JP2025514304A5 - - Google Patents

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Publication number
JP2025514304A5
JP2025514304A5 JP2024563564A JP2024563564A JP2025514304A5 JP 2025514304 A5 JP2025514304 A5 JP 2025514304A5 JP 2024563564 A JP2024563564 A JP 2024563564A JP 2024563564 A JP2024563564 A JP 2024563564A JP 2025514304 A5 JP2025514304 A5 JP 2025514304A5
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JP
Japan
Prior art keywords
sequence
item
targeting segment
dna targeting
genome
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Pending
Application number
JP2024563564A
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English (en)
Japanese (ja)
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JP2025514304A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/066343 external-priority patent/WO2023212677A2/en
Publication of JP2025514304A publication Critical patent/JP2025514304A/ja
Publication of JP2025514304A5 publication Critical patent/JP2025514304A5/ja
Pending legal-status Critical Current

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JP2024563564A 2022-04-29 2023-04-28 遺伝子治療法のための組織特異的遺伝子外セーフハーバーの同定 Pending JP2025514304A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263336663P 2022-04-29 2022-04-29
US63/336,663 2022-04-29
PCT/US2023/066343 WO2023212677A2 (en) 2022-04-29 2023-04-28 Identification of tissue-specific extragenic safe harbors for gene therapy approaches

Publications (2)

Publication Number Publication Date
JP2025514304A JP2025514304A (ja) 2025-05-02
JP2025514304A5 true JP2025514304A5 (enExample) 2026-05-12

Family

ID=86603715

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024563564A Pending JP2025514304A (ja) 2022-04-29 2023-04-28 遺伝子治療法のための組織特異的遺伝子外セーフハーバーの同定

Country Status (5)

Country Link
US (1) US20250332287A1 (enExample)
EP (1) EP4514981A2 (enExample)
JP (1) JP2025514304A (enExample)
CN (1) CN119487200A (enExample)
WO (1) WO2023212677A2 (enExample)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2024218715A1 (en) 2023-04-19 2024-10-24 Btl Healthcare Technologies A.S. Culture media based on protein hydrolysate and a process for preparing thereof
US12668774B2 (en) 2023-10-12 2026-06-30 Btl Healthcare Technologies A.S. Product, system and method of cell cultivation

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TWI507525B (zh) 2009-06-26 2015-11-11 Regeneron Pharma 具天然免疫球蛋白形式之易分離的雙專一性抗體
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