JP5706602B2 - ニーマンピック病ａ型に対する遺伝子治療 - Google Patents

ニーマンピック病ａ型に対する遺伝子治療 Download PDF

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JP5706602B2
JP5706602B2 JP2008554342A JP2008554342A JP5706602B2 JP 5706602 B2 JP5706602 B2 JP 5706602B2 JP 2008554342 A JP2008554342 A JP 2008554342A JP 2008554342 A JP2008554342 A JP 2008554342A JP 5706602 B2 JP5706602 B2 JP 5706602B2
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brain
transgene
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JP2009526067A (ja
JP2009526067A5 (enExample
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マルコ・エイ・パッシーニ
ロビン・ジェイ・ジーグラー
ジェイムズ・ドッジ
ラムヤ・シハブッディン
セン・エイチ・チェン
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Genzyme Corp
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JP2008554342A 2006-02-08 2007-02-08 ニーマンピック病ａ型に対する遺伝子治療 Active JP5706602B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US77162806P 2006-02-08 2006-02-08
US60/771,628 2006-02-08
US77236006P 2006-02-09 2006-02-09
US60/772,360 2006-02-09
PCT/US2007/003388 WO2007092563A2 (en) 2006-02-08 2007-02-08 Gene therapy for niemann-pick disease type a

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JP2013092907A Division JP5881641B2 (ja) 2006-02-08 2013-04-25 ニーマンピック病ａ型に対する遺伝子治療

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JP2009526067A JP2009526067A (ja) 2009-07-16
JP2009526067A5 JP2009526067A5 (enExample) 2010-04-08
JP5706602B2 true JP5706602B2 (ja) 2015-04-22

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JP2013092907A Active JP5881641B2 (ja) 2006-02-08 2013-04-25 ニーマンピック病ａ型に対する遺伝子治療

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US (3) US20090117156A1 (enExample)
EP (2) EP1986661B1 (enExample)
JP (2) JP5706602B2 (enExample)
AR (1) AR059371A1 (enExample)
BR (1) BRPI0707590A2 (enExample)
CY (1) CY1121380T1 (enExample)
DK (1) DK1986661T3 (enExample)
ES (1) ES2700048T3 (enExample)
HU (1) HUE041928T2 (enExample)
IL (2) IL193165B (enExample)
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PT (1) PT1986661T (enExample)
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RU2020140209A (ru) 2014-10-21 2021-01-25 Юниверсити Оф Массачусетс Варианты рекомбинантных aav и их применения
JP6879486B2 (ja) * 2015-03-17 2021-06-02 フリーイェ・ユニヴェルシテイト・ブリュッセルＶｒｉｊｅ Ｕｎｉｖｅｒｓｉｅｉｔ Ｂｒｕｓｓｅｌ Ｆｖｉｉｉおよびｆｉｘ用の最適化された肝臓特異的発現系
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CN112543766A (zh) 2018-04-03 2021-03-23 斯特里迪比奥公司 抗体逃避性病毒载体
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PH12021552661A1 (en) * 2019-04-24 2023-02-27 Univ Oregon Health & Science Promoter sequence and related products and uses thereof
TW202128736A (zh) 2019-10-17 2021-08-01 美商史崔德生物公司 用於治療ｃ型尼曼—匹克病之腺相關病毒載體
CN116209477A (zh) * 2020-06-30 2023-06-02 儿童国家医疗中心 使用重组人酸性鞘氨醇酶改善骨骼肌纤维的修复
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JP2013166777A (ja) 2013-08-29
JP2009526067A (ja) 2009-07-16
JP5881641B2 (ja) 2016-03-09
EP3456331B1 (en) 2021-05-26
AR059371A1 (es) 2008-03-26
PT1986661T (pt) 2018-12-05
US20200080066A1 (en) 2020-03-12
HUE041928T2 (hu) 2019-06-28
LT1986661T (lt) 2018-12-10
EP3456331A1 (en) 2019-03-20
EP1986661A2 (en) 2008-11-05
IL193165B (en) 2018-04-30
WO2007092563A2 (en) 2007-08-16
DK1986661T3 (da) 2019-01-02
MX2018008355A (es) 2021-06-15
CY1121380T1 (el) 2020-05-29
US20230287366A1 (en) 2023-09-14
MX360595B (es) 2018-11-09
BRPI0707590A2 (pt) 2011-05-10
PL1986661T3 (pl) 2019-02-28
IL258587A (en) 2018-06-28
US20090117156A1 (en) 2009-05-07
ES2700048T3 (es) 2019-02-13
EP1986661A4 (en) 2012-04-25
MX2018013684A (es) 2021-06-15
WO2007092563A3 (en) 2007-11-22
EP1986661B1 (en) 2018-08-29
SI1986661T1 (sl) 2018-12-31

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