JP7563694B2 - 優性網膜色素変性症の処置のための組成物および方法 - Google Patents

優性網膜色素変性症の処置のための組成物および方法 Download PDF

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JP7563694B2
JP7563694B2 JP2020567085A JP2020567085A JP7563694B2 JP 7563694 B2 JP7563694 B2 JP 7563694B2 JP 2020567085 A JP2020567085 A JP 2020567085A JP 2020567085 A JP2020567085 A JP 2020567085A JP 7563694 B2 JP7563694 B2 JP 7563694B2
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rho
vector
seq
shrna
nucleotide sequence
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JP2021525531A (ja
JP2021525531A5 (https=
JPWO2019232517A5 (https=
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レーウィン，アルフレッド，エス．
ハウスワース，ウィリアム，ダブリュー．
マッセンギル，マイケル，ティー．
ベルトラン，ウィリアム
アグイッレ，グスターボ，ディー．
シデシアン，アーサー
ヤコブソン，サミュエル
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University of Florida Research Foundation Inc
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JP2020567085A 2018-06-01 2019-06-03 優性網膜色素変性症の処置のための組成物および方法 Active JP7563694B2 (ja)

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US201862679585P 2018-06-01 2018-06-01
US62/679,585 2018-06-01
US201962809539P 2019-02-22 2019-02-22
US62/809,539 2019-02-22
PCT/US2019/035159 WO2019232517A1 (en) 2018-06-01 2019-06-03 Compositions and methods for treatment of dominant retinitis pigmentosa

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CN114521214A (zh) * 2020-07-24 2022-05-20 尔知渃米斯股份有限公司 视紫红质转录体特异性反式剪接核酶及其用途
JP7334346B2 (ja) * 2020-07-24 2023-08-28 アールズィーノミクス・インコーポレイテッド ロドプシン転写体に特異的なトランススプライシングリボザイム及びその用途
US20220098615A1 (en) * 2020-09-30 2022-03-31 NGGT, Inc. Dual functional expression vectors and methods of use thereof
WO2024211266A1 (en) * 2023-04-07 2024-10-10 University Of Houston System Downregulation of rhodopsin as a therapeutic strategy for peripherin-2-associated inherited retinal disorders

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IL279091B1 (en) 2026-01-01
IL279091A (en) 2021-01-31
JP2021525531A (ja) 2021-09-27
US20250215437A1 (en) 2025-07-03
WO2019232517A1 (en) 2019-12-05
US12203074B2 (en) 2025-01-21
US20210207147A1 (en) 2021-07-08
AU2019276645A1 (en) 2020-11-26
EP3802836A4 (en) 2022-10-19
EP3802836A1 (en) 2021-04-14
CN118480544A (zh) 2024-08-13
CN112204145A (zh) 2021-01-08
AU2019276645B2 (en) 2025-06-26
CN112204145B (zh) 2024-03-26
CA3102095A1 (en) 2019-12-05

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