FI3773744T3 (fi) | Koostumukset ja menetelmät vallitsevasti perityn katekoliamiiniherkän polymorfisen kammiotakykardian hoitoon | |
| JP2020510433A5 (ru) | ||
| JPWO2021067448A5 (ru) | ||
| JPWO2021053222A5 (ru) | ||
| JP2023065516A5 (ru) | ||
| JPWO2019153009A5 (ru) | ||
| FI3177313T3 (fi) | Telomeraasi-käänteistranskriptaasipohjaisia hoitoja sydäninfarktiin liittyvien tilojen hoitamiseksi | |
| JPWO2020214609A5 (ru) | ||
| JP2020533313A5 (ru) | ||
| JPWO2020232297A5 (ru) | ||
| JPWO2021221995A5 (ru) | ||
| JP2020519251A5 (ru) |