AU2022360979A1 - Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type - Google Patents
Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type Download PDFInfo
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- AU2022360979A1 AU2022360979A1 AU2022360979A AU2022360979A AU2022360979A1 AU 2022360979 A1 AU2022360979 A1 AU 2022360979A1 AU 2022360979 A AU2022360979 A AU 2022360979A AU 2022360979 A AU2022360979 A AU 2022360979A AU 2022360979 A1 AU2022360979 A1 AU 2022360979A1
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- A61K48/0008—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
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- C12N2750/14011—Parvoviridae
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- C12N2840/00—Vectors comprising a special translation-regulating system
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- Neurology (AREA)
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- Gastroenterology & Hepatology (AREA)
- Proteomics, Peptides & Aminoacids (AREA)
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163252520P | 2021-10-05 | 2021-10-05 | |
| US63/252,520 | 2021-10-05 | ||
| PCT/US2022/077586 WO2023060112A1 (en) | 2021-10-05 | 2022-10-05 | Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| AU2022360979A1 true AU2022360979A1 (en) | 2024-05-09 |
Family
ID=85803726
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| AU2022360979A Pending AU2022360979A1 (en) | 2021-10-05 | 2022-10-05 | Artificial expression constructs for modulating gene expression in the cerebellum and a secondary cell type |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20250235550A1 (https=) |
| EP (1) | EP4413142A4 (https=) |
| JP (1) | JP2024537165A (https=) |
| AU (1) | AU2022360979A1 (https=) |
| CA (1) | CA3233342A1 (https=) |
| WO (1) | WO2023060112A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2024308266A1 (en) * | 2023-06-28 | 2025-12-18 | Allen Institute | Artificial expression constructs for modulating gene expression in cardiomyocytes |
| WO2025179180A1 (en) * | 2024-02-23 | 2025-08-28 | Allen Institute | Artificial expression constructs for modulating gene expression in motor neurons and cerebellar neurons |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2013155222A2 (en) * | 2012-04-10 | 2013-10-17 | The Regents Of The University Of California | Brain-specific enhancers for cell-based therapy |
| US20220249703A1 (en) * | 2019-02-15 | 2022-08-11 | Allen Institute | Artificial expression constructs for selectively modulating gene expression in selected neuronal cell populations |
| CA3173609A1 (en) * | 2020-03-27 | 2021-09-30 | Allen Institute | Artificial expression constructs for selectively modulating gene expression in non-neuronal brain cells |
| AU2021261359A1 (en) * | 2020-04-21 | 2022-12-08 | Allen Institute | Artificial expression constructs for selectively modulating gene expression in neocortical layer 5 glutamatergic neurons |
| WO2022246276A2 (en) * | 2021-05-21 | 2022-11-24 | Allen Institute | Artificial expression constructs for modulating gene expression in neurons within the thalamus |
-
2022
- 2022-10-05 EP EP22879443.4A patent/EP4413142A4/en active Pending
- 2022-10-05 JP JP2024520839A patent/JP2024537165A/ja active Pending
- 2022-10-05 WO PCT/US2022/077586 patent/WO2023060112A1/en not_active Ceased
- 2022-10-05 CA CA3233342A patent/CA3233342A1/en active Pending
- 2022-10-05 AU AU2022360979A patent/AU2022360979A1/en active Pending
- 2022-10-05 US US18/698,499 patent/US20250235550A1/en active Pending
Also Published As
| Publication number | Publication date |
|---|---|
| CA3233342A1 (en) | 2023-04-13 |
| JP2024537165A (ja) | 2024-10-10 |
| WO2023060112A1 (en) | 2023-04-13 |
| US20250235550A1 (en) | 2025-07-24 |
| EP4413142A1 (en) | 2024-08-14 |
| EP4413142A4 (en) | 2025-11-05 |
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