JP2025501768A5 - - Google Patents
Info
- Publication number
- JP2025501768A5 JP2025501768A5 JP2024538396A JP2024538396A JP2025501768A5 JP 2025501768 A5 JP2025501768 A5 JP 2025501768A5 JP 2024538396 A JP2024538396 A JP 2024538396A JP 2024538396 A JP2024538396 A JP 2024538396A JP 2025501768 A5 JP2025501768 A5 JP 2025501768A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- promoter
- mature
- aav
- raav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163293680P | 2021-12-24 | 2021-12-24 | |
| US63/293,680 | 2021-12-24 | ||
| PCT/US2022/082383 WO2023122803A1 (en) | 2021-12-24 | 2022-12-24 | Gene therapy for lamin a - associated deficiencies |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025501768A JP2025501768A (ja) | 2025-01-23 |
| JP2025501768A5 true JP2025501768A5 (https=) | 2026-01-07 |
Family
ID=86903820
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024538396A Pending JP2025501768A (ja) | 2021-12-24 | 2022-12-24 | ラミンａ関連欠損症に対する遺伝子療法 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20250049949A1 (https=) |
| EP (1) | EP4453226A4 (https=) |
| JP (1) | JP2025501768A (https=) |
| KR (1) | KR20240118821A (https=) |
| CN (1) | CN118434877A (https=) |
| AU (1) | AU2022419657A1 (https=) |
| CA (1) | CA3241202A1 (https=) |
| CO (1) | CO2024008188A2 (https=) |
| IL (1) | IL313734A (https=) |
| MX (1) | MX2024007903A (https=) |
| WO (1) | WO2023122803A1 (https=) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2024130070A2 (en) | 2022-12-17 | 2024-06-20 | The Trustees Of The University Of Pennsylvania | Recombinant aav capsids with cardiac- and skeletal muscle- specific targeting motifs and uses thereof |
| EP4634394A2 (en) | 2022-12-17 | 2025-10-22 | The Trustees of The University of Pennsylvania | Recombinant aav mutant vectors with cardiac and skeletal muscle-specific targeting motifs and compositions containing same |
| TW202516019A (zh) | 2023-06-29 | 2025-04-16 | 賓州大學委員會 | 具中樞神經系統靶向模體的突變aav及含有其之組成物 |
| WO2025075551A1 (en) * | 2023-10-06 | 2025-04-10 | National University Of Singapore | Method of treating lmna dilated cardiomyopathy |
| WO2025106661A1 (en) | 2023-11-14 | 2025-05-22 | The Trustees Of The University Of Pennsylvania | Compositions with cardiac and skeletal musclespecific targeting motifs and uses thereof |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US7291699B2 (en) * | 2003-03-18 | 2007-11-06 | The Regents Of The University Of Colorado | Product and methods for diagnosis and therapy for cardiac and skeletal muscle disorders |
| WO2013071047A1 (en) * | 2011-11-11 | 2013-05-16 | Children's Medical Center Corporation | Compositions and methods for in vitro transcription of rna |
| CN111886029B (zh) * | 2018-01-19 | 2024-04-12 | 新加坡科技研究局 | 破坏linc复合物以治疗核纤层蛋白病 |
| SG11202109362XA (en) * | 2019-02-28 | 2021-09-29 | Encoded Therapeutics Inc | Compositions and methods for treating laminopathies |
| EP4198053A1 (en) * | 2021-12-15 | 2023-06-21 | Universitätsklinikum Hamburg-Eppendorf | Lmna gene expression for treatment of laminopathies |
-
2022
- 2022-12-24 CA CA3241202A patent/CA3241202A1/en active Pending
- 2022-12-24 IL IL313734A patent/IL313734A/en unknown
- 2022-12-24 WO PCT/US2022/082383 patent/WO2023122803A1/en not_active Ceased
- 2022-12-24 EP EP22912777.4A patent/EP4453226A4/en active Pending
- 2022-12-24 JP JP2024538396A patent/JP2025501768A/ja active Pending
- 2022-12-24 US US18/723,236 patent/US20250049949A1/en active Pending
- 2022-12-24 KR KR1020247022099A patent/KR20240118821A/ko active Pending
- 2022-12-24 AU AU2022419657A patent/AU2022419657A1/en active Pending
- 2022-12-24 CN CN202280085172.6A patent/CN118434877A/zh active Pending
- 2022-12-24 MX MX2024007903A patent/MX2024007903A/es unknown
-
2024
- 2024-06-24 CO CONC2024/0008188A patent/CO2024008188A2/es unknown
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