JP6637961B2 - Ｍｙｈ７ｂの阻害剤およびその使用 - Google Patents
Ｍｙｈ７ｂの阻害剤およびその使用 Download PDFInfo
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- JP6637961B2 JP6637961B2 JP2017506382A JP2017506382A JP6637961B2 JP 6637961 B2 JP6637961 B2 JP 6637961B2 JP 2017506382 A JP2017506382 A JP 2017506382A JP 2017506382 A JP2017506382 A JP 2017506382A JP 6637961 B2 JP6637961 B2 JP 6637961B2
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- Prior art keywords
- antisense oligonucleotide
- nucleotides
- myh7b
- sequence
- inhibitor
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Landscapes
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| GB2547586A (en) * | 2014-08-20 | 2017-08-23 | Lifesplice Pharma Llc | Splice modulating oligonucleotides and methods of use thereof(In the PCT request) |
| US11015196B2 (en) | 2016-05-20 | 2021-05-25 | The General Hospital Corporation | Using microRNAs to control activation status of hepatic stellate cells and to prevent fibrosis in progressive liver diseases |
| WO2018102397A1 (en) | 2016-11-29 | 2018-06-07 | PureTech Health LLC | Exosomes for delivery of therapeutic agents |
| EP3728562A4 (en) * | 2017-12-19 | 2021-09-29 | The Regents of The University of Michigan | HEART MICROTISSUE AND ASSOCIATED USES |
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| AU2019316103B2 (en) | 2018-08-02 | 2026-02-19 | Dyne Therapeutics, Inc. | Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy |
| US12018087B2 (en) | 2018-08-02 | 2024-06-25 | Dyne Therapeutics, Inc. | Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject |
| US11638761B2 (en) | 2021-07-09 | 2023-05-02 | Dyne Therapeutics, Inc. | Muscle targeting complexes and uses thereof for treating Facioscapulohumeral muscular dystrophy |
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| US5981505A (en) | 1993-01-26 | 1999-11-09 | The Trustees Of The University Of Pennsylvania | Compositions and methods for delivery of genetic material |
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| WO2016022536A3 (en) | 2016-03-31 |
| US10144930B2 (en) | 2018-12-04 |
| US9752144B2 (en) | 2017-09-05 |
| US20180094262A1 (en) | 2018-04-05 |
| EP3177327A4 (en) | 2018-03-14 |
| CA2957618A1 (en) | 2016-02-11 |
| CN108064175A (zh) | 2018-05-22 |
| KR20170042625A (ko) | 2017-04-19 |
| AU2015301221B2 (en) | 2020-07-02 |
| AU2015301221A1 (en) | 2017-03-02 |
| TW201614069A (en) | 2016-04-16 |
| AR101449A1 (es) | 2016-12-21 |
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