JP2025516639A - ＡＩＭＰ２－ＤＸ２および必要に応じてｍｉＲ－１４２に対する標的配列を使用して網膜変性疾患を処置する方法ならびにその組成物 - Google Patents

ＡＩＭＰ２－ＤＸ２および必要に応じてｍｉＲ－１４２に対する標的配列を使用して網膜変性疾患を処置する方法ならびにその組成物 Download PDF

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JP2025516639A
JP2025516639A JP2024566533A JP2024566533A JP2025516639A JP 2025516639 A JP2025516639 A JP 2025516639A JP 2024566533 A JP2024566533 A JP 2024566533A JP 2024566533 A JP2024566533 A JP 2024566533A JP 2025516639 A JP2025516639 A JP 2025516639A
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aimp2
promoter
mir
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seq
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JP2025516639A5 (enExample
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ジン ウ チェ，
キュンファ ベク，
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ジェネロス カンパニー， リミテッド
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JP2024566533A 2022-05-13 2023-05-13 ＡＩＭＰ２－ＤＸ２および必要に応じてｍｉＲ－１４２に対する標的配列を使用して網膜変性疾患を処置する方法ならびにその組成物 Pending JP2025516639A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263341798P 2022-05-13 2022-05-13
US63/341,798 2022-05-13
PCT/IB2023/054956 WO2023218430A1 (en) 2022-05-13 2023-05-13 Methods of treating retinal degenerative diseases using aimp2-dx2 and optionally a target sequence for mir‑142 and compositions thereof

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JP2025516639A true JP2025516639A (ja) 2025-05-30
JP2025516639A5 JP2025516639A5 (enExample) 2026-05-21

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US (1) US20250281573A1 (enExample)
EP (1) EP4522226A4 (enExample)
JP (1) JP2025516639A (enExample)
KR (1) KR20250021321A (enExample)
CN (1) CN119343154A (enExample)
WO (1) WO2023218430A1 (enExample)

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* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4221760A4 (en) * 2020-09-30 2025-08-13 Generoath Co Ltd METHODS OF TREATING AGE-RELATED MACULAR DISEASES USING AIMP2-DX2 AND OPTIONALLY A TARGET SEQUENCE FOR MIR-142 AND RELATED COMPOSITIONS

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7459529B2 (en) * 2004-11-24 2008-12-02 Seoul National University Industry Foundation AIMP2-DX2 and its uses
DK2002003T3 (en) * 2005-05-27 2016-03-21 Ospedale San Raffaele Srl Gene vector comprising miRNA
CN107184594A (zh) * 2017-06-02 2017-09-22 青岛大学 miR‑142‑3p用于预防和/或治疗心脏疾病的组合物及应用
KR102248420B1 (ko) * 2019-03-15 2021-05-06 주식회사 제너로스 miR-142-3p의 표적 서열을 포함하는 재조합 벡터
KR20220035693A (ko) * 2020-09-14 2022-03-22 주식회사 제너로스 표적화된 유전자 전달을 위한 아데노-부속 바이러스 벡터
JP2023541168A (ja) * 2020-09-14 2023-09-28 ジェネロス カンパニー， リミテッド 改良された生着可能性を有する幹細胞を調製するための方法
KR102626543B1 (ko) * 2020-09-14 2024-01-23 주식회사 제너로스 AIMP2-DX2 및 miR-142의 표적 핵산을 포함하는 재조합 벡터
MA71714A (fr) * 2020-09-30 2025-05-30 Generoath Co., Ltd. Méthodes de traitement de maladies neuronales à l'aide d'aimp2-dx2 et éventuellement d'une séquence cible de mir-142 et compositions associées
EP4221760A4 (en) * 2020-09-30 2025-08-13 Generoath Co Ltd METHODS OF TREATING AGE-RELATED MACULAR DISEASES USING AIMP2-DX2 AND OPTIONALLY A TARGET SEQUENCE FOR MIR-142 AND RELATED COMPOSITIONS

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KR20250021321A (ko) 2025-02-12
CN119343154A (zh) 2025-01-21
US20250281573A1 (en) 2025-09-11
EP4522226A1 (en) 2025-03-19
EP4522226A4 (en) 2026-06-03
WO2023218430A1 (en) 2023-11-16

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