JP7832758B2 - Ｎｔ－３遺伝子治療のための方法及び材料 - Google Patents

Ｎｔ－３遺伝子治療のための方法及び材料

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JP7832758B2
JP7832758B2 JP2020522007A JP2020522007A JP7832758B2 JP 7832758 B2 JP7832758 B2 JP 7832758B2 JP 2020522007 A JP2020522007 A JP 2020522007A JP 2020522007 A JP2020522007 A JP 2020522007A JP 7832758 B2 JP7832758 B2 JP 7832758B2
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muscle
raav
aav
nucleic acid
tmck
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JP2021500029A5 (https=
JP2021500029A (ja
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ザリフェ サヘンク，
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リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル
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JP2020522007A 2017-10-20 2018-10-19 Ｎｔ－３遺伝子治療のための方法及び材料 Active JP7832758B2 (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2023151106A JP2023166580A (ja) 2017-10-20 2023-09-19 Ｎｔ－３遺伝子治療のための方法及び材料
JP2025127206A JP2025157575A (ja) 2017-10-20 2025-07-30 Ｎｔ－３遺伝子治療のための方法及び材料

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762574828P 2017-10-20 2017-10-20
US62/574,828 2017-10-20
US201862676687P 2018-05-25 2018-05-25
US62/676,687 2018-05-25
US201862741335P 2018-10-04 2018-10-04
US62/741,335 2018-10-04
PCT/US2018/056765 WO2019079755A1 (en) 2017-10-20 2018-10-19 METHODS AND MATERIALS FOR NT-3 GENE THERAPY

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JP2023151106A Division JP2023166580A (ja) 2017-10-20 2023-09-19 Ｎｔ－３遺伝子治療のための方法及び材料

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JP2021500029A JP2021500029A (ja) 2021-01-07
JP2021500029A5 JP2021500029A5 (https=) 2021-12-02
JP7832758B2 true JP7832758B2 (ja) 2026-03-18

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JP2020522007A Active JP7832758B2 (ja) 2017-10-20 2018-10-19 Ｎｔ－３遺伝子治療のための方法及び材料
JP2023151106A Pending JP2023166580A (ja) 2017-10-20 2023-09-19 Ｎｔ－３遺伝子治療のための方法及び材料
JP2025127206A Pending JP2025157575A (ja) 2017-10-20 2025-07-30 Ｎｔ－３遺伝子治療のための方法及び材料

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JP2023151106A Pending JP2023166580A (ja) 2017-10-20 2023-09-19 Ｎｔ－３遺伝子治療のための方法及び材料
JP2025127206A Pending JP2025157575A (ja) 2017-10-20 2025-07-30 Ｎｔ－３遺伝子治療のための方法及び材料

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US (2) US11926653B2 (https=)
EP (1) EP3697916A4 (https=)
JP (3) JP7832758B2 (https=)
KR (2) KR20200083495A (https=)
CN (2) CN119193705A (https=)
AU (2) AU2018351528B2 (https=)
BR (1) BR112020007790A2 (https=)
CA (1) CA3079416A1 (https=)
CL (1) CL2020001060A1 (https=)
CO (1) CO2020006148A2 (https=)
IL (2) IL321310A (https=)
MA (1) MA50412A (https=)
MX (2) MX2020004035A (https=)
MY (1) MY207563A (https=)
SA (1) SA520411798B1 (https=)
SG (1) SG11202003285PA (https=)
TW (1) TWI879721B (https=)
WO (1) WO2019079755A1 (https=)

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CA3005633C (en) 2015-11-16 2023-11-21 Research Institute Of Nationwide Children's Hospital Materials and methods for treatment of titin-based myopathies and other titinopathies
MX2020007876A (es) 2018-01-31 2020-12-03 Res Inst Nationwide Childrens Hospital Terapia genica para la distrofia muscular de cinturas tipo 2c.
MX2020014119A (es) 2018-06-29 2021-06-18 Res Inst Nationwide Childrens Hospital Productos y métodos de virus adenoasociado recombinante para el tratamiento de la distrofia muscular de cinturas 2a.
JP2022523038A (ja) * 2019-02-02 2022-04-21 ユニバーシティ オブ ピッツバーグ －オブ ザ コモンウェルス システム オブ ハイヤー エデュケイション 遺伝子置換及び抗炎症を介したデュシェンヌ型筋ジストロフィーに対する一段階遺伝子療法
MX2021010356A (es) 2019-02-26 2022-03-04 Res Inst Nationwide Childrens Hospital SUMINISTRO DE ß-SARCOGLICANO MEDIANTE VECTORES DE VIRUS ADENOASOCIADO Y EL TRATAMIENTO DE LA DISTROFIA MUSCULAR.
GB201907882D0 (en) * 2019-06-03 2019-07-17 Cyprus Foundation For Muscular Dystrophy Res Methods
PT4017871T (pt) 2019-08-21 2024-04-22 Res Inst Nationwide Childrens Hospital Distribuição de vetor de vírus adeno-associado de alfasarcoglicano e o tratamento da distrofia muscular
EP4025258A4 (en) * 2019-09-03 2023-09-06 University of Cincinnati METHODS AND COMPOSITIONS FOR THE TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS
WO2021211713A1 (en) * 2020-04-14 2021-10-21 Research Institute At Nationwide Children's Hospital Treatment of charcot-marie-tooth axonal type 2d using nt-3 gene therapy
WO2021211705A1 (en) * 2020-04-14 2021-10-21 Research Institute At Nationwide Children's Hospital Treatment of sarcopenia using nt-3 gene therapy
CN111514279B (zh) * 2020-06-16 2023-07-18 温州医科大学附属第二医院（温州医科大学附属育英儿童医院） 神经营养因子3在制备治疗男性性腺功能减退症的药物中的应用
EP4108263A3 (en) * 2021-06-02 2023-03-22 Research Institute at Nationwide Children's Hospital Recombinant adeno-associated virus products and methods for treating limb girdle muscular dystrophy 2a
JP2023059858A (ja) 2021-10-15 2023-04-27 リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル 自己相補的アデノ随伴ウイルスベクター及び筋ジストロフィーの治療におけるその使用
CN115838725B (zh) * 2022-12-30 2023-09-08 广州派真生物技术有限公司 在哺乳动物心脏中特异性启动基因的启动子序列及其应用
WO2024229115A1 (en) * 2023-05-02 2024-11-07 Research Institute At Nationwide Children's Hospital Treatment of multiple sclerosis using nt-3 gene therapy
AU2024265705A1 (en) 2023-05-02 2025-11-20 Research Institute At Nationwide Children's Hospital Gene therapy for treatment of protein misfolding diseases
CN119899809A (zh) * 2025-01-07 2025-04-29 广州派真生物技术有限公司 一种提高重组腺相关病毒生产效率的方法及应用

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