JP6518197B2 - バース症候群の予防または治療のための方法及び組成物 - Google Patents

バース症候群の予防または治療のための方法及び組成物 Download PDF

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JP6518197B2
JP6518197B2 JP2015560377A JP2015560377A JP6518197B2 JP 6518197 B2 JP6518197 B2 JP 6518197B2 JP 2015560377 A JP2015560377 A JP 2015560377A JP 2015560377 A JP2015560377 A JP 2015560377A JP 6518197 B2 JP6518197 B2 JP 6518197B2
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taz1
peptide
aromatic
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JP2016511259A (ja
JP2016511259A5 (https=
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ディー トラヴィス ウィルソン
ディー トラヴィス ウィルソン
マーク バンバーガー
マーク バンバーガー
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ステルス バイオセラピューティックス コープ
ステルス バイオセラピューティックス コープ
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    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00—Medicinal preparations containing peptides
    • A61K38/04—Peptides having up to 20 amino acids in a fully defined sequence; Derivatives thereof
    • A61K38/06—Tripeptides
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00—Medicinal preparations containing peptides
    • A61K38/04—Peptides having up to 20 amino acids in a fully defined sequence; Derivatives thereof
    • A61K38/07—Tetrapeptides
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K45/00—Medicinal preparations containing active ingredients not provided for in groups A61K31/00 - A61K41/00
    • A61K45/06—Mixtures of active ingredients without chemical characterisation, e.g. antiphlogistics and cardiaca
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P11/00—Drugs for disorders of the respiratory system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P7/00—Drugs for disorders of the blood or the extracellular fluid
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00—Drugs for disorders of the cardiovascular system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P9/00—Drugs for disorders of the cardiovascular system
    • A61P9/04—Inotropic agents, i.e. stimulants of cardiac contraction; Drugs for heart failure

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  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Animal Behavior & Ethology (AREA)
  • General Health & Medical Sciences (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Engineering & Computer Science (AREA)
  • Epidemiology (AREA)
  • Organic Chemistry (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Immunology (AREA)
  • Cardiology (AREA)
  • Heart & Thoracic Surgery (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Hospice & Palliative Care (AREA)
  • Neurology (AREA)
  • Pulmonology (AREA)
  • Diabetes (AREA)
  • Hematology (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Peptides Or Proteins (AREA)
JP2015560377A 2013-03-01 2014-02-28 バース症候群の予防または治療のための方法及び組成物 Active JP6518197B2 (ja)

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US201361771642P 2013-03-01 2013-03-01
US201361771534P 2013-03-01 2013-03-01
US61/771,534 2013-03-01
US61/771,642 2013-03-01
US201361839753P 2013-06-26 2013-06-26
US61/839,753 2013-06-26
PCT/US2014/019622 WO2014134554A1 (en) 2013-03-01 2014-02-28 Methods and compositions for the prevention or treatment of barth syndrome

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JP2016511259A JP2016511259A (ja) 2016-04-14
JP2016511259A5 JP2016511259A5 (https=) 2017-04-06
JP6518197B2 true JP6518197B2 (ja) 2019-05-22

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JP2019080101A Active JP6918046B2 (ja) 2013-03-01 2019-04-19 バース症候群の予防または治療のための方法及び組成物
JP2021019903A Active JP7072692B2 (ja) 2013-03-01 2021-02-10 バース症候群の予防または治療のための方法及び組成物
JP2022077425A Active JP7381652B2 (ja) 2013-03-01 2022-05-10 バース症候群の予防または治療のための方法及び組成物

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JP2021019903A Active JP7072692B2 (ja) 2013-03-01 2021-02-10 バース症候群の予防または治療のための方法及び組成物
JP2022077425A Active JP7381652B2 (ja) 2013-03-01 2022-05-10 バース症候群の予防または治療のための方法及び組成物

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Country Link
US (6) US9687519B2 (https=)
EP (2) EP3626252A1 (https=)
JP (4) JP6518197B2 (https=)
CN (3) CN105407906A (https=)
CA (1) CA2916880C (https=)
DK (1) DK2961420T3 (https=)
ES (1) ES2750258T3 (https=)
HU (1) HUE046924T2 (https=)
WO (1) WO2014134554A1 (https=)

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Also Published As

Publication number Publication date
US20200345803A1 (en) 2020-11-05
DK2961420T3 (da) 2019-10-07
CN105407906A (zh) 2016-03-16
JP2016511259A (ja) 2016-04-14
JP2022116008A (ja) 2022-08-09
JP7072692B2 (ja) 2022-05-20
US11083771B2 (en) 2021-08-10
EP2961420B1 (en) 2019-09-11
JP2019147815A (ja) 2019-09-05
US9687519B2 (en) 2017-06-27
CA2916880C (en) 2021-02-09
US11771734B2 (en) 2023-10-03
US20240156892A1 (en) 2024-05-16
CA2916880A1 (en) 2014-09-04
CN115990241A (zh) 2023-04-21
JP2021098704A (ja) 2021-07-01
US20160228487A1 (en) 2016-08-11
US20180147251A1 (en) 2018-05-31
JP6918046B2 (ja) 2021-08-11
EP3626252A1 (en) 2020-03-25
WO2014134554A1 (en) 2014-09-04
CN115990242A (zh) 2023-04-21
US12268724B2 (en) 2025-04-08
US20210401923A1 (en) 2021-12-30
US11083772B2 (en) 2021-08-10
EP2961420A1 (en) 2016-01-06
JP7381652B2 (ja) 2023-11-15
HUE046924T2 (hu) 2020-03-30
ES2750258T3 (es) 2020-03-25
EP2961420A4 (en) 2016-08-17
US20260061023A1 (en) 2026-03-05

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