JP7476199B2 - Ｓｃｎ１ａ脳症の治療のためのｓｃｎ２ａを標的とするアンチセンスオリゴヌクレオチド - Google Patents

Ｓｃｎ１ａ脳症の治療のためのｓｃｎ２ａを標的とするアンチセンスオリゴヌクレオチド Download PDF

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JP7476199B2
JP7476199B2 JP2021533377A JP2021533377A JP7476199B2 JP 7476199 B2 JP7476199 B2 JP 7476199B2 JP 2021533377 A JP2021533377 A JP 2021533377A JP 2021533377 A JP2021533377 A JP 2021533377A JP 7476199 B2 JP7476199 B2 JP 7476199B2
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oligonucleotide
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スティーブン ペトロー，
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ロジコン， インコーポレイテッド
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JP2021533377A 2018-08-20 2019-08-20 Ｓｃｎ１ａ脳症の治療のためのｓｃｎ２ａを標的とするアンチセンスオリゴヌクレオチド Active JP7476199B2 (ja)

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JP2024066672A JP7851349B2 (ja) 2018-08-20 2024-04-17 Ｓｃｎ１ａ脳症の治療のためのｓｃｎ２ａを標的とするアンチセンスオリゴヌクレオチド

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US201862765344P 2018-08-20 2018-08-20
US62/765,344 2018-08-20
PCT/US2019/047313 WO2020041348A1 (en) 2018-08-20 2019-08-20 Antisense oligonucleotides targeting scn2a for the treatment of scn1a encephalopathies

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JP2021535204A5 JP2021535204A5 (enExample) 2022-08-03
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JP2024066672A Active JP7851349B2 (ja) 2018-08-20 2024-04-17 Ｓｃｎ１ａ脳症の治療のためのｓｃｎ２ａを標的とするアンチセンスオリゴヌクレオチド

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EP4110919A4 (en) * 2020-02-28 2024-06-05 Ionis Pharmaceuticals, Inc. COMPOUNDS AND METHODS FOR MODULATING SCN1A EXPRESSION
CN115867657A (zh) 2020-05-11 2023-03-28 斯托克制药公司 用于治疗疾患和疾病的opa1反义寡聚物
KR20230095056A (ko) * 2020-07-22 2023-06-28 더 플로레이 인스티튜트 오브 뉴로사이언스 앤드 멘탈 헬스 Scn2a에서 기능-상실 돌연변이와 연관된 장애를 치료하기 위한 조성물 및 방법
IL300258A (en) * 2020-08-07 2023-03-01 Ionis Pharmaceuticals Inc Compounds and methods for modulating SCN2A
EP4155402A1 (en) 2021-09-22 2023-03-29 Royal College of Surgeons in Ireland Modulation of microrna-335 for the treatment of sodium channelopathies
KR20250087733A (ko) * 2022-07-29 2025-06-16 스톡 테라퓨틱스, 인크. 병태 및 질환의 치료를 위한 화합물
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