CN119343154A - 使用AIMP2-DX2和任选的miR-142靶序列及其组合物治疗视网膜退行性疾病的方法 - Google Patents

使用AIMP2-DX2和任选的miR-142靶序列及其组合物治疗视网膜退行性疾病的方法 Download PDF

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CN119343154A
CN119343154A CN202380039975.2A CN202380039975A CN119343154A CN 119343154 A CN119343154 A CN 119343154A CN 202380039975 A CN202380039975 A CN 202380039975A CN 119343154 A CN119343154 A CN 119343154A
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aimp2
promoter
mir
cells
gene
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崔镇宇
白京和
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Genelotti Inc
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CN202380039975.2A 2022-05-13 2023-05-13 使用AIMP2-DX2和任选的miR-142靶序列及其组合物治疗视网膜退行性疾病的方法 Pending CN119343154A (zh)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263341798P 2022-05-13 2022-05-13
US63/341,798 2022-05-13
PCT/IB2023/054956 WO2023218430A1 (en) 2022-05-13 2023-05-13 Methods of treating retinal degenerative diseases using aimp2-dx2 and optionally a target sequence for mir‑142 and compositions thereof

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CN119343154A true CN119343154A (zh) 2025-01-21

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CN202380039975.2A Pending CN119343154A (zh) 2022-05-13 2023-05-13 使用AIMP2-DX2和任选的miR-142靶序列及其组合物治疗视网膜退行性疾病的方法

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US (1) US20250281573A1 (enExample)
EP (1) EP4522226A4 (enExample)
JP (1) JP2025516639A (enExample)
KR (1) KR20250021321A (enExample)
CN (1) CN119343154A (enExample)
WO (1) WO2023218430A1 (enExample)

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN116406304A (zh) * 2020-09-30 2023-07-07 杰内罗蒂股份有限公司 使用AIMP2-DX2和任选地miR-142的靶序列及其组合物治疗年龄相关的黄斑疾病的方法

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7459529B2 (en) * 2004-11-24 2008-12-02 Seoul National University Industry Foundation AIMP2-DX2 and its uses
DK2002003T3 (en) * 2005-05-27 2016-03-21 Ospedale San Raffaele Srl Gene vector comprising miRNA
CN107184594A (zh) * 2017-06-02 2017-09-22 青岛大学 miR‑142‑3p用于预防和/或治疗心脏疾病的组合物及应用
KR102248420B1 (ko) * 2019-03-15 2021-05-06 주식회사 제너로스 miR-142-3p의 표적 서열을 포함하는 재조합 벡터
KR20220035693A (ko) * 2020-09-14 2022-03-22 주식회사 제너로스 표적화된 유전자 전달을 위한 아데노-부속 바이러스 벡터
JP2023541168A (ja) * 2020-09-14 2023-09-28 ジェネロス カンパニー， リミテッド 改良された生着可能性を有する幹細胞を調製するための方法
KR102626543B1 (ko) * 2020-09-14 2024-01-23 주식회사 제너로스 AIMP2-DX2 및 miR-142의 표적 핵산을 포함하는 재조합 벡터
MA71714A (fr) * 2020-09-30 2025-05-30 Generoath Co., Ltd. Méthodes de traitement de maladies neuronales à l'aide d'aimp2-dx2 et éventuellement d'une séquence cible de mir-142 et compositions associées
EP4221760A4 (en) * 2020-09-30 2025-08-13 Generoath Co Ltd METHODS OF TREATING AGE-RELATED MACULAR DISEASES USING AIMP2-DX2 AND OPTIONALLY A TARGET SEQUENCE FOR MIR-142 AND RELATED COMPOSITIONS

Cited By (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN116406304A (zh) * 2020-09-30 2023-07-07 杰内罗蒂股份有限公司 使用AIMP2-DX2和任选地miR-142的靶序列及其组合物治疗年龄相关的黄斑疾病的方法

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JP2025516639A (ja) 2025-05-30
KR20250021321A (ko) 2025-02-12
US20250281573A1 (en) 2025-09-11
EP4522226A1 (en) 2025-03-19
EP4522226A4 (en) 2026-06-03
WO2023218430A1 (en) 2023-11-16

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