JP2024536088A5 - - Google Patents

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Publication number
JP2024536088A5
JP2024536088A5 JP2024518725A JP2024518725A JP2024536088A5 JP 2024536088 A5 JP2024536088 A5 JP 2024536088A5 JP 2024518725 A JP2024518725 A JP 2024518725A JP 2024518725 A JP2024518725 A JP 2024518725A JP 2024536088 A5 JP2024536088 A5 JP 2024536088A5
Authority
JP
Japan
Prior art keywords
nucleic acid
oligonucleotide
target nucleic
target
oligonucleotides
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024518725A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024536088A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/044767 external-priority patent/WO2023049477A2/en
Publication of JP2024536088A publication Critical patent/JP2024536088A/ja
Publication of JP2024536088A5 publication Critical patent/JP2024536088A5/ja
Pending legal-status Critical Current

Links

JP2024518725A 2021-09-26 2022-09-26 Mecp2転写物を編集するための組成物及びその方法 Pending JP2024536088A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202163248524P 2021-09-26 2021-09-26
US63/248,524 2021-09-26
US202263341391P 2022-05-12 2022-05-12
US63/341,391 2022-05-12
PCT/US2022/044767 WO2023049477A2 (en) 2021-09-26 2022-09-26 Compositions for editing mecp2 transcripts and methods thereof

Publications (2)

Publication Number Publication Date
JP2024536088A JP2024536088A (ja) 2024-10-04
JP2024536088A5 true JP2024536088A5 (https=) 2025-10-06

Family

ID=85721202

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024518725A Pending JP2024536088A (ja) 2021-09-26 2022-09-26 Mecp2転写物を編集するための組成物及びその方法

Country Status (6)

Country Link
US (1) US20250135036A1 (https=)
EP (1) EP4404942A2 (https=)
JP (1) JP2024536088A (https=)
AU (1) AU2022349529A1 (https=)
CA (1) CA3232965A1 (https=)
WO (1) WO2023049477A2 (https=)

Families Citing this family (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PL2872485T3 (pl) 2012-07-13 2021-05-31 Wave Life Sciences Ltd. Asymetryczna grupa pomocnicza
BR112016016400A2 (pt) 2014-01-16 2017-10-03 Wave Life Sciences Ltd Composições de oligonucleotídeos quiralmente controlados, seu uso, sua composição farmacêutica, e métodos
IL320434A (en) 2015-07-22 2025-06-01 Wave Life Sciences Ltd Oligonucleotide preparations and methods
JP2019520339A (ja) 2016-06-03 2019-07-18 ウェイブ ライフ サイエンシズ リミテッドWave Life Sciences Ltd. オリゴヌクレオチド、その組成物および方法
US11873316B2 (en) 2016-11-23 2024-01-16 Wave Life Sciences Ltd. Compositions and methods for phosphoramidite and oligonucleotide synthesis
US11718638B2 (en) 2017-06-21 2023-08-08 Wave Life Sciences Ltd. Compounds, compositions and methods for synthesis
CA3072110A1 (en) 2017-09-18 2019-03-21 Wave Life Sciences Ltd. Technologies for oligonucleotide preparation
SG11202009877XA (en) 2018-04-12 2020-11-27 Wave Life Sciences Ltd Oligonucleotide compositions and methods of use thereof
US12391942B2 (en) 2018-05-11 2025-08-19 Wave Life Sciences Ltd. Oligonucleotide compositions and methods of use thereof
JP2022525541A (ja) 2019-03-20 2022-05-17 ウェイブ ライフ サイエンシズ リミテッド オリゴヌクレオチド調製に有用な技術
AU2024354150A1 (en) * 2023-09-28 2026-03-12 Wave Life Sciences Ltd. Oligonucleotide compositions and methods thereof
WO2026077951A1 (en) 2024-10-07 2026-04-16 Vico Therapeutics B.V. Improved aon for rna editing

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20030190626A1 (en) * 2002-04-09 2003-10-09 Vasulinga Ravikumar Phosphorothioate monoester modified oligomers
US11866697B2 (en) * 2017-05-18 2024-01-09 The Broad Institute, Inc. Systems, methods, and compositions for targeted nucleic acid editing
AU2020279751A1 (en) * 2019-05-21 2021-12-02 Beam Therapeutics Inc. Methods of editing a single nucleotide polymorphism using programmable base editor systems
KR20230118716A (ko) * 2020-11-08 2023-08-11 웨이브 라이프 사이언시스 리미티드 올리고뉴클레오티드 조성물 및 이의 방법

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