JP2024537165A5 - - Google Patents

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Publication number
JP2024537165A5
JP2024537165A5 JP2024520839A JP2024520839A JP2024537165A5 JP 2024537165 A5 JP2024537165 A5 JP 2024537165A5 JP 2024520839 A JP2024520839 A JP 2024520839A JP 2024520839 A JP2024520839 A JP 2024520839A JP 2024537165 A5 JP2024537165 A5 JP 2024537165A5
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JP
Japan
Prior art keywords
ehgt
seq
sequence
mgt
cells
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024520839A
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English (en)
Japanese (ja)
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JP2024537165A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/077586 external-priority patent/WO2023060112A1/en
Publication of JP2024537165A publication Critical patent/JP2024537165A/ja
Publication of JP2024537165A5 publication Critical patent/JP2024537165A5/ja
Pending legal-status Critical Current

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JP2024520839A 2021-10-05 2022-10-05 小脳と第2の種類の細胞において遺伝子発現を調節するための人工発現コンストラクト Pending JP2024537165A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163252520P 2021-10-05 2021-10-05
US63/252,520 2021-10-05
PCT/US2022/077586 WO2023060112A1 (en) 2021-10-05 2022-10-05 Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type

Publications (2)

Publication Number Publication Date
JP2024537165A JP2024537165A (ja) 2024-10-10
JP2024537165A5 true JP2024537165A5 (https=) 2025-10-01

Family

ID=85803726

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024520839A Pending JP2024537165A (ja) 2021-10-05 2022-10-05 小脳と第2の種類の細胞において遺伝子発現を調節するための人工発現コンストラクト

Country Status (6)

Country Link
US (1) US20250235550A1 (https=)
EP (1) EP4413142A4 (https=)
JP (1) JP2024537165A (https=)
AU (1) AU2022360979A1 (https=)
CA (1) CA3233342A1 (https=)
WO (1) WO2023060112A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2024308266A1 (en) * 2023-06-28 2025-12-18 Allen Institute Artificial expression constructs for modulating gene expression in cardiomyocytes
WO2025179180A1 (en) * 2024-02-23 2025-08-28 Allen Institute Artificial expression constructs for modulating gene expression in motor neurons and cerebellar neurons

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2013155222A2 (en) * 2012-04-10 2013-10-17 The Regents Of The University Of California Brain-specific enhancers for cell-based therapy
US20220249703A1 (en) * 2019-02-15 2022-08-11 Allen Institute Artificial expression constructs for selectively modulating gene expression in selected neuronal cell populations
CA3173609A1 (en) * 2020-03-27 2021-09-30 Allen Institute Artificial expression constructs for selectively modulating gene expression in non-neuronal brain cells
AU2021261359A1 (en) * 2020-04-21 2022-12-08 Allen Institute Artificial expression constructs for selectively modulating gene expression in neocortical layer 5 glutamatergic neurons
WO2022246276A2 (en) * 2021-05-21 2022-11-24 Allen Institute Artificial expression constructs for modulating gene expression in neurons within the thalamus

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