JP2025512445A5 - - Google Patents

Info

Publication number
JP2025512445A5
JP2025512445A5 JP2024560613A JP2024560613A JP2025512445A5 JP 2025512445 A5 JP2025512445 A5 JP 2025512445A5 JP 2024560613 A JP2024560613 A JP 2024560613A JP 2024560613 A JP2024560613 A JP 2024560613A JP 2025512445 A5 JP2025512445 A5 JP 2025512445A5
Authority
JP
Japan
Prior art keywords
pharmaceutical composition
oligonucleotide
disease
scap
ome
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024560613A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025512445A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/018657 external-priority patent/WO2023201043A1/en
Publication of JP2025512445A publication Critical patent/JP2025512445A/ja
Publication of JP2025512445A5 publication Critical patent/JP2025512445A5/ja
Pending legal-status Critical Current

Links

JP2024560613A 2022-04-15 2023-04-14 Scap活性を調節するための組成物及び方法 Pending JP2025512445A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263363091P 2022-04-15 2022-04-15
US63/363,091 2022-04-15
PCT/US2023/018657 WO2023201043A1 (en) 2022-04-15 2023-04-14 Compositions and methods for modulating scap activity

Publications (2)

Publication Number Publication Date
JP2025512445A JP2025512445A (ja) 2025-04-17
JP2025512445A5 true JP2025512445A5 (https=) 2026-04-21

Family

ID=86330765

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024560613A Pending JP2025512445A (ja) 2022-04-15 2023-04-14 Scap活性を調節するための組成物及び方法

Country Status (12)

Country Link
US (1) US20230374522A1 (https=)
EP (1) EP4508218A1 (https=)
JP (1) JP2025512445A (https=)
KR (1) KR20250005108A (https=)
CN (1) CN119013402A (https=)
AR (1) AR129073A1 (https=)
AU (1) AU2023254798A1 (https=)
CA (1) CA3245064A1 (https=)
IL (1) IL315878A (https=)
MX (1) MX2024012729A (https=)
TW (1) TW202345873A (https=)
WO (1) WO2023201043A1 (https=)

Family Cites Families (32)

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WO2007030167A1 (en) 2005-09-02 2007-03-15 Nastech Pharmaceutical Company Inc. Modification of double-stranded ribonucleic acid molecules
DK2341943T3 (en) 2008-09-22 2019-02-25 Dicerna Pharmaceuticals Inc COMPOSITIONS AND METHODS OF SPECIFIC INHIBITION OF DSRNA REPRINT WITH MODIFICATIONS
US8691971B2 (en) 2008-09-23 2014-04-08 Scott G. Petersen Self delivering bio-labile phosphate protected pro-oligos for oligonucleotide based therapeutics and mediating RNA interference
US20100249214A1 (en) 2009-02-11 2010-09-30 Dicerna Pharmaceuticals Multiplex dicer substrate rna interference molecules having joining sequences
KR101728655B1 (ko) 2008-12-18 2017-04-19 다이서나 파마수이티컬, 인크. 유전자 발현의 특이적 억제를 위한 연장된 다이서 기질 제제 및 방법
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