JP2025513851A - 遺伝子治療のためのｉｒａｋ４モジュレーターの使用 - Google Patents

遺伝子治療のためのｉｒａｋ４モジュレーターの使用 Download PDF

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JP2025513851A
JP2025513851A JP2024560405A JP2024560405A JP2025513851A JP 2025513851 A JP2025513851 A JP 2025513851A JP 2024560405 A JP2024560405 A JP 2024560405A JP 2024560405 A JP2024560405 A JP 2024560405A JP 2025513851 A JP2025513851 A JP 2025513851A
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gene therapy
capsid
irak
aav
individual
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JP2025513851A5 (OSRAM
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ソウラブ・ロイ・チョードリー
モナ・モトワニ
クリスティアン・ミュラー
ジョン・リード
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Genzyme Corp
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Genzyme Corp
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    • A61K31/535—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with at least one nitrogen and one oxygen as the ring hetero atoms, e.g. 1,2-oxazines
    • A61K31/5375—1,4-Oxazines, e.g. morpholine
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JP2024560405A 2022-04-12 2023-04-12 遺伝子治療のためのｉｒａｋ４モジュレーターの使用 Pending JP2025513851A (ja)

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US202263330245P 2022-04-12 2022-04-12
US63/330,245 2022-04-12
PCT/US2023/065689 WO2023201274A1 (en) 2022-04-12 2023-04-12 Use of an irak4 modulator for gene therapy

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JP2025513851A true JP2025513851A (ja) 2025-04-30
JP2025513851A5 JP2025513851A5 (OSRAM) 2026-04-20

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US (1) US20230405014A1 (OSRAM)
EP (1) EP4508226A1 (OSRAM)
JP (1) JP2025513851A (OSRAM)
KR (1) KR20250004738A (OSRAM)
CN (1) CN119343458A (OSRAM)
AU (1) AU2023253700A1 (OSRAM)
CA (1) CA3248216A1 (OSRAM)
IL (1) IL316222A (OSRAM)
MX (1) MX2024012617A (OSRAM)
TW (1) TW202402329A (OSRAM)
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