JP2024537165A - 小脳と第２の種類の細胞において遺伝子発現を調節するための人工発現コンストラクト - Google Patents

小脳と第２の種類の細胞において遺伝子発現を調節するための人工発現コンストラクト Download PDF

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JP2024537165A
JP2024537165A JP2024520839A JP2024520839A JP2024537165A JP 2024537165 A JP2024537165 A JP 2024537165A JP 2024520839 A JP2024520839 A JP 2024520839A JP 2024520839 A JP2024520839 A JP 2024520839A JP 2024537165 A JP2024537165 A JP 2024537165A
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ehgt
cells
coding sequence
heterologous coding
seq
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デイグル，タニア
セバスティアン レイン，エドワード
ピー． レヴィ，ボアズ
タシック，ボシリカ
ティン，ジョナサン
ゼン，ホンクイ
ケー． ミック，ジョン
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アレン インスティテュート
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JP2024520839A 2021-10-05 2022-10-05 小脳と第２の種類の細胞において遺伝子発現を調節するための人工発現コンストラクト Pending JP2024537165A (ja)

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US202163252520P 2021-10-05 2021-10-05
US63/252,520 2021-10-05
PCT/US2022/077586 WO2023060112A1 (en) 2021-10-05 2022-10-05 Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type

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JP2024537165A true JP2024537165A (ja) 2024-10-10
JP2024537165A5 JP2024537165A5 (https=) 2025-10-01

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US (1) US20250235550A1 (https=)
EP (1) EP4413142A4 (https=)
JP (1) JP2024537165A (https=)
AU (1) AU2022360979A1 (https=)
CA (1) CA3233342A1 (https=)
WO (1) WO2023060112A1 (https=)

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AU2024308266A1 (en) * 2023-06-28 2025-12-18 Allen Institute Artificial expression constructs for modulating gene expression in cardiomyocytes
WO2025179180A1 (en) * 2024-02-23 2025-08-28 Allen Institute Artificial expression constructs for modulating gene expression in motor neurons and cerebellar neurons

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WO2013155222A2 (en) * 2012-04-10 2013-10-17 The Regents Of The University Of California Brain-specific enhancers for cell-based therapy
US20220249703A1 (en) * 2019-02-15 2022-08-11 Allen Institute Artificial expression constructs for selectively modulating gene expression in selected neuronal cell populations
CA3173609A1 (en) * 2020-03-27 2021-09-30 Allen Institute Artificial expression constructs for selectively modulating gene expression in non-neuronal brain cells
AU2021261359A1 (en) * 2020-04-21 2022-12-08 Allen Institute Artificial expression constructs for selectively modulating gene expression in neocortical layer 5 glutamatergic neurons
WO2022246276A2 (en) * 2021-05-21 2022-11-24 Allen Institute Artificial expression constructs for modulating gene expression in neurons within the thalamus

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CA3233342A1 (en) 2023-04-13
AU2022360979A1 (en) 2024-05-09
WO2023060112A1 (en) 2023-04-13
US20250235550A1 (en) 2025-07-24
EP4413142A1 (en) 2024-08-14
EP4413142A4 (en) 2025-11-05

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