AU2023254798A1 - Compositions and methods for modulating scap activity - Google Patents

Compositions and methods for modulating scap activity Download PDF

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Publication number
AU2023254798A1
AU2023254798A1 AU2023254798A AU2023254798A AU2023254798A1 AU 2023254798 A1 AU2023254798 A1 AU 2023254798A1 AU 2023254798 A AU2023254798 A AU 2023254798A AU 2023254798 A AU2023254798 A AU 2023254798A AU 2023254798 A1 AU2023254798 A1 AU 2023254798A1
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seq
nucleotides
nos
antisense strand
oligonucleotide
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AU2023254798A
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Bob Dale Brown
Seongmoon CHEONG
Henryk T. Dudek
Nicole Alexis Spiegelman
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Dicerna Pharmaceuticals Inc
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Dicerna Pharmaceuticals Inc
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    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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    • A61P1/16—Drugs for disorders of the alimentary tract or the digestive system for liver or gallbladder disorders, e.g. hepatoprotective agents, cholagogues, litholytics
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AU2023254798A 2022-04-15 2023-04-14 Compositions and methods for modulating scap activity Pending AU2023254798A1 (en)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263363091P 2022-04-15 2022-04-15
US63/363,091 2022-04-15
PCT/US2023/018657 WO2023201043A1 (en) 2022-04-15 2023-04-14 Compositions and methods for modulating scap activity

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AU2023254798A1 true AU2023254798A1 (en) 2024-09-19

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US (1) US20230374522A1 (https=)
EP (1) EP4508218A1 (https=)
JP (1) JP2025512445A (https=)
KR (1) KR20250005108A (https=)
CN (1) CN119013402A (https=)
AR (1) AR129073A1 (https=)
AU (1) AU2023254798A1 (https=)
CA (1) CA3245064A1 (https=)
IL (1) IL315878A (https=)
MX (1) MX2024012729A (https=)
TW (1) TW202345873A (https=)
WO (1) WO2023201043A1 (https=)

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MX2024012729A (es) 2024-11-08
JP2025512445A (ja) 2025-04-17
CA3245064A1 (en) 2023-10-19
IL315878A (en) 2024-11-01
KR20250005108A (ko) 2025-01-09
WO2023201043A1 (en) 2023-10-19
AR129073A1 (es) 2024-07-10
TW202345873A (zh) 2023-12-01
EP4508218A1 (en) 2025-02-19
US20230374522A1 (en) 2023-11-23
CN119013402A (zh) 2024-11-22

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